505 related articles for article (PubMed ID: 24622513)
21. Evidence for long-term efficacy and safety of gene therapy for Wiskott-Aldrich syndrome in preclinical models.
Marangoni F; Bosticardo M; Charrier S; Draghici E; Locci M; Scaramuzza S; Panaroni C; Ponzoni M; Sanvito F; Doglioni C; Liabeuf M; Gjata B; Montus M; Siminovitch K; Aiuti A; Naldini L; Dupré L; Roncarolo MG; Galy A; Villa A
Mol Ther; 2009 Jun; 17(6):1073-82. PubMed ID: 19259069
[TBL] [Abstract][Full Text] [Related]
22. Hematopoietic-specific lentiviral vectors circumvent cellular toxicity due to ectopic expression of Wiskott-Aldrich syndrome protein.
Toscano MG; Frecha C; Benabdellah K; Cobo M; Blundell M; Thrasher AJ; García-Olivares E; Molina IJ; Martin F
Hum Gene Ther; 2008 Feb; 19(2):179-97. PubMed ID: 18240968
[TBL] [Abstract][Full Text] [Related]
23. Expression of human Wiskott-Aldrich syndrome protein in patients' cells leads to partial correction of a phenotypic abnormality of cell surface glycoproteins.
Huang MM; Tsuboi S; Wong A; Yu XJ; Oh-Eda M; Derry JM; Francke U; Fukuda M; Weinberg KI; Kohn DB
Gene Ther; 2000 Feb; 7(4):314-20. PubMed ID: 10694812
[TBL] [Abstract][Full Text] [Related]
24. Gene Correction of iPSCs from a Wiskott-Aldrich Syndrome Patient Normalizes the Lymphoid Developmental and Functional Defects.
Laskowski TJ; Van Caeneghem Y; Pourebrahim R; Ma C; Ni Z; Garate Z; Crane AM; Li XS; Liao W; Gonzalez-Garay M; Segovia JC; Paschon DE; Rebar EJ; Holmes MC; Kaufman D; Vandekerckhove B; Davis BR
Stem Cell Reports; 2016 Aug; 7(2):139-48. PubMed ID: 27396937
[TBL] [Abstract][Full Text] [Related]
25. The genotype of the original Wiskott phenotype.
Binder V; Albert MH; Kabus M; Bertone M; Meindl A; Belohradsky BH
N Engl J Med; 2006 Oct; 355(17):1790-3. PubMed ID: 17065640
[TBL] [Abstract][Full Text] [Related]
26. Comparison of insulators and promoters for expression of the Wiskott-Aldrich syndrome protein using lentiviral vectors.
Koldej RM; Carney G; Wielgosz MM; Zhou S; Zhan J; Sorrentino BP; Nienhuis AW
Hum Gene Ther Clin Dev; 2013 Jun; 24(2):77-85. PubMed ID: 23786330
[TBL] [Abstract][Full Text] [Related]
27. Improved lentiviral vectors for Wiskott-Aldrich syndrome gene therapy mimic endogenous expression profiles throughout haematopoiesis.
Frecha C; Toscano MG; Costa C; Saez-Lara MJ; Cosset FL; Verhoeyen E; Martin F
Gene Ther; 2008 Jun; 15(12):930-41. PubMed ID: 18323794
[TBL] [Abstract][Full Text] [Related]
28. Defects in T-cell-mediated immunity to influenza virus in murine Wiskott-Aldrich syndrome are corrected by oncoretroviral vector-mediated gene transfer into repopulating hematopoietic cells.
Strom TS; Turner SJ; Andreansky S; Liu H; Doherty PC; Srivastava DK; Cunningham JM; Nienhuis AW
Blood; 2003 Nov; 102(9):3108-16. PubMed ID: 12855574
[TBL] [Abstract][Full Text] [Related]
29. A lentiviral vector encoding the human Wiskott-Aldrich syndrome protein corrects immune and cytoskeletal defects in WASP knockout mice.
