246 related articles for article (PubMed ID: 24572793)
1. Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors.
Colella P; Trapani I; Cesi G; Sommella A; Manfredi A; Puppo A; Iodice C; Rossi S; Simonelli F; Giunti M; Bacci ML; Auricchio A
Gene Ther; 2014 Apr; 21(4):450-6. PubMed ID: 24572793
[TBL] [Abstract][Full Text] [Related]
2. Effective delivery of large genes to the retina by dual AAV vectors.
Trapani I; Colella P; Sommella A; Iodice C; Cesi G; de Simone S; Marrocco E; Rossi S; Giunti M; Palfi A; Farrar GJ; Polishchuk R; Auricchio A
EMBO Mol Med; 2014 Feb; 6(2):194-211. PubMed ID: 24150896
[TBL] [Abstract][Full Text] [Related]
3. Dual AAV Vectors for Stargardt Disease.
Trapani I
Methods Mol Biol; 2018; 1715():153-175. PubMed ID: 29188512
[TBL] [Abstract][Full Text] [Related]
4. Improved dual AAV vectors with reduced expression of truncated proteins are safe and effective in the retina of a mouse model of Stargardt disease.
Trapani I; Toriello E; de Simone S; Colella P; Iodice C; Polishchuk EV; Sommella A; Colecchi L; Rossi S; Simonelli F; Giunti M; Bacci ML; Polishchuk RS; Auricchio A
Hum Mol Genet; 2015 Dec; 24(23):6811-25. PubMed ID: 26420842
[TBL] [Abstract][Full Text] [Related]
5. Dual
Dyka FM; Molday LL; Chiodo VA; Molday RS; Hauswirth WW
Hum Gene Ther; 2019 Nov; 30(11):1361-1370. PubMed ID: 31418294
[TBL] [Abstract][Full Text] [Related]
6. Dual adeno-associated virus vectors result in efficient in vitro and in vivo expression of an oversized gene, MYO7A.
Dyka FM; Boye SL; Chiodo VA; Hauswirth WW; Boye SE
Hum Gene Ther Methods; 2014 Apr; 25(2):166-77. PubMed ID: 24568220
[TBL] [Abstract][Full Text] [Related]
7. Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus.
Lopes VS; Boye SE; Louie CM; Boye S; Dyka F; Chiodo V; Fofo H; Hauswirth WW; Williams DS
Gene Ther; 2013 Aug; 20(8):824-33. PubMed ID: 23344065
[TBL] [Abstract][Full Text] [Related]
8. EIAV-based retinal gene therapy in the shaker1 mouse model for usher syndrome type 1B: development of UshStat.
Zallocchi M; Binley K; Lad Y; Ellis S; Widdowson P; Iqball S; Scripps V; Kelleher M; Loader J; Miskin J; Peng YW; Wang WM; Cheung L; Delimont D; Mitrophanous KA; Cosgrove D
PLoS One; 2014; 9(4):e94272. PubMed ID: 24705452
[TBL] [Abstract][Full Text] [Related]
9. Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice.
Allocca M; Doria M; Petrillo M; Colella P; Garcia-Hoyos M; Gibbs D; Kim SR; Maguire A; Rex TS; Di Vicino U; Cutillo L; Sparrow JR; Williams DS; Bennett J; Auricchio A
J Clin Invest; 2008 May; 118(5):1955-64. PubMed ID: 18414684
[TBL] [Abstract][Full Text] [Related]
10. Assessment of different virus-mediated approaches for retinal gene therapy of Usher 1B.
Lopes VS; Diemer T; Williams DS
Adv Exp Med Biol; 2014; 801():725-31. PubMed ID: 24664764
[TBL] [Abstract][Full Text] [Related]
11. Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy.
