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5. Acid sphingomyelinase: identification of nine novel mutations among Italian Niemann Pick type B patients and characterization of in vivo functional in-frame start codon. Pittis MG; Ricci V; Guerci VI; Marçais C; Ciana G; Dardis A; Gerin F; Stroppiano M; Vanier MT; Filocamo M; Bembi B Hum Mutat; 2004 Aug; 24(2):186-7. PubMed ID: 15241805 [TBL] [Abstract][Full Text] [Related]
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13. [Niemann-Pick disease type C--a neurometabolic disease through disturbed intracellular lipid transport]. Grau AJ; Weisbrod M; Hund E; Harzer K Nervenarzt; 2003 Oct; 74(10):900-5. PubMed ID: 14551697 [TBL] [Abstract][Full Text] [Related]
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