551 related articles for article (PubMed ID: 28056565)
21. Immunomodulation of transgene responses following naked DNA transfer of human factor VIII into hemophilia A mice.
Miao CH; Ye P; Thompson AR; Rawlings DJ; Ochs HD
Blood; 2006 Jul; 108(1):19-27. PubMed ID: 16507778
[TBL] [Abstract][Full Text] [Related]
22. AAV5-Factor VIII Gene Transfer in Severe Hemophilia A.
Rangarajan S; Walsh L; Lester W; Perry D; Madan B; Laffan M; Yu H; Vettermann C; Pierce GF; Wong WY; Pasi KJ
N Engl J Med; 2017 Dec; 377(26):2519-2530. PubMed ID: 29224506
[TBL] [Abstract][Full Text] [Related]
23. Interindividual variability in transgene mRNA and protein production following adeno-associated virus gene therapy for hemophilia A.
Fong S; Yates B; Sihn CR; Mattis AN; Mitchell N; Liu S; Russell CB; Kim B; Lawal A; Rangarajan S; Lester W; Bunting S; Pierce GF; Pasi KJ; Wong WY
Nat Med; 2022 Apr; 28(4):789-797. PubMed ID: 35411075
[TBL] [Abstract][Full Text] [Related]
24. Efficacy and safety of long-term prophylaxis in severe hemophilia A dogs following liver gene therapy using AAV vectors.
Sabatino DE; Lange AM; Altynova ES; Sarkar R; Zhou S; Merricks EP; Franck HG; Nichols TC; Arruda VR; Kazazian HH
Mol Ther; 2011 Mar; 19(3):442-9. PubMed ID: 21081906
[TBL] [Abstract][Full Text] [Related]
25. Targeted modifications in adeno-associated virus serotype 8 capsid improves its hepatic gene transfer efficiency in vivo.
Sen D; Gadkari RA; Sudha G; Gabriel N; Kumar YS; Selot R; Samuel R; Rajalingam S; Ramya V; Nair SC; Srinivasan N; Srivastava A; Jayandharan GR
Hum Gene Ther Methods; 2013 Apr; 24(2):104-16. PubMed ID: 23442071
[TBL] [Abstract][Full Text] [Related]
26. Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette.
Lu H; Chen L; Wang J; Huack B; Sarkar R; Zhou S; Xu R; Ding Q; Wang X; Wang H; Xiao W
Hum Gene Ther; 2008 Jun; 19(6):648-54. PubMed ID: 18500941
[TBL] [Abstract][Full Text] [Related]
27. Adenovirus-mediated factor VIII gene expression results in attenuated anti-factor VIII-specific immunity in hemophilia A mice compared with factor VIII protein infusion.
Bristol JA; Gallo-Penn A; Andrews J; Idamakanti N; Kaleko M; Connelly S
Hum Gene Ther; 2001 Sep; 12(13):1651-61. PubMed ID: 11535168
[TBL] [Abstract][Full Text] [Related]
28. Hemophilia Gene Therapy: Ready for Prime Time?
VandenDriessche T; Chuah MK
Hum Gene Ther; 2017 Nov; 28(11):1013-1023. PubMed ID: 28793786
[TBL] [Abstract][Full Text] [Related]
29. Expression of therapeutic levels of factor VIII in hemophilia A mice using a novel adeno/adeno-associated hybrid virus.
Gnatenko DV; Wu Y; Jesty J; Damon AL; Hearing P; Bahou WF
Thromb Haemost; 2004 Aug; 92(2):317-27. PubMed ID: 15269828
[TBL] [Abstract][Full Text] [Related]
30. A single adeno-associated virus (AAV)-murine factor VIII vector partially corrects the hemophilia A phenotype.
Sarkar R; Xiao W; Kazazian HH
J Thromb Haemost; 2003 Feb; 1(2):220-6. PubMed ID: 12871492
[TBL] [Abstract][Full Text] [Related]
31. B Cell Depletion Eliminates FVIII Memory B Cells and Enhances AAV8-coF8 Immune Tolerance Induction When Combined With Rapamycin.
