298 related articles for article (PubMed ID: 26245762)
1. Long-term outcomes after allogeneic hematopoietic stem cell transplantation for metachromatic leukodystrophy: the largest single-institution cohort report.
Boucher AA; Miller W; Shanley R; Ziegler R; Lund T; Raymond G; Orchard PJ
Orphanet J Rare Dis; 2015 Aug; 10():94. PubMed ID: 26245762
[TBL] [Abstract][Full Text] [Related]
2. Long-term Outcome of Allogeneic Hematopoietic Stem Cell Transplantation in Patients With Juvenile Metachromatic Leukodystrophy Compared With Nontransplanted Control Patients.
Groeschel S; Kühl JS; Bley AE; Kehrer C; Weschke B; Döring M; Böhringer J; Schrum J; Santer R; Kohlschütter A; Krägeloh-Mann I; Müller I
JAMA Neurol; 2016 Sep; 73(9):1133-40. PubMed ID: 27400410
[TBL] [Abstract][Full Text] [Related]
3. Neurodevelopmental outcomes of umbilical cord blood transplantation in metachromatic leukodystrophy.
Martin HR; Poe MD; Provenzale JM; Kurtzberg J; Mendizabal A; Escolar ML
Biol Blood Marrow Transplant; 2013 Apr; 19(4):616-24. PubMed ID: 23348427
[TBL] [Abstract][Full Text] [Related]
4. Hematopoietic Stem Cell Transplantation with Mesenchymal Stromal Cells in Children with Metachromatic Leukodystrophy.
Cabanillas Stanchi KM; Böhringer J; Strölin M; Groeschel S; Lenglinger K; Treuner C; Kehrer C; Laugwitz L; Bevot A; Kaiser N; Schumm M; Lang P; Handgretinger R; Krägeloh-Mann I; Müller I; Döring M
Stem Cells Dev; 2022 Apr; 31(7-8):163-175. PubMed ID: 35323019
[TBL] [Abstract][Full Text] [Related]
5. Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access.
Fumagalli F; Calbi V; Natali Sora MG; Sessa M; Baldoli C; Rancoita PMV; Ciotti F; Sarzana M; Fraschini M; Zambon AA; Acquati S; Redaelli D; Attanasio V; Miglietta S; De Mattia F; Barzaghi F; Ferrua F; Migliavacca M; Tucci F; Gallo V; Del Carro U; Canale S; Spiga I; Lorioli L; Recupero S; Fratini ES; Morena F; Silvani P; Calvi MR; Facchini M; Locatelli S; Corti A; Zancan S; Antonioli G; Farinelli G; Gabaldo M; Garcia-Segovia J; Schwab LC; Downey GF; Filippi M; Cicalese MP; Martino S; Di Serio C; Ciceri F; Bernardo ME; Naldini L; Biffi A; Aiuti A
Lancet; 2022 Jan; 399(10322):372-383. PubMed ID: 35065785
[TBL] [Abstract][Full Text] [Related]
6. Insights into the natural history of metachromatic leukodystrophy from interviews with caregivers.
Harrington M; Whalley D; Twiss J; Rushton R; Martin S; Huynh L; Yang H
Orphanet J Rare Dis; 2019 Apr; 14(1):89. PubMed ID: 31036045
[TBL] [Abstract][Full Text] [Related]
7. Juvenile metachromatic leukodystrophy 10 years post transplant compared with a non-transplanted cohort.
Krägeloh-Mann I; Groeschel S; Kehrer C; Opherk K; Nägele T; Handgretinger R; Müller I
Bone Marrow Transplant; 2013 Mar; 48(3):369-75. PubMed ID: 22941383
[TBL] [Abstract][Full Text] [Related]
8. Metachromatic leukodystrophy: A single-center longitudinal study of 45 patients.
Fumagalli F; Zambon AA; Rancoita PMV; Baldoli C; Canale S; Spiga I; Medaglini S; Penati R; Facchini M; Ciotti F; Sarzana M; Lorioli L; Cesani M; Natali Sora MG; Del Carro U; Cugnata F; Antonioli G; Recupero S; Calbi V; Di Serio C; Aiuti A; Biffi A; Sessa M
J Inherit Metab Dis; 2021 Sep; 44(5):1151-1164. PubMed ID: 33855715
[TBL] [Abstract][Full Text] [Related]
9. A systematic review of clinical effectiveness and safety for historical and current treatment options for metachromatic leukodystrophy in children, including atidarsagene autotemcel.
Armstrong N; Olaye A; Noake C; Pang F
Orphanet J Rare Dis; 2023 Aug; 18(1):248. PubMed ID: 37644601
[TBL] [Abstract][Full Text] [Related]
10. Lentiviral haemopoietic stem-cell gene therapy in early-onset metachromatic leukodystrophy: an ad-hoc analysis of a non-randomised, open-label, phase 1/2 trial.
