130 related articles for article (PubMed ID: 27288778)
1. Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients.
García-Robles AA; Company-Albir MJ; Megías-Vericat JE; Fernández-Megía MJ; Pérez-Miralles FC; López-Briz E; Alcalá-Vicente C; Galeano I; Casanova B; Poveda JL
J Neurol Sci; 2016 Jul; 366():65-67. PubMed ID: 27288778
[No Abstract] [Full Text] [Related]
2. Intrathecal 2-hydroxypropyl-beta-cyclodextrin in a single patient with Niemann-Pick C1.
Maarup TJ; Chen AH; Porter FD; Farhat NY; Ory DS; Sidhu R; Jiang X; Dickson PI
Mol Genet Metab; 2015; 116(1-2):75-9. PubMed ID: 26189084
[TBL] [Abstract][Full Text] [Related]
3. [Treatment with cyclodextrin for Niemann Pick s disease].
Cruz-Pardos S; García-Poza P; Sánchez-García FJ
Farm Hosp; 2013; 37(3):271-2. PubMed ID: 23789807
[No Abstract] [Full Text] [Related]
4. Long-Term Treatment of Niemann-Pick Type C1 Disease With Intrathecal 2-Hydroxypropyl-β-Cyclodextrin.
Berry-Kravis E; Chin J; Hoffmann A; Winston A; Stoner R; LaGorio L; Friedmann K; Hernandez M; Ory DS; Porter FD; O'Keefe JA
Pediatr Neurol; 2018 Mar; 80():24-34. PubMed ID: 29429782
[TBL] [Abstract][Full Text] [Related]
5. Anesthetic management of pediatric patients with Niemann-Pick disease type C for intrathecal 2-hydroxypropyl-β-cyclodextrin injection.
Ulloa ML; Froyshteter AB; Kret LN; Chang DP; Sarah GE; McCarthy RJ; Barnes SD; Berry-Kravis EM
Paediatr Anaesth; 2020 Jul; 30(7):766-772. PubMed ID: 32349180
[TBL] [Abstract][Full Text] [Related]
6. Endocytosis of beta-cyclodextrins is responsible for cholesterol reduction in Niemann-Pick type C mutant cells.
Rosenbaum AI; Zhang G; Warren JD; Maxfield FR
Proc Natl Acad Sci U S A; 2010 Mar; 107(12):5477-82. PubMed ID: 20212119
[TBL] [Abstract][Full Text] [Related]
7. Early experience with compassionate use of 2 hydroxypropyl-beta-cyclodextrin for Niemann-Pick type C disease: review of initial published cases.
Megías-Vericat JE; García-Robles A; Company-Albir MJ; Fernández-Megía MJ; Pérez-Miralles FC; López-Briz E; Casanova B; Poveda JL
Neurol Sci; 2017 May; 38(5):727-743. PubMed ID: 28155026
[TBL] [Abstract][Full Text] [Related]
8. Lung toxicity of hydroxypropyl-β-cyclodextrin infusion.
Chien YH; Shieh YD; Yang CY; Lee NC; Hwu WL
Mol Genet Metab; 2013 Jun; 109(2):231-2. PubMed ID: 23611577
[No Abstract] [Full Text] [Related]
9. [Report of attendance at the Parseghian Scientific Conference for Niemann-Pick Type C (NP-C) Research, South Bend, Indiana: in search of new therapeutic possibilities for a very rare illness].
Fornfeist S
Kinderkrankenschwester; 2011 Oct; 30(10):425-7. PubMed ID: 22029143
[No Abstract] [Full Text] [Related]
10. Susceptibility of outer hair cells to cholesterol chelator 2-hydroxypropyl-β-cyclodextrine is prestin-dependent.
Takahashi S; Homma K; Zhou Y; Nishimura S; Duan C; Chen J; Ahmad A; Cheatham MA; Zheng J
Sci Rep; 2016 Feb; 6():21973. PubMed ID: 26903308
[TBL] [Abstract][Full Text] [Related]
11. Efficacy of 2-Hydroxypropyl-β-cyclodextrin in Niemann-Pick Disease Type C Model Mice and Its Pharmacokinetic Analysis in a Patient with the Disease.
