These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
4. The KLHL40 c.1516A>C is a Chinese-specific founder mutation causing nemaline myopathy 8: Report of six patients with pre- and postnatal phenotypes. Yeung KS; Yu FNY; Fung CW; Wong S; Lee HHC; Fung STH; Fung GPG; Leung KY; Chung WH; Lee YT; Ng VKS; Yu MHC; Fung JLF; Tsang MHY; Chan KYK; Chan SHS; Kan ASY; Chung BHY Mol Genet Genomic Med; 2020 Jul; 8(7):e1229. PubMed ID: 32352246 [TBL] [Abstract][Full Text] [Related]
5. Founder Mutation c.1516A>C in KLHL40 Is a Frequent Cause of Nemaline Myopathy With Hyponatremia in Ethnic Chinese. Lee HH; Wong S; Leung FY; Ho LC; Chan ST; Fung TS; Kwan KF; Yau KE; Li KW; Yau WN; Leung HC; Chen SP; Mak CM J Neuropathol Exp Neurol; 2019 Sep; 78(9):854-864. PubMed ID: 31360996 [TBL] [Abstract][Full Text] [Related]
6. Biallelic Mutations in MYPN, Encoding Myopalladin, Are Associated with Childhood-Onset, Slowly Progressive Nemaline Myopathy. Miyatake S; Mitsuhashi S; Hayashi YK; Purevjav E; Nishikawa A; Koshimizu E; Suzuki M; Yatabe K; Tanaka Y; Ogata K; Kuru S; Shiina M; Tsurusaki Y; Nakashima M; Mizuguchi T; Miyake N; Saitsu H; Ogata K; Kawai M; Towbin J; Nonaka I; Nishino I; Matsumoto N Am J Hum Genet; 2017 Jan; 100(1):169-178. PubMed ID: 28017374 [TBL] [Abstract][Full Text] [Related]
8. Clinical and molecular analysis of four unrelated Chinese families with pathogenic KLHL40 variants causing nemaline myopathy 8. Yuan H; Wang Q; Zeng X; He P; Xu W; Guo H; Liu Y; Lin Y Orphanet J Rare Dis; 2022 Apr; 17(1):149. PubMed ID: 35379254 [TBL] [Abstract][Full Text] [Related]
9. [Nemaline myopathy as a cause of neonatal hypotonia - with emphasis on personal experiences. Report of a family with two brothers affected]. Bojdo A; Obersztyn E; Wallgren-Pettersson C; Lehtokari V; Laing N; Davis M; Kułakowska Z Med Wieku Rozwoj; 2009; 13(1):5-10. PubMed ID: 19648653 [TBL] [Abstract][Full Text] [Related]
10. Congenital myopathy with cap-like structures and nemaline rods: case report and literature review. Piteau SJ; Rossiter JP; Smith RG; MacKenzie JJ Pediatr Neurol; 2014 Aug; 51(2):192-7. PubMed ID: 25079567 [TBL] [Abstract][Full Text] [Related]
11. Zebrafish models for nemaline myopathy reveal a spectrum of nemaline bodies contributing to reduced muscle function. Sztal TE; Zhao M; Williams C; Oorschot V; Parslow AC; Giousoh A; Yuen M; Hall TE; Costin A; Ramm G; Bird PI; Busch-Nentwich EM; Stemple DL; Currie PD; Cooper ST; Laing NG; Nowak KJ; Bryson-Richardson RJ Acta Neuropathol; 2015 Sep; 130(3):389-406. PubMed ID: 25931053 [TBL] [Abstract][Full Text] [Related]
12. A new homozygous missense variant in LMOD3 gene causing mild nemaline myopathy with prominent facial weakness. Segarra-Casas A; Collet R; Gonzalez-Quereda L; Vesperinas A; Caballero-Ávila M; Carbayo A; Díaz-Manera J; Rodriguez MJ; Gallardo E; Gallano P; Olivé M Neuromuscul Disord; 2023 Apr; 33(4):319-323. PubMed ID: 36893608 [TBL] [Abstract][Full Text] [Related]
13. Nemaline myopathy caused by mutations in the nebulin gene may present as a distal myopathy. Lehtokari VL; Pelin K; Herczegfalvi A; Karcagi V; Pouget J; Franques J; Pellissier JF; Figarella-Branger D; von der Hagen M; Huebner A; Schoser B; Lochmüller H; Wallgren-Pettersson C Neuromuscul Disord; 2011 Aug; 21(8):556-62. PubMed ID: 21724397 [TBL] [Abstract][Full Text] [Related]
14. Neb: a zebrafish model of nemaline myopathy due to nebulin mutation. Telfer WR; Nelson DD; Waugh T; Brooks SV; Dowling JJ Dis Model Mech; 2012 May; 5(3):389-96. PubMed ID: 22159874 [TBL] [Abstract][Full Text] [Related]
15. A novel and recurrent KLHL40 pathogenic variants in a Chinese family of multiple affected neonates with nemaline myopathy 8. Yi S; Zhang Y; Qin Z; Yi S; Zheng H; Luo J; Li Q; Wang J; Yang Q; Li M; Chen F; Zhang Q; Zhang Q; Shen Y Mol Genet Genomic Med; 2021 Jun; 9(6):e1683. PubMed ID: 33978323 [TBL] [Abstract][Full Text] [Related]
16. Mild phenotype of nemaline myopathy with sleep hypoventilation due to a mutation in the skeletal muscle alpha-actin (ACTA1) gene. Jungbluth H; Sewry CA; Brown SC; Nowak KJ; Laing NG; Wallgren-Pettersson C; Pelin K; Manzur AY; Mercuri E; Dubowitz V; Muntoni F Neuromuscul Disord; 2001 Jan; 11(1):35-40. PubMed ID: 11166164 [TBL] [Abstract][Full Text] [Related]
17. A KLHL40 3' UTR splice-altering variant causes milder NEM8, an under-appreciated disease mechanism. Dofash LNH; Monahan GV; Servián-Morilla E; Rivas E; Faiz F; Sullivan P; Oates E; Clayton J; Taylor RL; Davis MR; Beilharz T; Laing NG; Cabrera-Serrano M; Ravenscroft G Hum Mol Genet; 2023 Mar; 32(7):1127-1136. PubMed ID: 36322148 [TBL] [Abstract][Full Text] [Related]
18. Nemaline myopathies: a current view. Sewry CA; Laitila JM; Wallgren-Pettersson C J Muscle Res Cell Motil; 2019 Jun; 40(2):111-126. PubMed ID: 31228046 [TBL] [Abstract][Full Text] [Related]
19. KLHL40-Related Myopathy: A Systematic Review and Insight into a Follow-up Biomarker via a New Case Report. Buchignani B; Marinella G; Pasquariello R; Sgherri G; Frosini S; Santorelli FM; Orsini A; Battini R; Astrea G Genes (Basel); 2024 Feb; 15(2):. PubMed ID: 38397198 [TBL] [Abstract][Full Text] [Related]
20. Clinical and Histologic Findings in ACTA1-Related Nemaline Myopathy: Case Series and Review of the Literature. Moreno CAM; Abath Neto O; Donkervoort S; Hu Y; Reed UC; Oliveira ASB; Bönnemann C; Zanoteli E Pediatr Neurol; 2017 Oct; 75():11-16. PubMed ID: 28780987 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]