597 related articles for article (PubMed ID: 24390344)
1. Selection and evaluation of clinically relevant AAV variants in a xenograft liver model.
Lisowski L; Dane AP; Chu K; Zhang Y; Cunningham SC; Wilson EM; Nygaard S; Grompe M; Alexander IE; Kay MA
Nature; 2014 Feb; 506(7488):382-6. PubMed ID: 24390344
[TBL] [Abstract][Full Text] [Related]
2. Using a barcoded AAV capsid library to select for clinically relevant gene therapy vectors.
Pekrun K; De Alencastro G; Luo QJ; Liu J; Kim Y; Nygaard S; Galivo F; Zhang F; Song R; Tiffany MR; Xu J; Hebrok M; Grompe M; Kay MA
JCI Insight; 2019 Nov; 4(22):. PubMed ID: 31723052
[TBL] [Abstract][Full Text] [Related]
3. Bioengineered AAV Capsids with Combined High Human Liver Transduction In Vivo and Unique Humoral Seroreactivity.
Paulk NK; Pekrun K; Zhu E; Nygaard S; Li B; Xu J; Chu K; Leborgne C; Dane AP; Haft A; Zhang Y; Zhang F; Morton C; Valentine MB; Davidoff AM; Nathwani AC; Mingozzi F; Grompe M; Alexander IE; Lisowski L; Kay MA
Mol Ther; 2018 Jan; 26(1):289-303. PubMed ID: 29055620
[TBL] [Abstract][Full Text] [Related]
4. Engineered AAV vector minimizes in vivo targeting of transduced hepatocytes by capsid-specific CD8+ T cells.
Martino AT; Basner-Tschakarjan E; Markusic DM; Finn JD; Hinderer C; Zhou S; Ostrov DA; Srivastava A; Ertl HC; Terhorst C; High KA; Mingozzi F; Herzog RW
Blood; 2013 Mar; 121(12):2224-33. PubMed ID: 23325831
[TBL] [Abstract][Full Text] [Related]
5. Comparison of the ability of adeno-associated viral vectors pseudotyped with serotype 2, 5, and 8 capsid proteins to mediate efficient transduction of the liver in murine and nonhuman primate models.
Davidoff AM; Gray JT; Ng CY; Zhang Y; Zhou J; Spence Y; Bakar Y; Nathwani AC
Mol Ther; 2005 Jun; 11(6):875-88. PubMed ID: 15922958
[TBL] [Abstract][Full Text] [Related]
6. Transduction of pancreatic islets with pseudotyped adeno-associated virus: effect of viral capsid and genome conversion.
Zhang N; Clément N; Chen D; Fu S; Zhang H; Rebollo P; Linden RM; Bromberg JS
Transplantation; 2005 Sep; 80(5):683-90. PubMed ID: 16177645
[TBL] [Abstract][Full Text] [Related]
7. Utilizing minimally purified secreted rAAV for rapid and cost-effective manipulation of gene expression in the CNS.
Goodwin MS; Croft CL; Futch HS; Ryu D; Ceballos-Diaz C; Liu X; Paterno G; Mejia C; Deng D; Menezes K; Londono L; Arjona K; Parianos M; Truong V; Rostonics E; Hernandez A; Boye SL; Boye SE; Levites Y; Cruz PE; Golde TE
Mol Neurodegener; 2020 Mar; 15(1):15. PubMed ID: 32122372
[TBL] [Abstract][Full Text] [Related]
8. High-Throughput
Westhaus A; Cabanes-Creus M; Rybicki A; Baltazar G; Navarro RG; Zhu E; Drouyer M; Knight M; Albu RF; Ng BH; Kalajdzic P; Kwiatek M; Hsu K; Santilli G; Gold W; Kramer B; Gonzalez-Cordero A; Thrasher AJ; Alexander IE; Lisowski L
Hum Gene Ther; 2020 May; 31(9-10):575-589. PubMed ID: 32000541
[TBL] [Abstract][Full Text] [Related]
9. Heparan Sulfate Binding Promotes Accumulation of Intravitreally Delivered Adeno-associated Viral Vectors at the Retina for Enhanced Transduction but Weakly Influences Tropism.
