BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

214 related articles for article (PubMed ID: 24042561)

  • 1. Platelet gene therapy by lentiviral gene delivery to hematopoietic stem cells restores hemostasis and induces humoral immune tolerance in FIX(null) mice.
    Chen Y; Schroeder JA; Kuether EL; Zhang G; Shi Q
    Mol Ther; 2014 Jan; 22(1):169-77. PubMed ID: 24042561
    [TBL] [Abstract][Full Text] [Related]  

  • 2. In vivo enrichment of genetically manipulated platelets for murine hemophilia B gene therapy.
    Chen Y; Schroeder JA; Gao C; Li J; Hu J; Shi Q
    J Cell Physiol; 2021 Jan; 236(1):354-365. PubMed ID: 32510630
    [TBL] [Abstract][Full Text] [Related]  

  • 3. The impact of GPIbα on platelet-targeted FVIII gene therapy in hemophilia A mice with pre-existing anti-FVIII immunity.
    Chen J; Schroeder JA; Luo X; Montgomery RR; Shi Q
    J Thromb Haemost; 2019 Mar; 17(3):449-459. PubMed ID: 30609275
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Factor IX ectopically expressed in platelets can be stored in alpha-granules and corrects the phenotype of hemophilia B mice.
    Zhang G; Shi Q; Fahs SA; Kuether EL; Walsh CE; Montgomery RR
    Blood; 2010 Aug; 116(8):1235-43. PubMed ID: 20445020
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Lentivirus-mediated platelet gene therapy of murine hemophilia A with pre-existing anti-factor VIII immunity.
    Kuether EL; Schroeder JA; Fahs SA; Cooley BC; Chen Y; Montgomery RR; Wilcox DA; Shi Q
    J Thromb Haemost; 2012 Aug; 10(8):1570-80. PubMed ID: 22632092
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Immune tolerance induced by platelet-targeted factor VIII gene therapy in hemophilia A mice is CD4 T cell mediated.
    Chen Y; Luo X; Schroeder JA; Chen J; Baumgartner CK; Hu J; Shi Q
    J Thromb Haemost; 2017 Oct; 15(10):1994-2004. PubMed ID: 28799202
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Platelet-targeted hyperfunctional FIX gene therapy for hemophilia B mice even with preexisting anti-FIX immunity.
    Schroeder JA; Chen J; Chen Y; Cai Y; Yu H; Mattson JG; Monahan PE; Shi Q
    Blood Adv; 2021 Mar; 5(5):1224-1238. PubMed ID: 33646304
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice.
    Annoni A; Cantore A; Della Valle P; Goudy K; Akbarpour M; Russo F; Bartolaccini S; D'Angelo A; Roncarolo MG; Naldini L
    EMBO Mol Med; 2013 Nov; 5(11):1684-97. PubMed ID: 24106222
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Integration-deficient lentiviral vectors expressing codon-optimized R338L human FIX restore normal hemostasis in Hemophilia B mice.
    Suwanmanee T; Hu G; Gui T; Bartholomae CC; Kutschera I; von Kalle C; Schmidt M; Monahan PE; Kafri T
    Mol Ther; 2014 Mar; 22(3):567-574. PubMed ID: 23941813
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Correction of murine Bernard-Soulier syndrome by lentivirus-mediated gene therapy.
    Kanaji S; Kuether EL; Fahs SA; Schroeder JA; Ware J; Montgomery RR; Shi Q
    Mol Ther; 2012 Mar; 20(3):625-32. PubMed ID: 22044935
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-associated virus clinical trial.
    Monahan PE; Sun J; Gui T; Hu G; Hannah WB; Wichlan DG; Wu Z; Grieger JC; Li C; Suwanmanee T; Stafford DW; Booth CJ; Samulski JJ; Kafri T; McPhee SW; Samulski RJ
    Hum Gene Ther; 2015 Feb; 26(2):69-81. PubMed ID: 25419787
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Platelet gene therapy corrects the hemophilic phenotype in immunocompromised hemophilia A mice transplanted with genetically manipulated human cord blood stem cells.
    Shi Q; Kuether EL; Chen Y; Schroeder JA; Fahs SA; Montgomery RR
    Blood; 2014 Jan; 123(3):395-403. PubMed ID: 24269957
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Efficient induction of immune tolerance to coagulation factor IX following direct intramuscular gene transfer.
    Cohn EF; Zhuo J; Kelly ME; Chao HJ
    J Thromb Haemost; 2007 Jun; 5(6):1227-36. PubMed ID: 17362228
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Syngeneic transplantation of hematopoietic stem cells that are genetically modified to express factor VIII in platelets restores hemostasis to hemophilia A mice with preexisting FVIII immunity.
    Shi Q; Fahs SA; Wilcox DA; Kuether EL; Morateck PA; Mareno N; Weiler H; Montgomery RR
    Blood; 2008 Oct; 112(7):2713-21. PubMed ID: 18495954
    [TBL] [Abstract][Full Text] [Related]  

  • 15. In vivo enrichment of genetically manipulated platelets corrects the murine hemophilic phenotype and induces immune tolerance even using a low multiplicity of infection.
    Schroeder JA; Chen Y; Fang J; Wilcox DA; Shi Q
    J Thromb Haemost; 2014 Aug; 12(8):1283-93. PubMed ID: 24931217
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Oral gene therapy for hemophilia B using chitosan-formulated FIX mutants.
    Quade-Lyssy P; Milanov P; Abriss D; Ungerer C; Königs C; Seifried E; Schüttrumpf J
    J Thromb Haemost; 2014 Jun; 12(6):932-42. PubMed ID: 24679056
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Efficacy and safety of adeno-associated viral vectors based on serotype 8 and 9 vs. lentiviral vectors for hemophilia B gene therapy.
    Vandendriessche T; Thorrez L; Acosta-Sanchez A; Petrus I; Wang L; Ma L; DE Waele L; Iwasaki Y; Gillijns V; Wilson JM; Collen D; Chuah MK
    J Thromb Haemost; 2007 Jan; 5(1):16-24. PubMed ID: 17002653
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Sustained expression of coagulation factor IX by modified cord blood-derived mesenchymal stromal cells.
    Dodd M; Marquez-Curtis L; Janowska-Wieczorek A; Hortelano G
    J Gene Med; 2014; 16(5-6):131-42. PubMed ID: 24947827
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Hyperfunctional coagulation factor IX improves the efficacy of gene therapy in hemophilic mice.
    Cantore A; Nair N; Della Valle P; Di Matteo M; Màtrai J; Sanvito F; Brombin C; Di Serio C; D'Angelo A; Chuah M; Naldini L; Vandendriessche T
    Blood; 2012 Nov; 120(23):4517-20. PubMed ID: 23043073
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Lentivirus-mediated platelet-derived factor VIII gene therapy in murine haemophilia A.
    Shi Q; Wilcox DA; Fahs SA; Fang J; Johnson BD; DU LM; Desai D; Montgomery RR
    J Thromb Haemost; 2007 Feb; 5(2):352-61. PubMed ID: 17269937
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 11.