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23. Survival among patients receiving eteplirsen for up to 8 years for the treatment of Duchenne muscular dystrophy and contextualization with natural history controls. Iff J; Done N; Tuttle E; Zhong Y; Wei F; Darras BT; McDonald CM; Mercuri E; Muntoni F Muscle Nerve; 2024 Jul; 70(1):60-70. PubMed ID: 38482981 [TBL] [Abstract][Full Text] [Related]
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33. Shorter Phosphorodiamidate Morpholino Splice-Switching Oligonucleotides May Increase Exon-Skipping Efficacy in DMD. Akpulat U; Wang H; Becker K; Contreras A; Partridge TA; Novak JS; Cirak S Mol Ther Nucleic Acids; 2018 Dec; 13():534-542. PubMed ID: 30396145 [TBL] [Abstract][Full Text] [Related]
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