Woodard KT; Liang KJ; Bennett WC; Samulski RJ
J Virol; 2016 Nov; 90(21):9878-9888. PubMed ID: 27558418
[TBL] [Abstract][Full Text] [Related]
10. Recombinant AAV viral vectors pseudotyped with viral capsids from serotypes 1, 2, and 5 display differential efficiency and cell tropism after delivery to different regions of the central nervous system.
Burger C; Gorbatyuk OS; Velardo MJ; Peden CS; Williams P; Zolotukhin S; Reier PJ; Mandel RJ; Muzyczka N
Mol Ther; 2004 Aug; 10(2):302-17. PubMed ID: 15294177
[TBL] [Abstract][Full Text] [Related]
11. Pristimerin enhances recombinant adeno-associated virus vector-mediated transgene expression in human cell lines in vitro and murine hepatocytes in vivo.
Wang LN; Wang Y; Lu Y; Yin ZF; Zhang YH; Aslanidi GV; Srivastava A; Ling CQ; Ling C
J Integr Med; 2014 Jan; 12(1):20-34. PubMed ID: 24461592
[TBL] [Abstract][Full Text] [Related]
12. Enhanced gene transfer efficiency in the murine striatum and an orthotopic glioblastoma tumor model, using AAV-7- and AAV-8-pseudotyped vectors.
Harding TC; Dickinson PJ; Roberts BN; Yendluri S; Gonzalez-Edick M; Lecouteur RA; Jooss KU
Hum Gene Ther; 2006 Aug; 17(8):807-20. PubMed ID: 16942441
[TBL] [Abstract][Full Text] [Related]
13. Characterization of the relationship of AAV capsid domain swapping to liver transduction efficiency.
Shen X; Storm T; Kay MA
Mol Ther; 2007 Nov; 15(11):1955-62. PubMed ID: 17726459
[TBL] [Abstract][Full Text] [Related]
14. Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity.
Rabinowitz JE; Rolling F; Li C; Conrath H; Xiao W; Xiao X; Samulski RJ
J Virol; 2002 Jan; 76(2):791-801. PubMed ID: 11752169
[TBL] [Abstract][Full Text] [Related]
15. Liver directed adeno-associated viral vectors to treat metabolic disease.
Chuecos MA; Lagor WR
J Inherit Metab Dis; 2024 Jan; 47(1):22-40. PubMed ID: 37254440
[TBL] [Abstract][Full Text] [Related]
16. Identification and Validation of Small Molecules That Enhance Recombinant Adeno-associated Virus Transduction following High-Throughput Screens.
Nicolson SC; Li C; Hirsch ML; Setola V; Samulski RJ
J Virol; 2016 Aug; 90(16):7019-7031. PubMed ID: 27147738
[TBL] [Abstract][Full Text] [Related]
17. Targeted modifications in adeno-associated virus serotype 8 capsid improves its hepatic gene transfer efficiency in vivo.
Sen D; Gadkari RA; Sudha G; Gabriel N; Kumar YS; Selot R; Samuel R; Rajalingam S; Ramya V; Nair SC; Srinivasan N; Srivastava A; Jayandharan GR
Hum Gene Ther Methods; 2013 Apr; 24(2):104-16. PubMed ID: 23442071
[TBL] [Abstract][Full Text] [Related]
18. Comparison of gene transfer to the murine liver following intraperitoneal and intraportal delivery of hepatotropic AAV pseudo-serotypes.
Dane AP; Wowro SJ; Cunningham SC; Alexander IE
Gene Ther; 2013 Apr; 20(4):460-4. PubMed ID: 22895507
[TBL] [Abstract][Full Text] [Related]
19. Molecular Engineering of Adeno-Associated Virus Capsid Improves Its Therapeutic Gene Transfer in Murine Models of Hemophilia and Retinal Degeneration.
Mary B; Maurya S; Kumar M; Bammidi S; Kumar V; Jayandharan GR
Mol Pharm; 2019 Nov; 16(11):4738-4750. PubMed ID: 31596095
[TBL] [Abstract][Full Text] [Related]
20. Adeno-associated virus (AAV) capsid genes isolated from rat and mouse liver genomic DNA define two new AAV species distantly related to AAV-5.
Lochrie MA; Tatsuno GP; Arbetman AE; Jones K; Pater C; Smith PH; McDonnell JW; Zhou SZ; Kachi S; Kachi M; Campochiaro PA; Pierce GF; Colosi P
Virology; 2006 Sep; 353(1):68-82. PubMed ID: 16806384
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]