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27. Early higher dosage of alglucosidase alpha in classic Pompe disease. Spada M; Pagliardini V; Ricci F; Biamino E; Mongini T; Porta F J Pediatr Endocrinol Metab; 2018 Dec; 31(12):1343-1347. PubMed ID: 30433875 [TBL] [Abstract][Full Text] [Related]
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32. Prognostic factors for the late onset Pompe disease with enzyme replacement therapy: from our experience of 4 cases including an autopsy case. Kobayashi H; Shimada Y; Ikegami M; Kawai T; Sakurai K; Urashima T; Ijima M; Fujiwara M; Kaneshiro E; Ohashi T; Eto Y; Ishigaki K; Osawa M; Kyosen SO; Ida H Mol Genet Metab; 2010 May; 100(1):14-9. PubMed ID: 20202878 [TBL] [Abstract][Full Text] [Related]
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