These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

196 related articles for article (PubMed ID: 23989781)

  • 21. Ubiquitous high-level gene expression in hematopoietic lineages provides effective lentiviral gene therapy of murine Wiskott-Aldrich syndrome.
    Astrakhan A; Sather BD; Ryu BY; Khim S; Singh S; Humblet-Baron S; Ochs HD; Miao CH; Rawlings DJ
    Blood; 2012 May; 119(19):4395-407. PubMed ID: 22431569
    [TBL] [Abstract][Full Text] [Related]  

  • 22. An emerging era of clinical benefit from gene therapy.
    Malech HL; Ochs HD
    JAMA; 2015 Apr; 313(15):1522-3. PubMed ID: 25898049
    [No Abstract]   [Full Text] [Related]  

  • 23. Efficacy of gene therapy for Wiskott-Aldrich syndrome using a WAS promoter/cDNA-containing lentiviral vector and nonlethal irradiation.
    Dupré L; Marangoni F; Scaramuzza S; Trifari S; Hernández RJ; Aiuti A; Naldini L; Roncarolo MG
    Hum Gene Ther; 2006 Mar; 17(3):303-13. PubMed ID: 16544979
    [TBL] [Abstract][Full Text] [Related]  

  • 24. Biosafety challenges for use of lentiviral vectors in gene therapy.
    Rothe M; Modlich U; Schambach A
    Curr Gene Ther; 2013 Dec; 13(6):453-68. PubMed ID: 24195603
    [TBL] [Abstract][Full Text] [Related]  

  • 25. Lentiviral-mediated gene therapy leads to improvement of B-cell functionality in a murine model of Wiskott-Aldrich syndrome.
    Bosticardo M; Draghici E; Schena F; Sauer AV; Fontana E; Castiello MC; Catucci M; Locci M; Naldini L; Aiuti A; Roncarolo MG; Poliani PL; Traggiai E; Villa A
    J Allergy Clin Immunol; 2011 Jun; 127(6):1376-84.e5. PubMed ID: 21531013
    [TBL] [Abstract][Full Text] [Related]  

  • 26. Diverse genomic integration of a lentiviral vector developed for the treatment of Wiskott-Aldrich syndrome.
    Mantovani J; Charrier S; Eckenberg R; Saurin W; Danos O; Perea J; Galy A
    J Gene Med; 2009 Aug; 11(8):645-54. PubMed ID: 19455589
    [TBL] [Abstract][Full Text] [Related]  

  • 27. Development of novel efficient SIN vectors with improved safety features for Wiskott-Aldrich syndrome stem cell based gene therapy.
    Avedillo Díez I; Zychlinski D; Coci EG; Galla M; Modlich U; Dewey RA; Schwarzer A; Maetzig T; Mpofu N; Jaeckel E; Boztug K; Baum C; Klein C; Schambach A
    Mol Pharm; 2011 Oct; 8(5):1525-37. PubMed ID: 21851067
    [TBL] [Abstract][Full Text] [Related]  

  • 28. A possible turning point in the hematopoietic stem cell gene therapy for primary immunodeficiency diseases? Lentiviral vectors could take the place of retroviral vectors.
    Ariga T
    Expert Rev Clin Immunol; 2013 Nov; 9(11):1015-8. PubMed ID: 24168409
    [TBL] [Abstract][Full Text] [Related]  

  • 29. A roadmap to safe, efficient, and stable lentivirus-mediated gene therapy with hematopoietic cell transplantation.
    Neschadim A; McCart JA; Keating A; Medin JA
    Biol Blood Marrow Transplant; 2007 Dec; 13(12):1407-16. PubMed ID: 18022569
    [TBL] [Abstract][Full Text] [Related]  

  • 30. Opportunities for the use of lentiviral vectors in human gene therapy.
    Galimi F; Verma IM
    Curr Top Microbiol Immunol; 2002; 261():245-54. PubMed ID: 11892251
    [No Abstract]   [Full Text] [Related]  