Colella P; Sommella A; Marrocco E; Di Vicino U; Polishchuk E; Garcia Garrido M; Seeliger MW; Polishchuk R; Auricchio A
PLoS One; 2013; 8(8):e72027. PubMed ID: 23991031
[TBL] [Abstract][Full Text] [Related]
12. Single residue AAV capsid mutation improves transduction of photoreceptors in the Abca4
De Silva SR; Charbel Issa P; Singh MS; Lipinski DM; Barnea-Cramer AO; Walker NJ; Barnard AR; Hankins MW; MacLaren RE
Gene Ther; 2016 Nov; 23(11):767-774. PubMed ID: 27416076
[TBL] [Abstract][Full Text] [Related]
13. Triple Vectors Expand AAV Transfer Capacity in the Retina.
Maddalena A; Tornabene P; Tiberi P; Minopoli R; Manfredi A; Mutarelli M; Rossi S; Simonelli F; Naggert JK; Cacchiarelli D; Auricchio A
Mol Ther; 2018 Feb; 26(2):524-541. PubMed ID: 29292161
[TBL] [Abstract][Full Text] [Related]
14. Adeno-Associated Viral Vectors as a Tool for Large Gene Delivery to the Retina.
Trapani I
Genes (Basel); 2019 Apr; 10(4):. PubMed ID: 30970639
[TBL] [Abstract][Full Text] [Related]
15. An AAV Dual Vector Strategy Ameliorates the Stargardt Phenotype in Adult
McClements ME; Barnard AR; Singh MS; Charbel Issa P; Jiang Z; Radu RA; MacLaren RE
Hum Gene Ther; 2019 May; 30(5):590-600. PubMed ID: 30381971
[TBL] [Abstract][Full Text] [Related]
16. AAV-mediated photoreceptor transduction of the pig cone-enriched retina.
Mussolino C; della Corte M; Rossi S; Viola F; Di Vicino U; Marrocco E; Neglia S; Doria M; Testa F; Giovannoni R; Crasta M; Giunti M; Villani E; Lavitrano M; Bacci ML; Ratiglia R; Simonelli F; Auricchio A; Surace EM
Gene Ther; 2011 Jul; 18(7):637-45. PubMed ID: 21412286
[TBL] [Abstract][Full Text] [Related]
17. mRNA trans-splicing dual AAV vectors for (epi)genome editing and gene therapy.
Riedmayr LM; Hinrichsmeyer KS; Thalhammer SB; Mittas DM; Karguth N; Otify DY; Böhm S; Weber VJ; Bartoschek MD; Splith V; Brümmer M; Ferreira R; Boon N; Wögenstein GM; Grimm C; Wijnholds J; Mehlfeld V; Michalakis S; Fenske S; Biel M; Becirovic E
Nat Commun; 2023 Oct; 14(1):6578. PubMed ID: 37852949
[TBL] [Abstract][Full Text] [Related]
18. Recombinant vectors based on porcine adeno-associated viral serotypes transduce the murine and pig retina.
Puppo A; Bello A; Manfredi A; Cesi G; Marrocco E; Della Corte M; Rossi S; Giunti M; Bacci ML; Simonelli F; Surace EM; Kobinger GP; Auricchio A
PLoS One; 2013; 8(3):e59025. PubMed ID: 23520549
[TBL] [Abstract][Full Text] [Related]
19. Assessment of AAV Dual Vector Safety in the
McClements ME; Barnard AR; Charbel Issa P; MacLaren RE
Transl Vis Sci Technol; 2020 Jun; 9(7):20. PubMed ID: 32724727
[TBL] [Abstract][Full Text] [Related]
20. High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction In Vitro and in Mouse Retina.
Maddalena A; Dell'Aquila F; Giovannelli P; Tiberi P; Wanderlingh LG; Montefusco S; Tornabene P; Iodice C; Visconte F; Carissimo A; Medina DL; Castoria G; Auricchio A
Hum Gene Ther; 2018 Aug; 29(8):886-901. PubMed ID: 29641320
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]