These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

175 related articles for article (PubMed ID: 26870664)

  • 1. Compliance to Care Guidelines for Duchenne Muscular Dystrophy.
    Landfeldt E; Lindgren P; Bell CF; Schmitt C; Guglieri M; Straub V; Lochmüller H; Bushby K
    J Neuromuscul Dis; 2015; 2(1):63-72. PubMed ID: 26870664
    [TBL] [Abstract][Full Text] [Related]  

  • 2. European Cross-Sectional Survey of Current Care Practices for Duchenne Muscular Dystrophy Reveals Regional and Age-Dependent Differences.
    Vry J; Gramsch K; Rodger S; Thompson R; Steffensen BF; Rahbek J; Doerken S; Tassoni A; Beytía ML; Guergueltcheva V; Chamova T; Tournev I; Kostera-Pruszczyk A; Kaminska A; Lusakowska A; Mrazova L; Pavlovska L; Strenkova J; Vondráček P; Garami M; Karcagi V; Herczegfalvi Á; Bushby K; Lochmüller H; Kirschner J
    J Neuromuscul Dis; 2016 Nov; 3(4):517-527. PubMed ID: 27911335
    [TBL] [Abstract][Full Text] [Related]  

  • 3. The burden of Duchenne muscular dystrophy: an international, cross-sectional study.
    Landfeldt E; Lindgren P; Bell CF; Schmitt C; Guglieri M; Straub V; Lochmüller H; Bushby K
    Neurology; 2014 Aug; 83(6):529-36. PubMed ID: 24991029
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Patient and caregiver perspectives on guideline adherence: the case of endocrine and bone health recommendations for Duchenne muscular dystrophy.
    Denger B; Kinnett K; Martin A; Grant S; Armstrong C; Khodyakov D
    Orphanet J Rare Dis; 2019 Aug; 14(1):205. PubMed ID: 31429780
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Adult care for Duchenne muscular dystrophy in the UK.
    Rodger S; Woods KL; Bladen CL; Stringer A; Vry J; Gramsch K; Kirschner J; Thompson R; Bushby K; Lochmüller H
    J Neurol; 2015 Mar; 262(3):629-41. PubMed ID: 25536903
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Standards of care for Duchenne muscular dystrophy: brief TREAT-NMD recommendations.
    Sejerson T; Bushby K;
    Adv Exp Med Biol; 2009; 652():13-21. PubMed ID: 20225016
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Compliance to DMD Care Considerations in the Netherlands.
    Heutinck L; Houwen-van Opstal SLS; Krom YD; Niks EH; Verschuuren JJGM; Jansen M; de Groot IJM
    J Neuromuscul Dis; 2021; 8(6):927-938. PubMed ID: 34120911
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Health-related quality of life in patients with Duchenne muscular dystrophy: a multinational, cross-sectional study.
    Landfeldt E; Lindgren P; Bell CF; Guglieri M; Straub V; Lochmüller H; Bushby K
    Dev Med Child Neurol; 2016 May; 58(5):508-15. PubMed ID: 26483095
    [TBL] [Abstract][Full Text] [Related]  

  • 9. The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence review.
    Ryder S; Leadley RM; Armstrong N; Westwood M; de Kock S; Butt T; Jain M; Kleijnen J
    Orphanet J Rare Dis; 2017 Apr; 12(1):79. PubMed ID: 28446219
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Reliability and validity of the Thai version of the Pediatric Quality of Life inventory™ 3.0 Duchenne Muscular Dystrophy module in Thai children with Duchenne Muscular Dystrophy.
    Thongsing A; Likasitwattanakul S; Sanmaneechai O
    Health Qual Life Outcomes; 2019 May; 17(1):76. PubMed ID: 31046775
    [TBL] [Abstract][Full Text] [Related]  

