568 related articles for article (PubMed ID: 27256364)
21. Induced Pluripotency and Gene Editing in Fanconi Anemia.
Navarro S; Giorgetti A; Raya A; Tolar J
Curr Gene Ther; 2017; 16(5):321-328. PubMed ID: 28103772
[TBL] [Abstract][Full Text] [Related]
22. Transcription activator-like effector nuclease (TALEN)-mediated gene correction in integration-free β-thalassemia induced pluripotent stem cells.
Ma N; Liao B; Zhang H; Wang L; Shan Y; Xue Y; Huang K; Chen S; Zhou X; Chen Y; Pei D; Pan G
J Biol Chem; 2013 Nov; 288(48):34671-9. PubMed ID: 24155235
[TBL] [Abstract][Full Text] [Related]
23. Factor-induced Reprogramming and Zinc Finger Nuclease-aided Gene Targeting Cause Different Genome Instability in β-Thalassemia Induced Pluripotent Stem Cells (iPSCs).
Ma N; Shan Y; Liao B; Kong G; Wang C; Huang K; Zhang H; Cai X; Chen S; Pei D; Chen N; Pan G
J Biol Chem; 2015 May; 290(19):12079-89. PubMed ID: 25795783
[TBL] [Abstract][Full Text] [Related]
24. Induced Pluripotent Stem Cells and CRISPR-Cas9 Innovations for Treating Alpha-1 Antitrypsin Deficiency and Glycogen Storage Diseases.
Walsh C; Jin S
Cells; 2024 Jun; 13(12):. PubMed ID: 38920680
[TBL] [Abstract][Full Text] [Related]
25. Targeted correction and restored function of the CFTR gene in cystic fibrosis induced pluripotent stem cells.
Crane AM; Kramer P; Bui JH; Chung WJ; Li XS; Gonzalez-Garay ML; Hawkins F; Liao W; Mora D; Choi S; Wang J; Sun HC; Paschon DE; Guschin DY; Gregory PD; Kotton DN; Holmes MC; Sorscher EJ; Davis BR
Stem Cell Reports; 2015 Apr; 4(4):569-77. PubMed ID: 25772471
[TBL] [Abstract][Full Text] [Related]
26. Modeling neurological diseases with induced pluripotent cells reprogrammed from immortalized lymphoblastoid cell lines.
Fujimori K; Tezuka T; Ishiura H; Mitsui J; Doi K; Yoshimura J; Tada H; Matsumoto T; Isoda M; Hashimoto R; Hattori N; Takahashi T; Morishita S; Tsuji S; Akamatsu W; Okano H
Mol Brain; 2016 Oct; 9(1):88. PubMed ID: 27716287
[TBL] [Abstract][Full Text] [Related]
27. Adenine base editing reduces misfolded protein accumulation and toxicity in alpha-1 antitrypsin deficient patient iPSC-hepatocytes.
Werder RB; Kaserman JE; Packer MS; Lindstrom-Vautrin J; Villacorta-Martin C; Young LE; Aratyn-Schaus Y; Gregoire F; Wilson AA
Mol Ther; 2021 Nov; 29(11):3219-3229. PubMed ID: 34217893
[TBL] [Abstract][Full Text] [Related]
28. Gene Correction of iPSCs from a Wiskott-Aldrich Syndrome Patient Normalizes the Lymphoid Developmental and Functional Defects.
Laskowski TJ; Van Caeneghem Y; Pourebrahim R; Ma C; Ni Z; Garate Z; Crane AM; Li XS; Liao W; Gonzalez-Garay M; Segovia JC; Paschon DE; Rebar EJ; Holmes MC; Kaufman D; Vandekerckhove B; Davis BR
Stem Cell Reports; 2016 Aug; 7(2):139-48. PubMed ID: 27396937
[TBL] [Abstract][Full Text] [Related]
29. Genetic correction of induced pluripotent stem cells mediated by transcription activator-like effector nucleases targeting ALPL recovers enzyme activity and calcification in vitro.
Nakano C; Kitabatake Y; Takeyari S; Ohata Y; Kubota T; Taketani K; Kogo M; Ozono K
Mol Genet Metab; 2019 Jun; 127(2):158-165. PubMed ID: 31178256
[TBL] [Abstract][Full Text] [Related]
30. Biallelic correction of sickle cell disease-derived induced pluripotent stem cells (iPSCs) confirmed at the protein level through serum-free iPS-sac/erythroid differentiation.
