BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

188 related articles for article (PubMed ID: 25842973)

  • 1. Clinical translation of TALENS: Treating SCID-X1 by gene editing in iPSCs.
    Biffi A
    Cell Stem Cell; 2015 Apr; 16(4):348-9. PubMed ID: 25842973
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Lymphoid regeneration from gene-corrected SCID-X1 subject-derived iPSCs.
    Menon T; Firth AL; Scripture-Adams DD; Galic Z; Qualls SJ; Gilmore WB; Ke E; Singer O; Anderson LS; Bornzin AR; Alexander IE; Zack JA; Verma IM
    Cell Stem Cell; 2015 Apr; 16(4):367-72. PubMed ID: 25772073
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency.
    De Ravin SS; Wu X; Moir S; Anaya-O'Brien S; Kwatemaa N; Littel P; Theobald N; Choi U; Su L; Marquesen M; Hilligoss D; Lee J; Buckner CM; Zarember KA; O'Connor G; McVicar D; Kuhns D; Throm RE; Zhou S; Notarangelo LD; Hanson IC; Cowan MJ; Kang E; Hadigan C; Meagher M; Gray JT; Sorrentino BP; Malech HL; Kardava L
    Sci Transl Med; 2016 Apr; 8(335):335ra57. PubMed ID: 27099176
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Restoring T and B cell generation in X-linked severe combined immunodeficiency mice through hematopoietic stem cells adenine base editing.
    Zhang L; Li K; Liu Z; An L; Wei H; Pang S; Cao Z; Huang X; Jin X; Ma X
    Mol Ther; 2024 Jun; 32(6):1658-1671. PubMed ID: 38532630
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1.
    Mamcarz E; Zhou S; Lockey T; Abdelsamed H; Cross SJ; Kang G; Ma Z; Condori J; Dowdy J; Triplett B; Li C; Maron G; Aldave Becerra JC; Church JA; Dokmeci E; Love JT; da Matta Ain AC; van der Watt H; Tang X; Janssen W; Ryu BY; De Ravin SS; Weiss MJ; Youngblood B; Long-Boyle JR; Gottschalk S; Meagher MM; Malech HL; Puck JM; Cowan MJ; Sorrentino BP
    N Engl J Med; 2019 Apr; 380(16):1525-1534. PubMed ID: 30995372
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Targeted genome editing restores T cell differentiation in a humanized X-SCID pluripotent stem cell disease model.
    Alzubi J; Pallant C; Mussolino C; Howe SJ; Thrasher AJ; Cathomen T
    Sci Rep; 2017 Sep; 7(1):12475. PubMed ID: 28963568
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency.
    Gaspar HB; Cooray S; Gilmour KC; Parsley KL; Adams S; Howe SJ; Al Ghonaium A; Bayford J; Brown L; Davies EG; Kinnon C; Thrasher AJ
    Sci Transl Med; 2011 Aug; 3(97):97ra79. PubMed ID: 21865537
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Gene therapy model of X-linked severe combined immunodeficiency using a modified foamy virus vector.
    Horino S; Uchiyama T; So T; Nagashima H; Sun SL; Sato M; Asao A; Haji Y; Sasahara Y; Candotti F; Tsuchiya S; Kure S; Sugamura K; Ishii N
    PLoS One; 2013; 8(8):e71594. PubMed ID: 23990961
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?
    Cavazzana M; Six E; Lagresle-Peyrou C; André-Schmutz I; Hacein-Bey-Abina S
    Hum Gene Ther; 2016 Feb; 27(2):108-16. PubMed ID: 26790362
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Self-inactivating gammaretroviral vectors for gene therapy of X-linked severe combined immunodeficiency.
    Thornhill SI; Schambach A; Howe SJ; Ulaganathan M; Grassman E; Williams D; Schiedlmeier B; Sebire NJ; Gaspar HB; Kinnon C; Baum C; Thrasher AJ
    Mol Ther; 2008 Mar; 16(3):590-8. PubMed ID: 18180772
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Advancing gene targeting for primary immune deficiencies: Adenine base editing of the human IL2RG locus for correction of SCID-X1.
    McIvor RS; Eaton EJ; Webber BR; Moriarity BS
    Mol Ther; 2024 Jun; 32(6):1606-1608. PubMed ID: 38781958
    [No Abstract]   [Full Text] [Related]  

  • 12. Gene therapy outpaces haplo for SCID-X1.
    Kohn DB
    Blood; 2015 Jun; 125(23):3521-2. PubMed ID: 26045591
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Gene correction in patient-specific iPSCs for therapy development and disease modeling.
    Jang YY; Ye Z
    Hum Genet; 2016 Sep; 135(9):1041-58. PubMed ID: 27256364
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Gene therapy for severe combined immunodeficiencies and beyond.
    Fischer A; Hacein-Bey-Abina S
    J Exp Med; 2020 Jan; 217(2):. PubMed ID: 31826240
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Intravenous injection of a foamy virus vector to correct canine SCID-X1.
    Burtner CR; Beard BC; Kennedy DR; Wohlfahrt ME; Adair JE; Trobridge GD; Scharenberg AM; Torgerson TR; Rawlings DJ; Felsburg PJ; Kiem HP
    Blood; 2014 Jun; 123(23):3578-84. PubMed ID: 24642749
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Gene therapy for primary immunodeficiencies: Part 1.
    Cavazzana-Calvo M; Fischer A; Hacein-Bey-Abina S; Aiuti A
    Curr Opin Immunol; 2012 Oct; 24(5):580-4. PubMed ID: 22981681
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Immune Reconstitution After Gene Therapy Approaches in Patients With X-Linked Severe Combined Immunodeficiency Disease.
    Blanco E; Izotova N; Booth C; Thrasher AJ
    Front Immunol; 2020; 11():608653. PubMed ID: 33329605
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Treatment of an infant with X-linked severe combined immunodeficiency (SCID-X1) by gene therapy in Australia.
    Ginn SL; Curtin JA; Kramer B; Smyth CM; Wong M; Kakakios A; McCowage GB; Watson D; Alexander SI; Latham M; Cunningham SC; Zheng M; Hobson L; Rowe PB; Fischer A; Cavazzana-Calvo M; Hacein-Bey-Abina S; Alexander IE
    Med J Aust; 2005 May; 182(9):458-63. PubMed ID: 15865589
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Faster T-cell development following gene therapy compared with haploidentical HSCT in the treatment of SCID-X1.
    Touzot F; Moshous D; Creidy R; Neven B; Frange P; Cros G; Caccavelli L; Blondeau J; Magnani A; Luby JM; Ternaux B; Picard C; Blanche S; Fischer A; Hacein-Bey-Abina S; Cavazzana M
    Blood; 2015 Jun; 125(23):3563-9. PubMed ID: 25869287
    [TBL] [Abstract][Full Text] [Related]  

  • 20. T cell dynamics and response of the microbiota after gene therapy to treat X-linked severe combined immunodeficiency.
    Clarke EL; Connell AJ; Six E; Kadry NA; Abbas AA; Hwang Y; Everett JK; Hofstaedter CE; Marsh R; Armant M; Kelsen J; Notarangelo LD; Collman RG; Hacein-Bey-Abina S; Kohn DB; Cavazzana M; Fischer A; Williams DA; Pai SY; Bushman FD
    Genome Med; 2018 Sep; 10(1):70. PubMed ID: 30261899
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 10.