432 related articles for article (PubMed ID: 26061647)
1. Arylsulfatase A Overexpressing Human iPSC-derived Neural Cells Reduce CNS Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy.
Doerr J; Böckenhoff A; Ewald B; Ladewig J; Eckhardt M; Gieselmann V; Matzner U; Brüstle O; Koch P
Mol Ther; 2015 Sep; 23(9):1519-31. PubMed ID: 26061647
[TBL] [Abstract][Full Text] [Related]
2. Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy.
Meneghini V; Frati G; Sala D; De Cicco S; Luciani M; Cavazzin C; Paulis M; Mentzen W; Morena F; Giannelli S; Sanvito F; Villa A; Bulfone A; Broccoli V; Martino S; Gritti A
Stem Cells Transl Med; 2017 Feb; 6(2):352-368. PubMed ID: 28191778
[TBL] [Abstract][Full Text] [Related]
3. Embryonic stem cell-based reduction of central nervous system sulfatide storage in an animal model of metachromatic leukodystrophy.
Klein D; Schmandt T; Muth-Köhne E; Perez-Bouza A; Segschneider M; Gieselmann V; Brüstle O
Gene Ther; 2006 Dec; 13(24):1686-95. PubMed ID: 16871228
[TBL] [Abstract][Full Text] [Related]
4. Human iPSC-based models highlight defective glial and neuronal differentiation from neural progenitor cells in metachromatic leukodystrophy.
Frati G; Luciani M; Meneghini V; De Cicco S; Ståhlman M; Blomqvist M; Grossi S; Filocamo M; Morena F; Menegon A; Martino S; Gritti A
Cell Death Dis; 2018 Jun; 9(6):698. PubMed ID: 29899471
[TBL] [Abstract][Full Text] [Related]
5. Partial cure of established disease in an animal model of metachromatic leukodystrophy after intracerebral adeno-associated virus-mediated gene transfer.
Sevin C; Verot L; Benraiss A; Van Dam D; Bonnin D; Nagels G; Fouquet F; Gieselmann V; Vanier MT; De Deyn PP; Aubourg P; Cartier N
Gene Ther; 2007 Mar; 14(5):405-14. PubMed ID: 17093507
[TBL] [Abstract][Full Text] [Related]
6. Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice.
Piguet F; Sondhi D; Piraud M; Fouquet F; Hackett NR; Ahouansou O; Vanier MT; Bieche I; Aubourg P; Crystal RG; Cartier N; Sevin C
Hum Gene Ther; 2012 Aug; 23(8):903-14. PubMed ID: 22642214
[TBL] [Abstract][Full Text] [Related]
7. Safety of arylsulfatase A overexpression for gene therapy of metachromatic leukodystrophy.
Capotondo A; Cesani M; Pepe S; Fasano S; Gregori S; Tononi L; Venneri MA; Brambilla R; Quattrini A; Ballabio A; Cosma MP; Naldini L; Biffi A
Hum Gene Ther; 2007 Sep; 18(9):821-36. PubMed ID: 17845130
[TBL] [Abstract][Full Text] [Related]
8. Increasing sulfatide synthesis in myelin-forming cells of arylsulfatase A-deficient mice causes demyelination and neurological symptoms reminiscent of human metachromatic leukodystrophy.
Ramakrishnan H; Hedayati KK; Lüllmann-Rauch R; Wessig C; Fewou SN; Maier H; Goebel HH; Gieselmann V; Eckhardt M
J Neurosci; 2007 Aug; 27(35):9482-90. PubMed ID: 17728461
[TBL] [Abstract][Full Text] [Related]
9. Axons mediate the distribution of arylsulfatase A within the mouse hippocampus upon gene delivery.
Luca T; Givogri MI; Perani L; Galbiati F; Follenzi A; Naldini L; Bongarzone ER
Mol Ther; 2005 Oct; 12(4):669-79. PubMed ID: 16087406
[TBL] [Abstract][Full Text] [Related]
10. Lysosomal sulfatide storage in the brain of arylsulfatase A-deficient mice: cellular alterations and topographic distribution.
