These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
7. Molecular Engineering of Adeno-Associated Virus Capsid Improves Its Therapeutic Gene Transfer in Murine Models of Hemophilia and Retinal Degeneration. Mary B; Maurya S; Kumar M; Bammidi S; Kumar V; Jayandharan GR Mol Pharm; 2019 Nov; 16(11):4738-4750. PubMed ID: 31596095 [TBL] [Abstract][Full Text] [Related]
8. Directed evolution of adeno-associated virus (AAV) as vector for muscle gene therapy. Yang L; Li J; Xiao X Methods Mol Biol; 2011; 709():127-39. PubMed ID: 21194025 [TBL] [Abstract][Full Text] [Related]
9. Adeno-associated virus as a gene therapy vector: strategies to neutralize the neutralizing antibodies. Lotfinia M; Abdollahpour-Alitappeh M; Hatami B; Zali MR; Karimipoor M Clin Exp Med; 2019 Aug; 19(3):289-298. PubMed ID: 31054018 [TBL] [Abstract][Full Text] [Related]
10. AAV-Mediated Gene Delivery to the Liver: Overview of Current Technologies and Methods. Palaschak B; Herzog RW; Markusic DM Methods Mol Biol; 2019; 1950():333-360. PubMed ID: 30783984 [TBL] [Abstract][Full Text] [Related]
11. Computationally guided AAV engineering for enhanced gene delivery. Guo J; Lin LF; Oraskovich SV; Rivera de Jesús JA; Listgarten J; Schaffer DV Trends Biochem Sci; 2024 May; 49(5):457-469. PubMed ID: 38531696 [TBL] [Abstract][Full Text] [Related]
12. Small But Increasingly Mighty: Latest Advances in AAV Vector Research, Design, and Evolution. Grimm D; Büning H Hum Gene Ther; 2017 Nov; 28(11):1075-1086. PubMed ID: 28835125 [TBL] [Abstract][Full Text] [Related]
13. Recombinant adeno-associated virus as delivery vector for gene therapy--a review. Lu Y Stem Cells Dev; 2004 Feb; 13(1):133-45. PubMed ID: 15068701 [TBL] [Abstract][Full Text] [Related]
14. Advances in gene therapy for hemophilia: basis, current status, and future perspectives. Ohmori T Int J Hematol; 2020 Jan; 111(1):31-41. PubMed ID: 30083852 [TBL] [Abstract][Full Text] [Related]
15. Designer gene delivery vectors: molecular engineering and evolution of adeno-associated viral vectors for enhanced gene transfer. Kwon I; Schaffer DV Pharm Res; 2008 Mar; 25(3):489-99. PubMed ID: 17763830 [TBL] [Abstract][Full Text] [Related]
16. Viral Vectors for Gene Therapy: Translational and Clinical Outlook. Kotterman MA; Chalberg TW; Schaffer DV Annu Rev Biomed Eng; 2015; 17():63-89. PubMed ID: 26643018 [TBL] [Abstract][Full Text] [Related]
17. AAV-mediated gene transfer for hemophilia. High KA Ann N Y Acad Sci; 2001 Dec; 953():64-74. PubMed ID: 11795424 [TBL] [Abstract][Full Text] [Related]
18. Machine-learning-guided Directed Evolution for AAV Capsid Engineering. Fu X; Suo H; Zhang J; Chen D Curr Pharm Des; 2024; 30(11):811-824. PubMed ID: 38445704 [TBL] [Abstract][Full Text] [Related]
19. Hemophilia gene therapy: ushering in a new treatment paradigm? George LA Hematology Am Soc Hematol Educ Program; 2021 Dec; 2021(1):226-233. PubMed ID: 34889378 [TBL] [Abstract][Full Text] [Related]
20. New approaches to gene and cell therapy for hemophilia. Ohmori T; Mizukami H; Ozawa K; Sakata Y; Nishimura S J Thromb Haemost; 2015 Jun; 13 Suppl 1():S133-42. PubMed ID: 26149014 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]