Tanaka Y; Yamada Y; Ishitsuka Y; Matsuo M; Shiraishi K; Wada K; Uchio Y; Kondo Y; Takeo T; Nakagata N; Higashi T; Motoyama K; Arima H; Mochinaga S; Higaki K; Ohno K; Irie T
Biol Pharm Bull; 2015; 38(6):844-51. PubMed ID: 26027824
[TBL] [Abstract][Full Text] [Related]
12. Intracisternal cyclodextrin prevents cerebellar dysfunction and Purkinje cell death in feline Niemann-Pick type C1 disease.
Vite CH; Bagel JH; Swain GP; Prociuk M; Sikora TU; Stein VM; O'Donnell P; Ruane T; Ward S; Crooks A; Li S; Mauldin E; Stellar S; De Meulder M; Kao ML; Ory DS; Davidson C; Vanier MT; Walkley SU
Sci Transl Med; 2015 Feb; 7(276):276ra26. PubMed ID: 25717099
[TBL] [Abstract][Full Text] [Related]
13. Methyl-β-cyclodextrin restores impaired autophagy flux in Niemann-Pick C1-deficient cells through activation of AMPK.
Dai S; Dulcey AE; Hu X; Wassif CA; Porter FD; Austin CP; Ory DS; Marugan J; Zheng W
Autophagy; 2017 Aug; 13(8):1435-1451. PubMed ID: 28613987
[TBL] [Abstract][Full Text] [Related]
14. Characterization of hydroxypropyl-beta-cyclodextrins used in the treatment of Niemann-Pick Disease type C1.
Yergey AL; Blank PS; Cologna SM; Backlund PS; Porter FD; Darling AJ
PLoS One; 2017; 12(4):e0175478. PubMed ID: 28414792
[TBL] [Abstract][Full Text] [Related]
15. [Inclusion Solves Insolubility -Translational Research Cycle from Bedside to Bench and Bench to Bedside for Drug Development Targeting Niemann-Pick Disease Type C].
Irie T
Yakugaku Zasshi; 2022; 142(4):389-400. PubMed ID: 35370195
[TBL] [Abstract][Full Text] [Related]
16. 2-Hydroxypropyl-β-cyclodextrins and the Blood-Brain Barrier: Considerations for Niemann-Pick Disease Type C1.
Calias P
Curr Pharm Des; 2017; 23(40):6231-6238. PubMed ID: 29065825
[TBL] [Abstract][Full Text] [Related]
17. Response letter to comments on "Cyclodextrins promote protein aggregation posing risks for therapeutic applications".
Wang M; Boddapati S; Sierks M
Biochem Biophys Res Commun; 2009 Dec; 390(4):1426-7. PubMed ID: 19852940
[No Abstract] [Full Text] [Related]
18. Long-Term Neuropsychological Outcomes from an Open-Label Phase I/IIa Trial of 2-Hydroxypropyl-β-Cyclodextrins (VTS-270) in Niemann-Pick Disease, Type C1.
Farmer CA; Thurm A; Farhat N; Bianconi S; Keener LA; Porter FD
CNS Drugs; 2019 Jul; 33(7):677-683. PubMed ID: 31187454
[TBL] [Abstract][Full Text] [Related]
19. Reply: lung toxicity of hydroxyl-β-cyclodextrin infusion.
Matsuo M; Arima H; Irie T
Mol Genet Metab; 2013 Jun; 109(2):233. PubMed ID: 23660393
[No Abstract] [Full Text] [Related]
20. Synthesis of 2-hydroxypropyl-β-cyclodextrin/pluronic-based polyrotaxanes via heterogeneous reaction as potential Niemann-Pick type C therapeutics.
Mondjinou YA; McCauliff LA; Kulkarni A; Paul L; Hyun SH; Zhang Z; Wu Z; Wirth M; Storch J; Thompson DH
Biomacromolecules; 2013 Dec; 14(12):4189-97. PubMed ID: 24180231
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
