These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
266 related articles for article (PubMed ID: 26011400)
1. Modeling correction of severe urea cycle defects in the growing murine liver using a hybrid recombinant adeno-associated virus/piggyBac transposase gene delivery system. Cunningham SC; Siew SM; Hallwirth CV; Bolitho C; Sasaki N; Garg G; Michael IP; Hetherington NA; Carpenter K; de Alencastro G; Nagy A; Alexander IE Hepatology; 2015 Aug; 62(2):417-28. PubMed ID: 26011400 [TBL] [Abstract][Full Text] [Related]
2. AAV-encoded OTC activity persisting to adulthood following delivery to newborn spf(ash) mice is insufficient to prevent shRNA-induced hyperammonaemia. Cunningham SC; Kok CY; Spinoulas A; Carpenter KH; Alexander IE Gene Ther; 2013 Dec; 20(12):1184-7. PubMed ID: 24108150 [TBL] [Abstract][Full Text] [Related]
3. Stable transduction of the neonatal mouse liver using a hybrid rAAV/sleeping beauty transposon gene delivery system. Cunningham SC; Zakas PM; Sasaki N; van Dijk EB; Zhu E; Fu Y; Salomon WE; Citorik RJ; Rubens JR; Cotta-Ramusino C; Querbes W; Alexander IE J Gene Med; 2024 Aug; 26(8):e3726. PubMed ID: 39160647 [TBL] [Abstract][Full Text] [Related]
4. Prevention of Cholestatic Liver Disease and Reduced Tumorigenicity in a Murine Model of PFIC Type 3 Using Hybrid AAV-piggyBac Gene Therapy. Siew SM; Cunningham SC; Zhu E; Tay SS; Venuti E; Bolitho C; Alexander IE Hepatology; 2019 Dec; 70(6):2047-2061. PubMed ID: 31099022 [TBL] [Abstract][Full Text] [Related]
5. Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency. Zakas PM; Cunningham SC; Doherty A; van Dijk EB; Ibraheim R; Yu S; Mekonnen BD; Lang B; English EJ; Sun G; Duncan MC; Benczkowski MS; Altshuler RC; Singh MJ; Kibbler ES; Tonga GY; Wang ZJ; Wang ZJ; Li G; An D; Rottman JB; Bhavsar Y; Purcell C; Jain R; Alberry R; Roquet N; Fu Y; Citorik RJ; Rubens JR; Holmes MC; Cotta-Ramusino C; Querbes W; Alexander IE; Salomon WE Mol Ther; 2024 Oct; 32(10):3356-3371. PubMed ID: 38981468 [TBL] [Abstract][Full Text] [Related]
6. Induction and prevention of severe hyperammonemia in the spfash mouse model of ornithine transcarbamylase deficiency using shRNA and rAAV-mediated gene delivery. Cunningham SC; Kok CY; Dane AP; Carpenter K; Kizana E; Kuchel PW; Alexander IE Mol Ther; 2011 May; 19(5):854-9. PubMed ID: 21386824 [TBL] [Abstract][Full Text] [Related]
7. Correction of ornithine transcarbamylase deficiency in adult spf(ash) mice and in OTC-deficient human hepatocytes with recombinant adenoviruses bearing the CAG promoter. Kiwaki K; Kanegae Y; Saito I; Komaki S; Nakamura K; Miyazaki JI; Endo F; Matsuda I Hum Gene Ther; 1996 May; 7(7):821-30. PubMed ID: 8860834 [TBL] [Abstract][Full Text] [Related]
8. Hybrid nonviral/viral vector systems for improved piggyBac DNA transposon in vivo delivery. Cooney AL; Singh BK; Sinn PL Mol Ther; 2015 Apr; 23(4):667-74. PubMed ID: 25557623 [TBL] [Abstract][Full Text] [Related]
9. Adeno-associated virus-mediated rescue of neonatal lethality in argininosuccinate synthetase-deficient mice. Kok CY; Cunningham SC; Carpenter KH; Dane AP; Siew SM; Logan GJ; Kuchel PW; Alexander IE Mol Ther; 2013 Oct; 21(10):1823-31. PubMed ID: 23817206 [TBL] [Abstract][Full Text] [Related]
