296 related articles for article (PubMed ID: 27184436)
1. In vitro evaluation of 2-hydroxyalkylated β-cyclodextrins as potential therapeutic agents for Niemann-Pick Type C disease.
Kondo Y; Tokumaru H; Ishitsuka Y; Matsumoto T; Taguchi M; Motoyama K; Higashi T; Arima H; Matsuo M; Higaki K; Ohno K; Irie T
Mol Genet Metab; 2016 Jul; 118(3):214-219. PubMed ID: 27184436
[TBL] [Abstract][Full Text] [Related]
2. Differential Effects of 2-Hydroxypropyl-Cyclodextrins on Lipid Accumulation in
Hoque S; Kondo Y; Sakata N; Yamada Y; Fukaura M; Higashi T; Motoyama K; Arima H; Higaki K; Hayashi A; Komiya T; Ishitsuka Y; Irie T
Int J Mol Sci; 2020 Jan; 21(3):. PubMed ID: 32019132
[TBL] [Abstract][Full Text] [Related]
3. In Vitro and In Vivo Evaluation of 6-O-α-Maltosyl-β-Cyclodextrin as a Potential Therapeutic Agent Against Niemann-Pick Disease Type C.
Yasmin N; Ishitsuka Y; Fukaura M; Yamada Y; Nakahara S; Ishii A; Kondo Y; Takeo T; Nakagata N; Motoyama K; Higashi T; Okada Y; Nishikawa J; Ichikawa A; Iohara D; Hirayama F; Higaki K; Ohno K; Matsuo M; Irie T
Int J Mol Sci; 2019 Mar; 20(5):. PubMed ID: 30845767
[TBL] [Abstract][Full Text] [Related]
4. Efficacy of 2-Hydroxypropyl-β-cyclodextrin in Niemann-Pick Disease Type C Model Mice and Its Pharmacokinetic Analysis in a Patient with the Disease.
Tanaka Y; Yamada Y; Ishitsuka Y; Matsuo M; Shiraishi K; Wada K; Uchio Y; Kondo Y; Takeo T; Nakagata N; Higashi T; Motoyama K; Arima H; Mochinaga S; Higaki K; Ohno K; Irie T
Biol Pharm Bull; 2015; 38(6):844-51. PubMed ID: 26027824
[TBL] [Abstract][Full Text] [Related]
5. Hydroxypropyl-beta and -gamma cyclodextrins rescue cholesterol accumulation in Niemann-Pick C1 mutant cell via lysosome-associated membrane protein 1.
Singhal A; Szente L; Hildreth JEK; Song B
Cell Death Dis; 2018 Oct; 9(10):1019. PubMed ID: 30282967
[TBL] [Abstract][Full Text] [Related]
6. β-Cyclodextrin-threaded biocleavable polyrotaxanes ameliorate impaired autophagic flux in Niemann-Pick type C disease.
Tamura A; Yui N
J Biol Chem; 2015 Apr; 290(15):9442-54. PubMed ID: 25713067
[TBL] [Abstract][Full Text] [Related]
7. Influence of
Tanaka Y; Ishitsuka Y; Yamada Y; Kondo Y; Takeo T; Nakagata N; Higashi T; Motoyama K; Arima H; Matsuo M; Higaki K; Ohno K; Irie T
Mol Genet Metab Rep; 2014; 1():19-30. PubMed ID: 27896072
[TBL] [Abstract][Full Text] [Related]
8. [Inclusion Solves Insolubility -Translational Research Cycle from Bedside to Bench and Bench to Bedside for Drug Development Targeting Niemann-Pick Disease Type C].
Irie T
Yakugaku Zasshi; 2022; 142(4):389-400. PubMed ID: 35370195
[TBL] [Abstract][Full Text] [Related]
9. Endocytosis of beta-cyclodextrins is responsible for cholesterol reduction in Niemann-Pick type C mutant cells.
Rosenbaum AI; Zhang G; Warren JD; Maxfield FR
Proc Natl Acad Sci U S A; 2010 Mar; 107(12):5477-82. PubMed ID: 20212119
[TBL] [Abstract][Full Text] [Related]
10. Normalization of cholesterol homeostasis by 2-hydroxypropyl-β-cyclodextrin in neurons and glia from Niemann-Pick C1 (NPC1)-deficient mice.