  • 11. The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia.
    Bladen CL; Rafferty K; Straub V; Monges S; Moresco A; Dawkins H; Roy A; Chamova T; Guergueltcheva V; Korngut L; Campbell C; Dai Y; Barišić N; Kos T; Brabec P; Rahbek J; Lahdetie J; Tuffery-Giraud S; Claustres M; Leturcq F; Ben Yaou R; Walter MC; Schreiber O; Karcagi V; Herczegfalvi A; Viswanathan V; Bayat F; de la Caridad Guerrero Sarmiento I; Ambrosini A; Ceradini F; Kimura E; van den Bergen JC; Rodrigues M; Roxburgh R; Lusakowska A; Oliveira J; Santos R; Neagu E; Butoianu N; Artemieva S; Rasic VM; Posada M; Palau F; Lindvall B; Bloetzer C; Karaduman A; Topaloğlu H; Inal S; Oflazer P; Stringer A; Shatillo AV; Martin AS; Peay H; Flanigan KM; Salgado D; von Rekowski B; Lynn S; Heslop E; Gainotti S; Taruscio D; Kirschner J; Verschuuren J; Bushby K; Béroud C; Lochmüller H
    Hum Mutat; 2013 Nov; 34(11):1449-57. PubMed ID: 23913485
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Lower Extremity Functional Outcome Measures in Duchenne Muscular Dystrophy-A Delphi Survey.
    Senesac CR; Lott DJ; Willcocks RJ; Duong T; Smith BK
    J Neuromuscul Dis; 2019; 6(1):75-83. PubMed ID: 30562905
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database.
    Koeks Z; Bladen CL; Salgado D; van Zwet E; Pogoryelova O; McMacken G; Monges S; Foncuberta ME; Kekou K; Kosma K; Dawkins H; Lamont L; Bellgard MI; Roy AJ; Chamova T; Guergueltcheva V; Chan S; Korngut L; Campbell C; Dai Y; Wang J; Barišić N; Brabec P; Lähdetie J; Walter MC; Schreiber-Katz O; Karcagi V; Garami M; Herczegfalvi A; Viswanathan V; Bayat F; Buccella F; Ferlini A; Kimura E; van den Bergen JC; Rodrigues M; Roxburgh R; Lusakowska A; Kostera-Pruszczyk A; Santos R; Neagu E; Artemieva S; Rasic VM; Vojinovic D; Posada M; Bloetzer C; Klein A; Díaz-Manera J; Gallardo E; Karaduman AA; Oznur T; Topaloğlu H; El Sherif R; Stringer A; Shatillo AV; Martin AS; Peay HL; Kirschner J; Flanigan KM; Straub V; Bushby K; Béroud C; Verschuuren JJ; Lochmüller H
    J Neuromuscul Dis; 2017; 4(4):293-306. PubMed ID: 29125504
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Respiratory Care Received by Individuals With Duchenne Muscular Dystrophy From 2000 to 2011.
    Andrews JG; Soim A; Pandya S; Westfield CP; Ciafaloni E; Fox DJ; Birnkrant DJ; Cunniff CM; Sheehan DW;
    Respir Care; 2016 Oct; 61(10):1349-59. PubMed ID: 27507176
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Social/economic costs and health-related quality of life in patients with Duchenne muscular dystrophy in Europe.
    Cavazza M; Kodra Y; Armeni P; De Santis M; López-Bastida J; Linertová R; Oliva-Moreno J; Serrano-Aguilar P; Posada-de-la-Paz M; Taruscio D; Schieppati A; Iskrov G; Péntek M; von der Schulenburg JM; Kanavos P; Chevreul K; Persson U; Fattore G;
    Eur J Health Econ; 2016 Apr; 17 Suppl 1():19-29. PubMed ID: 27038625
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Improving Access and Guideline Adherence in Pulmonary Care in Patients With Duchenne Muscular Dystrophy.
    Kaslow JA; Soslow JH; Burnette WB; Raucci FJ; Hills TJ; Ibach MG; Hebblethwaite RC; Arps KM; Sokolow AG
    Respir Care; 2022 Mar; 67(3):347-352. PubMed ID: 34876494
    [TBL] [Abstract][Full Text] [Related]  

  • 17. A checklist for clinical trials in rare disease: obstacles and anticipatory actions-lessons learned from the FOR-DMD trial.
    Crow RA; Hart KA; McDermott MP; Tawil R; Martens WB; Herr BE; McColl E; Wilkinson J; Kirschner J; King WM; Eagle M; Brown MW; Hirtz D; Lochmuller H; Straub V; Ciafaloni E; Shieh PB; Spinty S; Childs AM; Manzur AY; Morandi L; Butterfield RJ; Horrocks I; Roper H; Flanigan KM; Kuntz NL; Mah JK; Morrison L; Darras BT; von der Hagen M; Schara U; Wilichowski E; Mongini T; McDonald CM; Vita G; Barohn RJ; Finkel RS; Wicklund M; McMillan HJ; Hughes I; Pegoraro E; Bryan Burnette W; Howard JF; Thangarajh M; Campbell C; Griggs RC; Bushby K; Guglieri M
    Trials; 2018 May; 19(1):291. PubMed ID: 29793540
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Characterizing health state utilities associated with Duchenne muscular dystrophy: a systematic review.
    Szabo SM; Audhya IF; Malone DC; Feeny D; Gooch KL
    Qual Life Res; 2020 Mar; 29(3):593-605. PubMed ID: 31811595
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Current management of Duchenne muscular dystrophy in the Middle East: expert report.
    Jumah MA; Muhaizea MA; Rumayyan AA; Saman AA; Shehri AA; Cupler E; Jan M; Madani AA; Fathalla W; Kashyape P; Kodavooru G; Thihli KA; Bastaki L; Megarbane A; Skrypnyk C; Zamani G; Tuffery-Giraud S; Urtizberea A; Ortez González CI
    Neurodegener Dis Manag; 2019 Jun; 9(3):123-133. PubMed ID: 31166138
    [No Abstract]   [Full Text] [Related]  

  • 20. Patient demographics and characteristics from an ambispective, observational study of patients with duchenne muscular dystrophy in Saudi Arabia.
    AlSaman AS; Al Ghamdi F; Bamaga AK; AlShaikh N; Al Muqbil M; Muthaffar O; Bashiri FA; Ali B; Mulayim A; Heider E; Alshahrani AA; Al Muhaizea MA
    Front Pediatr; 2022; 10():1020059. PubMed ID: 36275069
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 9.