Charrier S; Stockholm D; Seye K; Opolon P; Taveau M; Gross DA; Bucher-Laurent S; Delenda C; Vainchenker W; Danos O; Galy A
Gene Ther; 2005 Apr; 12(7):597-606. PubMed ID: 15616597
[TBL] [Abstract][Full Text] [Related]
30. Clinical aspects and molecular analysis of Chinese patients with Wiskott-Aldrich syndrome in Taiwan.
Lee WI; Yang CY; Jaing TH; Huang JL; Chien YH; Chang KW
Int Arch Allergy Immunol; 2008; 145(1):15-23. PubMed ID: 17703096
[TBL] [Abstract][Full Text] [Related]
31. Lentiviral-mediated gene therapy leads to improvement of B-cell functionality in a murine model of Wiskott-Aldrich syndrome.
Bosticardo M; Draghici E; Schena F; Sauer AV; Fontana E; Castiello MC; Catucci M; Locci M; Naldini L; Aiuti A; Roncarolo MG; Poliani PL; Traggiai E; Villa A
J Allergy Clin Immunol; 2011 Jun; 127(6):1376-84.e5. PubMed ID: 21531013
[TBL] [Abstract][Full Text] [Related]
32. Mixed chimera status of 12 patients with Wiskott-Aldrich syndrome (WAS) after hematopoietic stem cell transplantation: evaluation by flow cytometric analysis of intracellular WAS protein expression.
Yamaguchi K; Ariga T; Yamada M; Nelson DL; Kobayashi R; Kobayashi C; Noguchi Y; Ito Y; Katamura K; Nagatoshi Y; Kondo S; Katoh H; Sakiyama Y
Blood; 2002 Aug; 100(4):1208-14. PubMed ID: 12149199
[TBL] [Abstract][Full Text] [Related]
33. Ten years of gene therapy for primary immune deficiencies.
Aiuti A; Roncarolo MG
Hematology Am Soc Hematol Educ Program; 2009; ():682-9. PubMed ID: 20008254
[TBL] [Abstract][Full Text] [Related]
34. Broadening the indications for hematopoietic stem cell genetic therapies.
Williams DA
Cell Stem Cell; 2013 Sep; 13(3):263-4. PubMed ID: 24012366
[TBL] [Abstract][Full Text] [Related]
35. [Wiskott-Aldrich syndrome].
Gulácsy V; Maródi L
Orv Hetil; 2008 Jul; 149(29):1367-71. PubMed ID: 18617469
[TBL] [Abstract][Full Text] [Related]
36. Dendritic cell functional improvement in a preclinical model of lentiviral-mediated gene therapy for Wiskott-Aldrich syndrome.
Catucci M; Prete F; Bosticardo M; Castiello MC; Draghici E; Locci M; Roncarolo MG; Aiuti A; Benvenuti F; Villa A
Gene Ther; 2012 Dec; 19(12):1150-8. PubMed ID: 22189416
[TBL] [Abstract][Full Text] [Related]
37. Wiskott-Aldrich syndrome; an x-linked primary immunodeficiency disease with unique and characteristic features.
Ariga T
Allergol Int; 2012 Jun; 61(2):183-9. PubMed ID: 22361515
[TBL] [Abstract][Full Text] [Related]
38. Wiskott-Aldrich syndrome: diagnosis, clinical and laboratory manifestations, and treatment.
Ochs HD; Filipovich AH; Veys P; Cowan MJ; Kapoor N
Biol Blood Marrow Transplant; 2009 Jan; 15(1 Suppl):84-90. PubMed ID: 19147084
[TBL] [Abstract][Full Text] [Related]
39. Hematopoietic stem cell transplantation for X-linked thrombocytopenia from a mild symptomatic carrier.
Okuya M; Kurosawa H; Kubota T; Endoh K; Ogiwara A; Nonoyama S; Hagisawa S; Sato Y; Matsushita T; Fukushima K; Sugita K; Sato T; Arisaka O
Bone Marrow Transplant; 2010 Mar; 45(3):607-9. PubMed ID: 19684625
[No Abstract] [Full Text] [Related]
40. Multiple independent second-site mutations in two siblings with somatic mosaicism for Wiskott-Aldrich syndrome.
Boztug K; Germeshausen M; Avedillo Díez I; Gulacsy V; Diestelhorst J; Ballmaier M; Welte K; Maródi L; Chernyshova L; Klein C
Clin Genet; 2008 Jul; 74(1):68-74. PubMed ID: 18479478
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]