Peake KB; Vance JE
J Biol Chem; 2012 Mar; 287(12):9290-8. PubMed ID: 22277650
[TBL] [Abstract][Full Text] [Related]
11. Long-term efficacy of intrathecal cyclodextrin in patients with Niemann-Pick disease type C.
Matsuo M; Sakakibara T; Sakiyama Y; So T; Kosuga M; Kakiuchi T; Ichinose F; Nakamura T; Ishitsuka Y; Irie T
Brain Dev; 2024 May; 46(5):207-212. PubMed ID: 38448301
[TBL] [Abstract][Full Text] [Related]
12. Differential mode of cholesterol inclusion with 2-hydroxypropyl-cyclodextrins increases safety margin in treatment of Niemann-Pick disease type C.
Yamada Y; Ishitsuka Y; Kondo Y; Nakahara S; Nishiyama A; Takeo T; Nakagata N; Motoyama K; Higashi T; Arima H; Kamei S; Shuto T; Kai H; Hayashino Y; Sugita M; Kikuchi T; Hirata F; Miwa T; Takeda H; Orita Y; Seki T; Ohta T; Kurauchi Y; Katsuki H; Matsuo M; Higaki K; Ohno K; Matsumoto S; Era T; Irie T
Br J Pharmacol; 2021 Jul; 178(13):2727-2746. PubMed ID: 33782944
[TBL] [Abstract][Full Text] [Related]
13. Beneficial effects of primidone in Niemann-Pick disease type C (NPC)-model cells and mice: Reduction of unesterified cholesterol levels in cells and extension of lifespan in mice.
Ashikawa H; Mogi H; Honda T; Nakamura H; Murayama T
Eur J Pharmacol; 2021 Apr; 896():173907. PubMed ID: 33503462
[TBL] [Abstract][Full Text] [Related]
14. Effects of 6-O-α-maltosyl-β cyclodextrin on lipid metabolism in Npc1-deficient Chinese hamster ovary cells.
Okada BY; Kuroiwa S; Noi A; Tanaka A; Nishikawa J; Kondo Y; Ishitsuka Y; Irie T; Higaki K; Matsuo M; Ichikawa A
Mol Genet Metab; 2022 Nov; 137(3):239-248. PubMed ID: 36182715
[TBL] [Abstract][Full Text] [Related]
15. Cyclodextrins in the treatment of a mouse model of Niemann-Pick C disease.
Camargo F; Erickson RP; Garver WS; Hossain GS; Carbone PN; Heidenreich RA; Blanchard J
Life Sci; 2001 Nov; 70(2):131-42. PubMed ID: 11787939
[TBL] [Abstract][Full Text] [Related]
16. Cyclodextrin overcomes deficient lysosome-to-endoplasmic reticulum transport of cholesterol in Niemann-Pick type C cells.
Abi-Mosleh L; Infante RE; Radhakrishnan A; Goldstein JL; Brown MS
Proc Natl Acad Sci U S A; 2009 Nov; 106(46):19316-21. PubMed ID: 19884502
[TBL] [Abstract][Full Text] [Related]
17. Systemic administration of 2-hydroxypropyl-β-cyclodextrin to symptomatic Npc1-deficient mice slows cholesterol sequestration in the major organs and improves liver function.
Lopez AM; Terpack SJ; Posey KS; Liu B; Ramirez CM; Turley SD
Clin Exp Pharmacol Physiol; 2014 Oct; 41(10):780-7. PubMed ID: 25115571
[TBL] [Abstract][Full Text] [Related]
18. HPGCD outperforms HPBCD as a potential treatment for Niemann-Pick disease type C during disease modeling with iPS cells.
Soga M; Ishitsuka Y; Hamasaki M; Yoneda K; Furuya H; Matsuo M; Ihn H; Fusaki N; Nakamura K; Nakagata N; Endo F; Irie T; Era T
Stem Cells; 2015 Apr; 33(4):1075-88. PubMed ID: 25522247
[TBL] [Abstract][Full Text] [Related]
19. Decreased neural stem cell proliferation and olfaction in mouse models of Niemann-Pick C1 disease and the response to hydroxypropyl-β-cyclodextrin.
Dragotto J; Palladino G; Canterini S; Caporali P; Patil R; Fiorenza MT; Erickson RP
J Appl Genet; 2019 Nov; 60(3-4):357-365. PubMed ID: 31485950
[TBL] [Abstract][Full Text] [Related]
20. Cholesterol-Lowering Effect of Octaarginine-Appended β-Cyclodextrin in Npc1-Trap-CHO Cells.
Motoyama K; Nishiyama R; Maeda Y; Higashi T; Kawaguchi Y; Futaki S; Ishitsuka Y; Kondo Y; Irie T; Era T; Arima H
Biol Pharm Bull; 2016 Nov; 39(11):1823-1829. PubMed ID: 27601082
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]