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10. A new severe mutation in the SLC5A7 gene related to congenital myasthenic syndrome type 20. Pardal-Fernández JM; Carrascosa-Romero MC; Álvarez S; Medina-Monzón MC; Caamaño MB; de Cabo C Neuromuscul Disord; 2018 Oct; 28(10):881-884. PubMed ID: 30172469 [TBL] [Abstract][Full Text] [Related]
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13. Electrophysiological and morphological characterization of a case of autosomal recessive congenital myasthenic syndrome with acetylcholine receptor deficiency due to a N88K rapsyn homozygous mutation. Yasaki E; Prioleau C; Barbier J; Richard P; Andreux F; Leroy JP; Dartevelle P; Koenig J; Molgó J; Fardeau M; Eymard B; Hantaï D Neuromuscul Disord; 2004 Jan; 14(1):24-32. PubMed ID: 14659409 [TBL] [Abstract][Full Text] [Related]
14. Biochemical characterization of two novel mutations in the human high-affinity choline transporter 1 identified in a patient with congenital myasthenic syndrome. Rizvi M; Truong TK; Zhou J; Batta M; Moran ES; Pappas J; Chu ML; Caluseriu O; Evrony GD; Leslie EM; Cordat E Hum Mol Genet; 2023 Apr; 32(9):1552-1564. PubMed ID: 36611016 [TBL] [Abstract][Full Text] [Related]
15. A new patient with congenital myasthenic syndrome type 20 due to compound heterozygous missense SLC5A7 variants suggests trends in genotype-phenotype correlation. Vlckova M; Prchalova D; Zimmermann P; Haberlova J; Bendova S; Moslerova V; Stranecky V; Sedlacek Z; Hancarova M Mol Genet Genomic Med; 2023 Jun; 11(6):e2154. PubMed ID: 36840359 [TBL] [Abstract][Full Text] [Related]
16. Impaired Synaptic Development, Maintenance, and Neuromuscular Transmission in LRP4-Related Myasthenia. Selcen D; Ohkawara B; Shen XM; McEvoy K; Ohno K; Engel AG JAMA Neurol; 2015 Aug; 72(8):889-96. PubMed ID: 26052878 [TBL] [Abstract][Full Text] [Related]
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18. Clinical variability of CMS-EA (congenital myasthenic syndrome with episodic apnea) due to identical CHAT mutations in two infants. Barisic N; Müller JS; Paucic-Kirincic E; Gazdik M; Lah-Tomulic K; Pertl A; Sertic J; Zurak N; Lochmüller H; Abicht A Eur J Paediatr Neurol; 2005; 9(1):7-12. PubMed ID: 15701560 [TBL] [Abstract][Full Text] [Related]
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