Biswas M; Palaschak B; Kumar SRP; Rana J; Markusic DM
Front Immunol; 2020; 11():1293. PubMed ID: 32670285
[TBL] [Abstract][Full Text] [Related]
32. Heterogeneity of the immune response to adenovirus-mediated factor VIII gene therapy in different inbred hemophilic mouse strains.
Rawle FE; Shi CX; Brown B; McKinven A; Tinlin S; Graham FL; Hough C; Lillicrap D
J Gene Med; 2004 Dec; 6(12):1358-68. PubMed ID: 15493040
[TBL] [Abstract][Full Text] [Related]
33. Hematopoietic stem cells encoding porcine factor VIII induce pro-coagulant activity in hemophilia A mice with pre-existing factor VIII immunity.
Doering CB; Gangadharan B; Dukart HZ; Spencer HT
Mol Ther; 2007 Jun; 15(6):1093-9. PubMed ID: 17387335
[TBL] [Abstract][Full Text] [Related]
34. Phenotype correction of hemophilia A mice with adeno-associated virus vectors carrying the B domain-deleted canine factor VIII gene.
Ishiwata A; Mimuro J; Kashiwakura Y; Niimura M; Takano K; Ohmori T; Madoiwa S; Mizukami H; Okada T; Naka H; Yoshioka A; Ozawa K; Sakata Y
Thromb Res; 2006; 118(5):627-35. PubMed ID: 16371232
[TBL] [Abstract][Full Text] [Related]
35. Long-term follow-up of liver-directed, adeno-associated vector-mediated gene therapy in the canine model of hemophilia A.
Batty P; Mo AM; Hurlbut D; Ishida J; Yates B; Brown C; Harpell L; Hough C; Pender A; Rimmer EK; Sardo Infirri S; Winterborn A; Fong S; Lillicrap D
Blood; 2022 Dec; 140(25):2672-2683. PubMed ID: 35405003
[TBL] [Abstract][Full Text] [Related]
36. Therapeutic factor VIII levels and negligible toxicity in mouse and dog models of hemophilia A following gene therapy with high-capacity adenoviral vectors.
Chuah MK; Schiedner G; Thorrez L; Brown B; Johnston M; Gillijns V; Hertel S; Van Rooijen N; Lillicrap D; Collen D; VandenDriessche T; Kochanek S
Blood; 2003 Mar; 101(5):1734-43. PubMed ID: 12406898
[TBL] [Abstract][Full Text] [Related]
37. Exploring the Potential Feasibility of Intra-Articular Adeno-Associated Virus-Mediated Gene Therapy for Hemophilia Arthropathy.
Zhang F; Yan X; Li M; Hua B; Xiao X; Monahan PE; Sun J
Hum Gene Ther; 2020 Apr; 31(7-8):448-458. PubMed ID: 32079420
[TBL] [Abstract][Full Text] [Related]
38. CMV-beta-actin promoter directs higher expression from an adeno-associated viral vector in the liver than the cytomegalovirus or elongation factor 1 alpha promoter and results in therapeutic levels of human factor X in mice.
Xu L; Daly T; Gao C; Flotte TR; Song S; Byrne BJ; Sands MS; Parker Ponder K
Hum Gene Ther; 2001 Mar; 12(5):563-73. PubMed ID: 11268288
[TBL] [Abstract][Full Text] [Related]
39. Naked DNA transfer of Factor VIII induced transgene-specific, species-independent immune response in hemophilia A mice.
Ye P; Thompson AR; Sarkar R; Shen Z; Lillicrap DP; Kaufman RJ; Ochs HD; Rawlings DJ; Miao CH
Mol Ther; 2004 Jul; 10(1):117-26. PubMed ID: 15233948
[TBL] [Abstract][Full Text] [Related]
40. Long-term expression of human coagulation factor VIII in a tolerant mouse model using the φC31 integrase system.
Chavez CL; Keravala A; Chu JN; Farruggio AP; Cuéllar VE; Voorberg J; Calos MP
Hum Gene Ther; 2012 Apr; 23(4):390-8. PubMed ID: 22077817
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]
