BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

165 related articles for article (PubMed ID: 27836529)

  • 1. Twelve years of experience with miglustat in the treatment of type 1 Gaucher disease: The Spanish ZAGAL project.
    Giraldo P; Andrade-Campos M; Alfonso P; Irun P; Atutxa K; Acedo A; Barez A; Blanes M; Diaz-Morant V; Fernández-Galán MA; Franco R; Gil-Cortes C; Giner V; Ibañez A; Latre P; Loyola I; Luño E; Hernández-Martin R; Medrano-Engay B; Puerta J; Roig I; de la Serna J; Salamero O; Villalón L; Pocovi M
    Blood Cells Mol Dis; 2018 Feb; 68():173-179. PubMed ID: 27836529
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Real-world clinical experience with long-term miglustat maintenance therapy in type 1 Gaucher disease: the ZAGAL project.
    Giraldo P; Alfonso P; Atutxa K; Fernández-Galán MA; Barez A; Franco R; Alonso D; Martin A; Latre P; Pocovi M
    Haematologica; 2009 Dec; 94(12):1771-5. PubMed ID: 19608672
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Successful switch from enzyme replacement therapy to miglustat in an adult patient with type 1 Gaucher disease: a case report.
    Giuffrida G; Lombardo R; Di Francesco E; Parrinello L; Di Raimondo F; Fiumara A
    J Med Case Rep; 2016 Nov; 10(1):315. PubMed ID: 27821156
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Oral maintenance clinical trial with miglustat for type I Gaucher disease: switch from or combination with intravenous enzyme replacement.
    Elstein D; Dweck A; Attias D; Hadas-Halpern I; Zevin S; Altarescu G; Aerts JF; van Weely S; Zimran A
    Blood; 2007 Oct; 110(7):2296-301. PubMed ID: 17609429
    [TBL] [Abstract][Full Text] [Related]  

  • 5. An open-label, noncomparative study of miglustat in type I Gaucher disease: efficacy and tolerability over 24 months of treatment.
    Pastores GM; Barnett NL; Kolodny EH
    Clin Ther; 2005 Aug; 27(8):1215-27. PubMed ID: 16199246
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Miglustat (Zavesca) in type 1 Gaucher disease: 5-year results of a post-authorisation safety surveillance programme.
    Hollak CE; Hughes D; van Schaik IN; Schwierin B; Bembi B
    Pharmacoepidemiol Drug Saf; 2009 Sep; 18(9):770-7. PubMed ID: 19507165
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Goal-oriented therapy with miglustat in Gaucher disease.
    Pastores GM; Giraldo P; Chérin P; Mehta A
    Curr Med Res Opin; 2009 Jan; 25(1):23-37. PubMed ID: 19210136
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Sustained therapeutic effects of oral miglustat (Zavesca, N-butyldeoxynojirimycin, OGT 918) in type I Gaucher disease.
    Elstein D; Hollak C; Aerts JM; van Weely S; Maas M; Cox TM; Lachmann RH; Hrebicek M; Platt FM; Butters TD; Dwek RA; Zimran A
    J Inherit Metab Dis; 2004; 27(6):757-66. PubMed ID: 15505381
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Miglustat therapy in type 1 Gaucher disease: clinical and safety outcomes in a multicenter retrospective cohort study.
    Kuter DJ; Mehta A; Hollak CE; Giraldo P; Hughes D; Belmatoug N; Brand M; Muller A; Schaaf B; Giorgino R; Zimran A
    Blood Cells Mol Dis; 2013 Aug; 51(2):116-24. PubMed ID: 23683771
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Effect of miglustat on bone disease in adults with type 1 Gaucher disease: a pooled analysis of three multinational, open-label studies.
    Pastores GM; Elstein D; Hrebícek M; Zimran A
    Clin Ther; 2007 Aug; 29(8):1645-54. PubMed ID: 17919546
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Switching from imiglucerase to miglustat for the treatment of French patients with Gaucher disease type 1: a case series.
    Serratrice C; Swiader L; Serratrice J
    J Med Case Rep; 2015 Jun; 9():146. PubMed ID: 26100396
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Changes in the atherogenic profile of patients with type 1 Gaucher disease after miglustat therapy.
    Puzo J; Alfonso P; Irun P; Gervas J; Pocovi M; Giraldo P
    Atherosclerosis; 2010 Apr; 209(2):515-9. PubMed ID: 19959168
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Short-term effect of miglustat in every day clinical use in treatment-naïve or previously treated patients with type 1 Gaucher's disease.
    Giraldo P; Latre P; Alfonso P; Acedo A; Alonso D; Barez A; Corrales A; Franco R; Roldan V; Serrano S; Pocovi M
    Haematologica; 2006 May; 91(5):703-6. PubMed ID: 16627252
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Biochemical response to substrate reduction therapy versus enzyme replacement therapy in Gaucher disease type 1 patients.
    Smid BE; Ferraz MJ; Verhoek M; Mirzaian M; Wisse P; Overkleeft HS; Hollak CE; Aerts JM
    Orphanet J Rare Dis; 2016 Mar; 11():28. PubMed ID: 27008851
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Evaluation of miglustat as maintenance therapy after enzyme therapy in adults with stable type 1 Gaucher disease: a prospective, open-label non-inferiority study.
    Cox TM; Amato D; Hollak CE; Luzy C; Silkey M; Giorgino R; Steiner RD;
    Orphanet J Rare Dis; 2012 Dec; 7():102. PubMed ID: 23270487
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Randomized, controlled trial of miglustat in Gaucher's disease type 3.
    Schiffmann R; Fitzgibbon EJ; Harris C; DeVile C; Davies EH; Abel L; van Schaik IN; Benko W; Timmons M; Ries M; Vellodi A
    Ann Neurol; 2008 Nov; 64(5):514-22. PubMed ID: 19067373
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Results from a 9-year Intensive Safety Surveillance Scheme (IS(3) ) in miglustat (Zavesca(®) )-treated patients.
    Brand M; Muller A; Alsop J; van Schaik IN; Bembi B; Hughes D
    Pharmacoepidemiol Drug Saf; 2015 Mar; 24(3):329-33. PubMed ID: 25656910
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Combined miglustat and enzyme replacement therapy in two patients with type 1 Gaucher disease: two case reports.
    Amato D; Patterson MA
    J Med Case Rep; 2018 Jan; 12(1):19. PubMed ID: 29373994
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Seven-year safety and efficacy with velaglucerase alfa for treatment-naïve adult patients with type 1 Gaucher disease.
    Zimran A; Wang N; Ogg C; Crombez E; Cohn GM; Elstein D
    Am J Hematol; 2015 Jul; 90(7):577-83. PubMed ID: 25903392
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Substrate reduction therapy with miglustat for type 1 Gaucher disease: a retrospective analysis from a single institution.
    Machaczka M; Hast R; Dahlman I; Lerner R; Klimkowska M; Engvall M; Hägglund H
    Ups J Med Sci; 2012 Mar; 117(1):28-34. PubMed ID: 22247978
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 9.