  • 31. Improvement of migratory defects in a murine model of Wiskott-Aldrich syndrome gene therapy.
    Blundell MP; Bouma G; Calle Y; Jones GE; Kinnon C; Thrasher AJ
    Mol Ther; 2008 May; 16(5):836-44. PubMed ID: 18388921
    [TBL] [Abstract][Full Text] [Related]  

  • 32. Use of Defibrotide to help prevent post-transplant endothelial injury in a genetically predisposed infant with metachromatic leukodystrophy undergoing hematopoietic stem cell gene therapy.
    Calbi V; Fumagalli F; Consiglieri G; Penati R; Acquati S; Redaelli D; Attanasio V; Marcella F; Cicalese MP; Migliavacca M; Barzaghi F; Ferrua F; Assanelli A; Silvani P; Zoccolillo M; Chidini G; Chiesa R; Arora R; Ciotti F; Sarzana M; Antonioli G; Baldoli C; Morena F; Martino S; Ardissino GL; Sora MGN; Naldini L; Ciceri F; Aiuti A; Bernardo ME
    Bone Marrow Transplant; 2018 Jul; 53(7):913-917. PubMed ID: 29379168
    [No Abstract]   [Full Text] [Related]  

  • 33. Genome editing for primary immunodeficiencies: A therapeutic perspective on Wiskott-Aldrich syndrome.
    Naseem A; Steinberg Z; Cavazza A
    Front Immunol; 2022; 13():966084. PubMed ID: 36059471
    [TBL] [Abstract][Full Text] [Related]  

  • 34. Stable mixed chimerism after hematopoietic stem cell transplantation in Wiskott-Aldrich syndrome.
    Doğu F; Kurtuluş-Ulküer M; Bilge Y; Bozdoğan G; Ulküer U; Malhatun E; Ikincioğullari A; Babacan E
    Pediatr Transplant; 2006 May; 10(3):395-9. PubMed ID: 16677369
    [TBL] [Abstract][Full Text] [Related]  

  • 35. [Wiskott-Aldrich syndrome: a new advance in gene therapy].
    Nau JY
    Rev Med Suisse; 2015 Apr; 11(472):996-7. PubMed ID: 26062229
    [No Abstract]   [Full Text] [Related]  

  • 36. Improved lentiviral vectors for Wiskott-Aldrich syndrome gene therapy mimic endogenous expression profiles throughout haematopoiesis.
    Frecha C; Toscano MG; Costa C; Saez-Lara MJ; Cosset FL; Verhoeyen E; Martin F
    Gene Ther; 2008 Jun; 15(12):930-41. PubMed ID: 18323794
    [TBL] [Abstract][Full Text] [Related]  

  • 37. Gene therapy for leukodystrophies.
    Biffi A; Aubourg P; Cartier N
    Hum Mol Genet; 2011 Apr; 20(R1):R42-53. PubMed ID: 21459776
    [TBL] [Abstract][Full Text] [Related]  

  • 38. A phase I/II clinical trial of beta-globin gene therapy for beta-thalassemia.
    Bank A; Dorazio R; Leboulch P
    Ann N Y Acad Sci; 2005; 1054():308-16. PubMed ID: 16339679
    [TBL] [Abstract][Full Text] [Related]  

  • 39. Development of lentiviral gene therapy for Wiskott Aldrich syndrome.
    Galy A; Roncarolo MG; Thrasher AJ
    Expert Opin Biol Ther; 2008 Feb; 8(2):181-90. PubMed ID: 18194074
    [TBL] [Abstract][Full Text] [Related]  

  • 40. Progress in gene therapy for primary immunodeficiencies using lentiviral vectors.
    Sauer AV; Di Lorenzo B; Carriglio N; Aiuti A
    Curr Opin Allergy Clin Immunol; 2014 Dec; 14(6):527-34. PubMed ID: 25207699
    [TBL] [Abstract][Full Text] [Related]  

    [Previous]   [Next]    [New Search]
    of 10.