These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.
26. C-terminal-truncated microdystrophin recruits dystrobrevin and syntrophin to the dystrophin-associated glycoprotein complex and reduces muscular dystrophy in symptomatic utrophin/dystrophin double-knockout mice. Yue Y; Liu M; Duan D Mol Ther; 2006 Jul; 14(1):79-87. PubMed ID: 16563874 [TBL] [Abstract][Full Text] [Related]
27. AAV genome loss from dystrophic mouse muscles during AAV-U7 snRNA-mediated exon-skipping therapy. Le Hir M; Goyenvalle A; Peccate C; Précigout G; Davies KE; Voit T; Garcia L; Lorain S Mol Ther; 2013 Aug; 21(8):1551-8. PubMed ID: 23752313 [TBL] [Abstract][Full Text] [Related]
28. Systemic delivery of full-length dystrophin in Duchenne muscular dystrophy mice. Zhou Y; Zhang C; Xiao W; Herzog RW; Han R Nat Commun; 2024 Jul; 15(1):6141. PubMed ID: 39034316 [TBL] [Abstract][Full Text] [Related]
29. Triple trans-splicing adeno-associated virus vectors capable of transferring the coding sequence for full-length dystrophin protein into dystrophic mice. Koo T; Popplewell L; Athanasopoulos T; Dickson G Hum Gene Ther; 2014 Feb; 25(2):98-108. PubMed ID: 24191945 [TBL] [Abstract][Full Text] [Related]
32. Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy. Birch SM; Lawlor MW; Conlon TJ; Guo LJ; Crudele JM; Hawkins EC; Nghiem PP; Ahn M; Meng H; Beatka MJ; Fickau BA; Prieto JC; Styner MA; Struharik MJ; Shanks C; Brown KJ; Golebiowski D; Bettis AK; Balog-Alvarez CJ; Clement N; Coleman KE; Corti M; Pan X; Hauschka SD; Gonzalez JP; Morris CA; Schneider JS; Duan D; Chamberlain JS; Byrne BJ; Kornegay JN Sci Transl Med; 2023 Jan; 15(677):eabo1815. PubMed ID: 36599002 [TBL] [Abstract][Full Text] [Related]
33. Enhanced in vivo delivery of antisense oligonucleotides to restore dystrophin expression in adult mdx mouse muscle. Wells KE; Fletcher S; Mann CJ; Wilton SD; Wells DJ FEBS Lett; 2003 Sep; 552(2-3):145-9. PubMed ID: 14527677 [TBL] [Abstract][Full Text] [Related]
34. Human α7 Integrin Gene (ITGA7) Delivered by Adeno-Associated Virus Extends Survival of Severely Affected Dystrophin/Utrophin-Deficient Mice. Heller KN; Montgomery CL; Shontz KM; Clark KR; Mendell JR; Rodino-Klapac LR Hum Gene Ther; 2015 Oct; 26(10):647-56. PubMed ID: 26076707 [TBL] [Abstract][Full Text] [Related]
35. In Silico Structural Prediction for the Generation of Novel Performant Midi-Dystrophins Based on Intein-Mediated Dual AAV Approach. Palmieri L; Ferrand M; Vu Hong A; Richard I; Albini S Int J Mol Sci; 2024 Sep; 25(19):. PubMed ID: 39408775 [TBL] [Abstract][Full Text] [Related]
36. Improvement of the mdx mouse dystrophic phenotype by systemic in utero AAV8 delivery of a minidystrophin gene. Koppanati BM; Li J; Reay DP; Wang B; Daood M; Zheng H; Xiao X; Watchko JF; Clemens PR Gene Ther; 2010 Nov; 17(11):1355-62. PubMed ID: 20535217 [TBL] [Abstract][Full Text] [Related]
37. Protein-Anchoring Therapy of Biglycan for Mdx Mouse Model of Duchenne Muscular Dystrophy. Ito M; Ehara Y; Li J; Inada K; Ohno K Hum Gene Ther; 2017 May; 28(5):428-436. PubMed ID: 27485975 [TBL] [Abstract][Full Text] [Related]
38. Safe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus. Yue Y; Pan X; Hakim CH; Kodippili K; Zhang K; Shin JH; Yang HT; McDonald T; Duan D Hum Mol Genet; 2015 Oct; 24(20):5880-90. PubMed ID: 26264580 [TBL] [Abstract][Full Text] [Related]
39. Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD). Athanasopoulos T; Graham IR; Foster H; Dickson G Gene Ther; 2004 Oct; 11 Suppl 1():S109-21. PubMed ID: 15454965 [TBL] [Abstract][Full Text] [Related]
40. Microdystrophin ameliorates muscular dystrophy in the canine model of duchenne muscular dystrophy. Shin JH; Pan X; Hakim CH; Yang HT; Yue Y; Zhang K; Terjung RL; Duan D Mol Ther; 2013 Apr; 21(4):750-7. PubMed ID: 23319056 [TBL] [Abstract][Full Text] [Related] [Previous] [Next] [New Search]