Sessa M; Lorioli L; Fumagalli F; Acquati S; Redaelli D; Baldoli C; Canale S; Lopez ID; Morena F; Calabria A; Fiori R; Silvani P; Rancoita PM; Gabaldo M; Benedicenti F; Antonioli G; Assanelli A; Cicalese MP; Del Carro U; Sora MG; Martino S; Quattrini A; Montini E; Di Serio C; Ciceri F; Roncarolo MG; Aiuti A; Naldini L; Biffi A
Lancet; 2016 Jul; 388(10043):476-87. PubMed ID: 27289174
[TBL] [Abstract][Full Text] [Related]
11. Inventory of current practices regarding hematopoietic stem cell transplantation in metachromatic leukodystrophy in Europe and neighboring countries.
Schoenmakers DH; Mochel F; Adang LA; Boelens JJ; Calbi V; Eklund EA; Grønborg SW; Fumagalli F; Groeschel S; Lindemans C; Sevin C; Schöls L; Ram D; Zerem A; Graessner H; Wolf NI
Orphanet J Rare Dis; 2024 Feb; 19(1):46. PubMed ID: 38326898
[TBL] [Abstract][Full Text] [Related]
12. Allogeneic mesenchymal stem cell infusion for treatment of metachromatic leukodystrophy (MLD) and Hurler syndrome (MPS-IH).
Koç ON; Day J; Nieder M; Gerson SL; Lazarus HM; Krivit W
Bone Marrow Transplant; 2002 Aug; 30(4):215-22. PubMed ID: 12203137
[TBL] [Abstract][Full Text] [Related]
13. Evaluating meaningful changes in physical functioning and cognitive declines in metachromatic leukodystrophy: a caregiver interview study.
Martin S; Harris N; Romanus D
J Patient Rep Outcomes; 2023 Jul; 7(1):70. PubMed ID: 37458805
[TBL] [Abstract][Full Text] [Related]
14. Early clinical course after hematopoietic stem cell transplantation in children with juvenile metachromatic leukodystrophy.
Beschle J; Döring M; Kehrer C; Raabe C; Bayha U; Strölin M; Böhringer J; Bevot A; Kaiser N; Bender B; Grimm A; Lang P; Müller I; Krägeloh-Mann I; Groeschel S
Mol Cell Pediatr; 2020 Sep; 7(1):12. PubMed ID: 32910272
[TBL] [Abstract][Full Text] [Related]
15. Clinical outcome in four children with metachromatic leukodystrophy treated by bone marrow transplantation.
Malm G; Ringdén O; Winiarski J; Gröndahl E; Uyebrant P; Eriksson U; Håkansson H; Skjeldal O; Månsson JE
Bone Marrow Transplant; 1996 Jun; 17(6):1003-8. PubMed ID: 8807106
[TBL] [Abstract][Full Text] [Related]
16. Hematopoietic SCT: a useful treatment for late metachromatic leukodystrophy.
Solders M; Martin DA; Andersson C; Remberger M; Andersson T; Ringdén O; Solders G
Bone Marrow Transplant; 2014 Aug; 49(8):1046-51. PubMed ID: 24797185
[TBL] [Abstract][Full Text] [Related]
17. Haematopoietic stem cell transplantation does not retard disease progression in the psycho-cognitive variant of late-onset metachromatic leukodystrophy.
Smith NJ; Marcus RE; Sahakian BJ; Kapur N; Cox TM
J Inherit Metab Dis; 2010 Dec; 33 Suppl 3():S471-5. PubMed ID: 21080229
[TBL] [Abstract][Full Text] [Related]
18. Allogenic hematopoietic stem cell transplantation in two siblings with adult metachromatic leukodystrophy and a systematic literature review.
Videbæk C; Stokholm J; Sengeløv H; Fjeldborg LU; Larsen VA; Krarup C; Nielsen JE; Grønborg S
JIMD Rep; 2021 Jul; 60(1):96-104. PubMed ID: 34258145
[TBL] [Abstract][Full Text] [Related]
19. Outcome of Early Juvenile Onset Metachromatic Leukodystrophy After Unrelated Cord Blood Transplantation: A Case Series and Review of the Literature.
Chen X; Gill D; Shaw P; Ouvrier R; Troedson C
J Child Neurol; 2016 Mar; 31(3):338-44. PubMed ID: 26187619
[TBL] [Abstract][Full Text] [Related]
20. The burden of disease in metachromatic leukodystrophy: results of a caregiver survey in the UK and Republic of Ireland.
Thomas S; Morrison A; Morton G; Roberts P; Clark V; Imrie J
Orphanet J Rare Dis; 2024 Feb; 19(1):87. PubMed ID: 38403596
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
