577 related articles for article (PubMed ID: 28067165)
1. Gene Therapy in Fanconi Anemia: A Matter of Time, Safety and Gene Transfer Tool Efficiency.
Verhoeyen E; Roman-Rodriguez FJ; Cosset FL; Levy C; Rio P
Curr Gene Ther; 2017; 16(5):297-308. PubMed ID: 28067165
[TBL] [Abstract][Full Text] [Related]
2. Stem Cell Genetic Therapy for Fanconi Anemia - A New Hope.
Hanenberg H; Roellecke K; Wiek C
Curr Gene Ther; 2017; 16(5):309-320. PubMed ID: 28067166
[TBL] [Abstract][Full Text] [Related]
3. Advances in Gene Therapy for Fanconi Anemia.
Río P; Navarro S; Bueren JA
Hum Gene Ther; 2018 Oct; 29(10):1114-1123. PubMed ID: 30117331
[TBL] [Abstract][Full Text] [Related]
4. Phenotypic correction of Fanconi anemia cells in the murine bone marrow after carrier cell mediated delivery of lentiviral vector.
Chakkaramakkil Verghese S; Goloviznina NA; Kurre P
Stem Cell Res Ther; 2016 Nov; 7(1):170. PubMed ID: 27865213
[TBL] [Abstract][Full Text] [Related]
5. Rapid lentiviral transduction preserves the engraftment potential of Fanca(-/-) hematopoietic stem cells.
Müller LU; Milsom MD; Kim MO; Schambach A; Schuesler T; Williams DA
Mol Ther; 2008 Jun; 16(6):1154-60. PubMed ID: 18398427
[TBL] [Abstract][Full Text] [Related]
6. Anchored Lentiviral Vector Episomes for Stem Cell Gene Therapy in Fanconi Anemia.
Verghese SC; Kurre P
Curr Gene Ther; 2017; 16(5):329-337. PubMed ID: 28093967
[TBL] [Abstract][Full Text] [Related]
7. Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34
Río P; Navarro S; Guenechea G; Sánchez-Domínguez R; Lamana ML; Yañez R; Casado JA; Mehta PA; Pujol MR; Surrallés J; Charrier S; Galy A; Segovia JC; Díaz de Heredia C; Sevilla J; Bueren JA
Blood; 2017 Sep; 130(13):1535-1542. PubMed ID: 28801449
[TBL] [Abstract][Full Text] [Related]
8. Functional correction of fanconi anemia group C hematopoietic cells by the use of a novel lentiviral vector.
Yamada K; Olsen JC; Patel M; Rao KW; Walsh CE
Mol Ther; 2001 Apr; 3(4):485-90. PubMed ID: 11319908
[TBL] [Abstract][Full Text] [Related]
9. Lentiviral-Mediated Gene Therapy in Fanconi Anemia-A Mice Reveals Long-Term Engraftment and Continuous Turnover of Corrected HSCs.
Molina-Estevez FJ; Nowrouzi A; Lozano ML; Galy A; Charrier S; von Kalle C; Guenechea G; Bueren JA; Schmidt M
Curr Gene Ther; 2015; 15(6):550-62. PubMed ID: 26415575
[TBL] [Abstract][Full Text] [Related]
10. Lessons Learned from Two Decades of Clinical Trial Experience in Gene Therapy for Fanconi Anemia.
Adair JE; Sevilla J; Heredia CD; Becker PS; Kiem HP; Bueren J
Curr Gene Ther; 2017; 16(5):338-348. PubMed ID: 28103787
[TBL] [Abstract][Full Text] [Related]
11. Minimal conditioning in Fanconi anemia promotes multi-lineage marrow engraftment at 10-fold lower cell doses.
Haworth KG; Ironside C; Ramirez MA; Weitz S; Beard BC; Schwartz JD; Adair JE; Kiem HP
J Gene Med; 2018 Oct; 20(10-11):e3050. PubMed ID: 30129972
[TBL] [Abstract][Full Text] [Related]
12. Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia.