10. Transposition from a gutless adeno-transposon vector stabilizes transgene expression in vivo. Yant SR; Ehrhardt A; Mikkelsen JG; Meuse L; Pham T; Kay MA Nat Biotechnol; 2002 Oct; 20(10):999-1005. PubMed ID: 12244327 [TBL] [Abstract][Full Text] [Related]
11. Gene delivery to the juvenile mouse liver using AAV2/8 vectors. Cunningham SC; Dane AP; Spinoulas A; Logan GJ; Alexander IE Mol Ther; 2008 Jun; 16(6):1081-8. PubMed ID: 18414478 [TBL] [Abstract][Full Text] [Related]
12. Gene therapy methods in bone and joint disorders. Evaluation of the adeno-associated virus vector in experimental models of articular cartilage disorders, periprosthetic osteolysis and bone healing. Ulrich-Vinther M Acta Orthop Suppl; 2007 Apr; 78(325):1-64. PubMed ID: 17427340 [TBL] [Abstract][Full Text] [Related]
13. AAV2/8-mediated correction of OTC deficiency is robust in adult but not neonatal Spf(ash) mice. Cunningham SC; Spinoulas A; Carpenter KH; Wilcken B; Kuchel PW; Alexander IE Mol Ther; 2009 Aug; 17(8):1340-6. PubMed ID: 19384294 [TBL] [Abstract][Full Text] [Related]
14. Stable therapeutic serum levels of human alpha-1 antitrypsin (AAT) after portal vein injection of recombinant adeno-associated virus (rAAV) vectors. Song S; Embury J; Laipis PJ; Berns KI; Crawford JM; Flotte TR Gene Ther; 2001 Sep; 8(17):1299-306. PubMed ID: 11571566 [TBL] [Abstract][Full Text] [Related]
15. Development of adenovirus hybrid vectors for Sleeping Beauty transposition in large mammals. Hausl M; Zhang W; Voigtländer R; Müther N; Rauschhuber C; Ehrhardt A Curr Gene Ther; 2011 Oct; 11(5):363-74. PubMed ID: 21888620 [TBL] [Abstract][Full Text] [Related]
16. Efficient gene transfer into human cord blood CD34+ cells and the CD34+CD38- subset using highly purified recombinant adeno-associated viral vector preparations that are free of helper virus and wild-type AAV. Nathwani AC; Hanawa H; Vandergriff J; Kelly P; Vanin EF; Nienhuis AW Gene Ther; 2000 Feb; 7(3):183-95. PubMed ID: 10694794 [TBL] [Abstract][Full Text] [Related]
17. Practical considerations of recombinant adeno-associated virus-mediated gene transfer for treatment of retinal degenerations. Shen WY; Lai CM; Lai YK; Zhang D; Zaknich T; Sutanto EN; Constable IJ; Rakoczy PE J Gene Med; 2003 Jul; 5(7):576-87. PubMed ID: 12825197 [TBL] [Abstract][Full Text] [Related]
18. Gene transfer into the CNS using recombinant adeno-associated virus: analysis of vector DNA forms resulting in sustained expression. Clark KR; Sferra TJ; Lo W; Qu G; Chen R; Johnson PR J Drug Target; 1999 Dec; 7(4):269-83. PubMed ID: 10682906 [TBL] [Abstract][Full Text] [Related]
19. Development of recombinant adeno-associated virus and adenovirus cocktail system for efficient hTERTC27 polypeptide-mediated cancer gene therapy. Gao Y; Ng SS; Chau DH; Yao H; Yang C; Man K; Huang PT; Huang C; Huang JJ; Kung HF; Lin MC Cancer Gene Ther; 2008 Nov; 15(11):723-32. PubMed ID: 18535618 [TBL] [Abstract][Full Text] [Related]
20. Adeno-associated viral gene therapy corrects a mouse model of argininosuccinic aciduria. Ashley SN; Nordin JML; Buza EL; Greig JA; Wilson JM Mol Genet Metab; 2018 Nov; 125(3):241-250. PubMed ID: 30253962 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]