These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
10. Gene therapy for lysosomal storage diseases (LSDs) in large animal models. Haskins M ILAR J; 2009; 50(2):112-21. PubMed ID: 19293456 [TBL] [Abstract][Full Text] [Related]
11. Enzyme Replacement Therapy: A Review and Its Role in Treating Lysosomal Storage Diseases. Li M Pediatr Ann; 2018 May; 47(5):e191-e197. PubMed ID: 29750286 [TBL] [Abstract][Full Text] [Related]
12. Current state of the management of LSDs. Germain DP; Aggio M Int J Clin Pharmacol Ther; 2009; 47 Suppl 1():S61-2. PubMed ID: 20040313 [No Abstract] [Full Text] [Related]
13. [Allogeneic bone marrow transplantation in the treatment of (lysosomal) storage diseases]. Maaswinkel-Mooij PD; Poorthuis BJ; Hoogerbrugge PM; Brouwer OF; Vossen JM Ned Tijdschr Geneeskd; 1998 Jan; 142(4):169-74. PubMed ID: 9557021 [TBL] [Abstract][Full Text] [Related]
14. Treatment for LSDs: no longer just enzyme replacement therapy for Gaucher disease. Foreword. Cohen IJ; Baris H; Mistry PK Pediatr Endocrinol Rev; 2013 Nov; 11 Suppl 1():58. PubMed ID: 24380122 [No Abstract] [Full Text] [Related]
15. Recent developments in therapeutic approaches for lysosomal storage diseases. Urbanelli L; Magini A; Polchi A; Polidoro M; Emiliani C Recent Pat CNS Drug Discov; 2011 Jan; 6(1):1-19. PubMed ID: 21073432 [TBL] [Abstract][Full Text] [Related]
16. Treatment strategies for lysosomal storage disorders. Beck M Dev Med Child Neurol; 2018 Jan; 60(1):13-18. PubMed ID: 29090451 [TBL] [Abstract][Full Text] [Related]
17. Therapeutic approaches for lysosomal storage diseases: a patent update. Urbanelli L; Sagini K; Polidoro M; Brozzi A; Magini A; Emiliani C Recent Pat CNS Drug Discov; 2013 Aug; 8(2):91-109. PubMed ID: 23713988 [TBL] [Abstract][Full Text] [Related]