Río P; Navarro S; Wang W; Sánchez-Domínguez R; Pujol RM; Segovia JC; Bogliolo M; Merino E; Wu N; Salgado R; Lamana ML; Yañez RM; Casado JA; Giménez Y; Román-Rodríguez FJ; Álvarez L; Alberquilla O; Raimbault A; Guenechea G; Lozano ML; Cerrato L; Hernando M; Gálvez E; Hladun R; Giralt I; Barquinero J; Galy A; García de Andoín N; López R; Catalá A; Schwartz JD; Surrallés J; Soulier J; Schmidt M; Díaz de Heredia C; Sevilla J; Bueren JA
Nat Med; 2019 Sep; 25(9):1396-1401. PubMed ID: 31501599
[TBL] [Abstract][Full Text] [Related]
13. Retroviral mediated gene transfer of the Fanconi anemia complementation group C gene to hematopoietic progenitors of group C patients.
Liu JM; Young NS; Walsh CE; Cottler-Fox M; Carter C; Dunbar C; Barrett AJ; Emmons R
Hum Gene Ther; 1997 Sep; 8(14):1715-30. PubMed ID: 9322874
[TBL] [Abstract][Full Text] [Related]
14. Lentiviral-mediated genetic correction of hematopoietic and mesenchymal progenitor cells from Fanconi anemia patients.
Jacome A; Navarro S; Río P; Yañez RM; González-Murillo A; Lozano ML; Lamana ML; Sevilla J; Olive T; Diaz-Heredia C; Badell I; Estella J; Madero L; Guenechea G; Casado J; Segovia JC; Bueren JA
Mol Ther; 2009 Jun; 17(6):1083-92. PubMed ID: 19277017
[TBL] [Abstract][Full Text] [Related]
15. Gene therapy of Fanconi anemia: preclinical efficacy using lentiviral vectors.
Galimi F; Noll M; Kanazawa Y; Lax T; Chen C; Grompe M; Verma IM
Blood; 2002 Oct; 100(8):2732-6. PubMed ID: 12351379
[TBL] [Abstract][Full Text] [Related]
16. Engraftment of hematopoietic progenitor cells transduced with the Fanconi anemia group C gene (FANCC).
Liu JM; Kim S; Read EJ; Futaki M; Dokal I; Carter CS; Leitman SF; Pensiero M; Young NS; Walsh CE
Hum Gene Ther; 1999 Sep; 10(14):2337-46. PubMed ID: 10515453
[TBL] [Abstract][Full Text] [Related]
17. A novel lentiviral vector targets gene transfer into human hematopoietic stem cells in marrow from patients with bone marrow failure syndrome and in vivo in humanized mice.
Frecha C; Costa C; Nègre D; Amirache F; Trono D; Rio P; Bueren J; Cosset FL; Verhoeyen E
Blood; 2012 Feb; 119(5):1139-50. PubMed ID: 22117040
[TBL] [Abstract][Full Text] [Related]
18. Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector.
Becker PS; Taylor JA; Trobridge GD; Zhao X; Beard BC; Chien S; Adair J; Kohn DB; Wagner JE; Shimamura A; Kiem HP
Gene Ther; 2010 Oct; 17(10):1244-52. PubMed ID: 20485382
[TBL] [Abstract][Full Text] [Related]
19. Transduction of CD34-enriched human peripheral and umbilical cord blood progenitors using a retroviral vector with the Fanconi anemia group C gene.
Walsh CE; Mann MM; Emmons RV; Wang S; Liu JM
J Investig Med; 1995 Aug; 43(4):379-85. PubMed ID: 7552587
[TBL] [Abstract][Full Text] [Related]
20. Phenotype correction of Fanconi anemia group A hematopoietic stem cells using lentiviral vector.
Yamada K; Ramezani A; Hawley RG; Ebell W; Arwert F; Arnold LW; Walsh CE
Mol Ther; 2003 Oct; 8(4):600-10. PubMed ID: 14529833
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]