Haro-Mora JJ; Uchida N; Demirci S; Wang Q; Zou J; Tisdale JF
Stem Cells Transl Med; 2020 May; 9(5):590-602. PubMed ID: 32034898
[TBL] [Abstract][Full Text] [Related]
31. Induced Pluripotent Stem Cells for Cardiovascular Disease Modeling and Precision Medicine: A Scientific Statement From the American Heart Association.
Musunuru K; Sheikh F; Gupta RM; Houser SR; Maher KO; Milan DJ; Terzic A; Wu JC;
Circ Genom Precis Med; 2018 Jan; 11(1):e000043. PubMed ID: 29874173
[TBL] [Abstract][Full Text] [Related]
32. CRISPR/Cas9 for Sickle Cell Disease: Applications, Future Possibilities, and Challenges.
Demirci S; Leonard A; Haro-Mora JJ; Uchida N; Tisdale JF
Adv Exp Med Biol; 2019; 1144():37-52. PubMed ID: 30715679
[TBL] [Abstract][Full Text] [Related]
33. Genome Editing and Induced Pluripotent Stem Cell Technologies for Personalized Study of Cardiovascular Diseases.
Chun YW; Durbin MD; Hong CC
Curr Cardiol Rep; 2018 Apr; 20(6):38. PubMed ID: 29666931
[TBL] [Abstract][Full Text] [Related]
34. Lymphoid regeneration from gene-corrected SCID-X1 subject-derived iPSCs.
Menon T; Firth AL; Scripture-Adams DD; Galic Z; Qualls SJ; Gilmore WB; Ke E; Singer O; Anderson LS; Bornzin AR; Alexander IE; Zack JA; Verma IM
Cell Stem Cell; 2015 Apr; 16(4):367-72. PubMed ID: 25772073
[TBL] [Abstract][Full Text] [Related]
35. Rescue of DNA-PK Signaling and T-Cell Differentiation by Targeted Genome Editing in a prkdc Deficient iPSC Disease Model.
Rahman SH; Kuehle J; Reimann C; Mlambo T; Alzubi J; Maeder ML; Riedel H; Fisch P; Cantz T; Rudolph C; Mussolino C; Joung JK; Schambach A; Cathomen T
PLoS Genet; 2015 May; 11(5):e1005239. PubMed ID: 26000857
[TBL] [Abstract][Full Text] [Related]
36. Concurrent progress of reprogramming and gene correction to overcome therapeutic limitation of mutant ALK2-iPSC.
Kim BY; Jeong S; Lee SY; Lee SM; Gweon EJ; Ahn H; Kim J; Chung SK
Exp Mol Med; 2016 Jun; 48(6):e237. PubMed ID: 27256111
[TBL] [Abstract][Full Text] [Related]
37. Generation of human organs in pigs via interspecies blastocyst complementation.
Wu J; Platero Luengo A; Gil MA; Suzuki K; Cuello C; Morales Valencia M; Parrilla I; Martinez CA; Nohalez A; Roca J; Martinez EA; Izpisua Belmonte JC
Reprod Domest Anim; 2016 Oct; 51 Suppl 2():18-24. PubMed ID: 27762052
[TBL] [Abstract][Full Text] [Related]
38. iPSCs as a Platform for Disease Modeling, Drug Screening, and Personalized Therapy in Muscular Dystrophies.
Ortiz-Vitali JL; Darabi R
Cells; 2019 Jan; 8(1):. PubMed ID: 30609814
[TBL] [Abstract][Full Text] [Related]
39. Precise Correction of Disease Mutations in Induced Pluripotent Stem Cells Derived From Patients With Limb Girdle Muscular Dystrophy.
Turan S; Farruggio AP; Srifa W; Day JW; Calos MP
Mol Ther; 2016 Apr; 24(4):685-96. PubMed ID: 26916285
[TBL] [Abstract][Full Text] [Related]
40. Generating patient-specific induced pluripotent stem cells-derived cardiomyocytes for the treatment of cardiac diseases.
Jeziorowska D; Korniat A; Salem JE; Fish K; Hulot JS
Expert Opin Biol Ther; 2015; 15(10):1399-409. PubMed ID: 26134098
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]