These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
10. New pharmacotherapies for genetic neuromuscular disorders: opportunities and challenges. Ricci F; Vacchetti M; Brusa C; Vercelli L; Davico C; Vitiello B; Mongini T Expert Rev Clin Pharmacol; 2019 Aug; 12(8):757-770. PubMed ID: 31220956 [No Abstract] [Full Text] [Related]
11. Genetic therapies for inherited neuromuscular disorders. Scoto M; Finkel R; Mercuri E; Muntoni F Lancet Child Adolesc Health; 2018 Aug; 2(8):600-609. PubMed ID: 30119719 [TBL] [Abstract][Full Text] [Related]
12. Gene-based therapies of neuromuscular disorders: an update and the pivotal role of patient organizations in their discovery and implementation. Braun S J Gene Med; 2013; 15(11-12):397-413. PubMed ID: 24123726 [TBL] [Abstract][Full Text] [Related]
13. Making sense of antisense oligonucleotides: A narrative review. Goyal N; Narayanaswami P Muscle Nerve; 2018 Mar; 57(3):356-370. PubMed ID: 29105153 [TBL] [Abstract][Full Text] [Related]
14. RNA-targeting approaches for neuromuscular diseases. Le Roy F; Charton K; Lorson CL; Richard I Trends Mol Med; 2009 Dec; 15(12):580-91. PubMed ID: 19906562 [TBL] [Abstract][Full Text] [Related]
15. Opportunities and challenges for the development of antisense treatment in neuromuscular disorders. van Putten M; Aartsma-Rus A Expert Opin Biol Ther; 2011 Aug; 11(8):1025-37. PubMed ID: 21510827 [TBL] [Abstract][Full Text] [Related]
16. Seeking a better landscape for therapy development in neuromuscular disorders. Larkindale J; Porter JD Muscle Nerve; 2018 Jan; 57(1):16-19. PubMed ID: 28881009 [TBL] [Abstract][Full Text] [Related]
17. Gene therapeutic strategies and relevant clinical trials in neuromuscular disorder in China. Hu C; Li X Gene Ther; 2020 Aug; 27(7-8):321-328. PubMed ID: 32591735 [TBL] [Abstract][Full Text] [Related]