Wittke D; Hartmann D; Gieselmann V; Lüllmann-Rauch R
Acta Neuropathol; 2004 Oct; 108(4):261-71. PubMed ID: 15322834
[TBL] [Abstract][Full Text] [Related]
11. Oligodendroglial progenitor cell therapy limits central neurological deficits in mice with metachromatic leukodystrophy.
Givogri MI; Galbiati F; Fasano S; Amadio S; Perani L; Superchi D; Morana P; Del Carro U; Marchesini S; Brambilla R; Wrabetz L; Bongarzone E
J Neurosci; 2006 Mar; 26(12):3109-19. PubMed ID: 16554462
[TBL] [Abstract][Full Text] [Related]
12. Microglia: a cellular vehicle for CNS gene therapy.
Neumann H
J Clin Invest; 2006 Nov; 116(11):2857-60. PubMed ID: 17080190
[TBL] [Abstract][Full Text] [Related]
13. Ex vivo cell-mediated gene therapy for metachromatic leukodystrophy using neurospheres.
Kawabata K; Migita M; Mochizuki H; Miyake K; Igarashi T; Fukunaga Y; Shimada T
Brain Res; 2006 Jun; 1094(1):13-23. PubMed ID: 16729983
[TBL] [Abstract][Full Text] [Related]
14. Treatment of adult metachromatic leukodystrophy model mice using intrathecal administration of type 9 AAV vector encoding arylsulfatase A.
Miyake N; Miyake K; Sakai A; Yamamoto M; Suzuki H; Shimada T
Sci Rep; 2021 Oct; 11(1):20513. PubMed ID: 34654893
[TBL] [Abstract][Full Text] [Related]
15. [Pathophysiology of sulfatide metabolism in metachromatic leukodystrophy].
Wiesmann UN
Bull Schweiz Akad Med Wiss; 1978 Mar; 34(1-3):33-47. PubMed ID: 27269
[TBL] [Abstract][Full Text] [Related]
16. Bone marrow stem cell-based gene transfer in a mouse model for metachromatic leukodystrophy: effects on visceral and nervous system disease manifestations.
Matzner U; Hartmann D; Lüllmann-Rauch R; Coenen R; Rothert F; Månsson JE; Fredman P; D'Hooge R; De Deyn PP; Gieselmann V
Gene Ther; 2002 Jan; 9(1):53-63. PubMed ID: 11850723
[TBL] [Abstract][Full Text] [Related]
17. Gene therapy of metachromatic leukodystrophy reverses neurological damage and deficits in mice.
Biffi A; Capotondo A; Fasano S; del Carro U; Marchesini S; Azuma H; Malaguti MC; Amadio S; Brambilla R; Grompe M; Bordignon C; Quattrini A; Naldini L
J Clin Invest; 2006 Nov; 116(11):3070-82. PubMed ID: 17080200
[TBL] [Abstract][Full Text] [Related]
18. Olaparib Attenuates Demyelination and Neuroinflammation in an Organotypic Slice Culture Model of Metachromatic Leukodystrophy.
Mekhaeil M; Conroy MJ; Dev KK
Neurotherapeutics; 2023 Sep; 20(5):1347-1368. PubMed ID: 37525026
[TBL] [Abstract][Full Text] [Related]
19. Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy.
Sevin C; Benraiss A; Van Dam D; Bonnin D; Nagels G; Verot L; Laurendeau I; Vidaud M; Gieselmann V; Vanier M; De Deyn PP; Aubourg P; Cartier N
Hum Mol Genet; 2006 Jan; 15(1):53-64. PubMed ID: 16311251
[TBL] [Abstract][Full Text] [Related]
20. Metabolic correction in oligodendrocytes derived from metachromatic leukodystrophy mouse model by using encapsulated recombinant myoblasts.
Consiglio A; Martino S; Dolcetta D; Cusella G; Conese M; Marchesini S; Benaglia G; Wrabetz L; Orlacchio A; Déglon N; Aebischer P; Severini GM; Bordignon C
J Neurol Sci; 2007 Apr; 255(1-2):7-16. PubMed ID: 17341424
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
