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3. CRISPR-Based Therapeutic Gene Editing for Duchenne Muscular Dystrophy: Advances, Challenges and Perspectives. Chen G; Wei T; Yang H; Li G; Li H Cells; 2022 Sep; 11(19):. PubMed ID: 36230926 [TBL] [Abstract][Full Text] [Related]
4. The emerging role of viral vectors as vehicles for DMD gene editing. Maggio I; Chen X; Gonçalves MA Genome Med; 2016 May; 8(1):59. PubMed ID: 27215286 [TBL] [Abstract][Full Text] [Related]
5. Cell and gene therapy in Duchenne muscular dystrophy. Morgan JE Hum Gene Ther; 1994 Feb; 5(2):165-73. PubMed ID: 7514447 [TBL] [Abstract][Full Text] [Related]
6. Dystrophin-glycoprotein complex: its role in the molecular pathogenesis of muscular dystrophies. Matsumura K; Campbell KP Muscle Nerve; 1994 Jan; 17(1):2-15. PubMed ID: 8264699 [TBL] [Abstract][Full Text] [Related]
7. Ex vivo gene editing of the dystrophin gene in muscle stem cells mediated by peptide nucleic acid single stranded oligodeoxynucleotides induces stable expression of dystrophin in a mouse model for Duchenne muscular dystrophy. Nik-Ahd F; Bertoni C Stem Cells; 2014 Jul; 32(7):1817-30. PubMed ID: 24753122 [TBL] [Abstract][Full Text] [Related]
8. Duchenne muscular dystrophy: genome editing gives new hope for treatment. Crispi V; Matsakas A Postgrad Med J; 2018 May; 94(1111):296-304. PubMed ID: 29386334 [TBL] [Abstract][Full Text] [Related]
10. Toward the correction of muscular dystrophy by gene editing. Olson EN Proc Natl Acad Sci U S A; 2021 Jun; 118(22):. PubMed ID: 34074727 [TBL] [Abstract][Full Text] [Related]
16. A Single CRISPR-Cas9 Deletion Strategy that Targets the Majority of DMD Patients Restores Dystrophin Function in hiPSC-Derived Muscle Cells. Young CS; Hicks MR; Ermolova NV; Nakano H; Jan M; Younesi S; Karumbayaram S; Kumagai-Cresse C; Wang D; Zack JA; Kohn DB; Nakano A; Nelson SF; Miceli MC; Spencer MJ; Pyle AD Cell Stem Cell; 2016 Apr; 18(4):533-40. PubMed ID: 26877224 [TBL] [Abstract][Full Text] [Related]
17. [Molecular pathology of Duchenne and Becker muscular dystrophy]. Gilgenkrantz H; Chelly J; Récan D; Chafey P; Kaplan JC C R Seances Soc Biol Fil; 1992; 186(4):349-53. PubMed ID: 1301222 [TBL] [Abstract][Full Text] [Related]
18. [Muscular dystrophies detected by immunophenotyping and genotype analysis (mRNA and DNA)]. Lukás Z; Vojtísková M; Fajkusová L; Bednarík J; Kadanka Z; Hájek J; Hermanová M; Vohánka S; Vytopil M Cesk Patol; 2001 Nov; 37(4):137-45. PubMed ID: 11813630 [TBL] [Abstract][Full Text] [Related]
19. [Duchenne muscular dystrophy]. Ishiura S; Sugita H No To Shinkei; 1991 May; 43(5):405-9. PubMed ID: 1910927 [No Abstract] [Full Text] [Related]