266 related articles for article (PubMed ID: 24195602)
1. Biosafety of recombinant adeno-associated virus vectors.
Dismuke DJ; Tenenbaum L; Samulski RJ
Curr Gene Ther; 2013 Dec; 13(6):434-52. PubMed ID: 24195602
[TBL] [Abstract][Full Text] [Related]
2. Progress with Recombinant Adeno-Associated Virus Vectors for Gene Therapy of Alpha-1 Antitrypsin Deficiency.
Gruntman AM; Flotte TR
Hum Gene Ther Methods; 2015 Jun; 26(3):77-81. PubMed ID: 26067712
[TBL] [Abstract][Full Text] [Related]
3. Assessing the potential for AAV vector genotoxicity in a murine model.
Li H; Malani N; Hamilton SR; Schlachterman A; Bussadori G; Edmonson SE; Shah R; Arruda VR; Mingozzi F; Wright JF; Bushman FD; High KA
Blood; 2011 Mar; 117(12):3311-9. PubMed ID: 21106988
[TBL] [Abstract][Full Text] [Related]
4. Current limitations of gene therapy for rare pediatric diseases: Lessons learned from clinical experience with AAV vectors.
Gardin A; Ronzitti G
Arch Pediatr; 2023 Nov; 30(8S1):8S46-8S52. PubMed ID: 38043983
[TBL] [Abstract][Full Text] [Related]
5. Unlocking the potential of adeno-associated virus in neuroscience: a brief review.
Minetti A
Mol Biol Rep; 2024 Apr; 51(1):563. PubMed ID: 38647711
[TBL] [Abstract][Full Text] [Related]
6. Adeno-associated viruses for gene therapy - clinical implications and liver-related complications, a guide for hepatologists.
Mücke MM; Fong S; Foster GR; Lillicrap D; Miesbach W; Zeuzem S
J Hepatol; 2024 Feb; 80(2):352-361. PubMed ID: 37890721
[TBL] [Abstract][Full Text] [Related]
7. Selection of appropriate non-clinical animal models to ensure translatability of novel AAV-gene therapies to the clinic.
Singh M; Brooks A; Toofan P; McLuckie K
Gene Ther; 2024 Jan; 31(1-2):56-63. PubMed ID: 37612361
[TBL] [Abstract][Full Text] [Related]
8. Adeno-associated virus as a delivery vector for gene therapy of human diseases.
Wang JH; Gessler DJ; Zhan W; Gallagher TL; Gao G
Signal Transduct Target Ther; 2024 Apr; 9(1):78. PubMed ID: 38565561
[TBL] [Abstract][Full Text] [Related]
9. Development of AAV-Mediated Gene Therapy Approaches to Treat Skeletal Diseases.
Lin C; Greenblatt MB; Gao G; Shim JH
Hum Gene Ther; 2024 May; 35(9-10):317-328. PubMed ID: 38534217
[TBL] [Abstract][Full Text] [Related]
10. The evolution of heart gene delivery vectors.
Wasala NB; Shin JH; Duan D
J Gene Med; 2011 Oct; 13(10):557-65. PubMed ID: 21837689
[TBL] [Abstract][Full Text] [Related]
11. Lessons learned from lung and liver in-vivo gene therapy: implications for the future.
van Haasteren J; Hyde SC; Gill DR
Expert Opin Biol Ther; 2018 Sep; 18(9):959-972. PubMed ID: 30067117
[TBL] [Abstract][Full Text] [Related]
12. Viral vectors for in vivo gene transfer in Parkinson's disease: properties and clinical grade production.
Mandel RJ; Burger C; Snyder RO
Exp Neurol; 2008 Jan; 209(1):58-71. PubMed ID: 17916354
[TBL] [Abstract][Full Text] [Related]
13. Drug product Formulation and Fill/Finish Manufacturing Process Considerations for AAV-Based Genomic Medicines.
Som M; Gikanga B; Kanapuram V; Yadav S
J Pharm Sci; 2024 Jul; 113(7):1711-1725. PubMed ID: 38570073
[TBL] [Abstract][Full Text] [Related]
14. Safety of Adeno-associated virus-based vector-mediated gene therapy-impact of vector dose.
Maurya S; Sarangi P; Jayandharan GR
Cancer Gene Ther; 2022 Oct; 29(10):1305-1306. PubMed ID: 35027711
[No Abstract] [Full Text] [Related]
15. Recent developments in gene therapy research in India.
Selot R; Ghosh A
J Biosci; 2024; 49():. PubMed ID: 38384245
[TBL] [Abstract][Full Text] [Related]
16. Gene therapy: design and prospects for craniofacial regeneration.
Scheller EL; Krebsbach PH
J Dent Res; 2009 Jul; 88(7):585-96. PubMed ID: 19641145
[TBL] [Abstract][Full Text] [Related]
17. Towards Clinical Implementation of Adeno-Associated Virus (AAV) Vectors for Cancer Gene Therapy: Current Status and Future Perspectives.
Hacker UT; Bentler M; Kaniowska D; Morgan M; Büning H
Cancers (Basel); 2020 Jul; 12(7):. PubMed ID: 32674264
[TBL] [Abstract][Full Text] [Related]
18. Gene Therapy.
Thorne B; Takeya R; Vitelli F; Swanson X
Adv Biochem Eng Biotechnol; 2018; 165():351-399. PubMed ID: 28289769
[TBL] [Abstract][Full Text] [Related]
19. The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute.
Flotte TR; Daniels E; Benson J; Bevett-Rose JM; Cornetta K; Diggins M; Johnston J; Sepelak S; van der Loo JCM; Wilson JM; McDonald CL
Hum Gene Ther Clin Dev; 2017 Dec; 28(4):178-186. PubMed ID: 29130351
[TBL] [Abstract][Full Text] [Related]
20. Progress in Respiratory Gene Therapy.
McLachlan G; Alton EWFW; Boyd AC; Clarke NK; Davies JC; Gill DR; Griesenbach U; Hickmott JW; Hyde SC; Miah KM; Molina CJ
Hum Gene Ther; 2022 Sep; 33(17-18):893-912. PubMed ID: 36074947
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
