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9. Current status of haemophilia gene therapy. High KH; Nathwani A; Spencer T; Lillicrap D Haemophilia; 2014 May; 20 Suppl 4():43-9. PubMed ID: 24762274 [TBL] [Abstract][Full Text] [Related]
10. Parvovirus-mediated gene transfer for the haemophilias. Walsh CE; Chao H Haemophilia; 2002 Mar; 8 Suppl 2():60-7. PubMed ID: 11966856 [TBL] [Abstract][Full Text] [Related]
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12. WFH State-of-the-art paper 2020: In vivo lentiviral vector gene therapy for haemophilia. Cantore A; Naldini L Haemophilia; 2021 Feb; 27 Suppl 3(Suppl 3):122-125. PubMed ID: 32537776 [TBL] [Abstract][Full Text] [Related]
13. Current and emerging gene therapies for haemophilia A and B. Kaczmarek R; Miesbach W; Ozelo MC; Chowdary P Haemophilia; 2024 Apr; 30 Suppl 3():12-20. PubMed ID: 38528615 [TBL] [Abstract][Full Text] [Related]
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15. Factor VIII delivered by haematopoietic stem cell-derived B cells corrects the phenotype of haemophilia A mice. Ramezani A; Zweier-Renn LA; Hawley RG Thromb Haemost; 2011 Apr; 105(4):676-87. PubMed ID: 21264447 [TBL] [Abstract][Full Text] [Related]
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17. Recent progress in gene therapy for hemophilia. Chuah MK; Nair N; VandenDriessche T Hum Gene Ther; 2012 Jun; 23(6):557-65. PubMed ID: 22671033 [TBL] [Abstract][Full Text] [Related]
18. Generation of an optimized lentiviral vector encoding a high-expression factor VIII transgene for gene therapy of hemophilia A. Johnston JM; Denning G; Doering CB; Spencer HT Gene Ther; 2013 Jun; 20(6):607-15. PubMed ID: 22996197 [TBL] [Abstract][Full Text] [Related]
19. Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette. Lu H; Chen L; Wang J; Huack B; Sarkar R; Zhou S; Xu R; Ding Q; Wang X; Wang H; Xiao W Hum Gene Ther; 2008 Jun; 19(6):648-54. PubMed ID: 18500941 [TBL] [Abstract][Full Text] [Related]
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