283 related articles for article (PubMed ID: 28566761)
1. Proof-of-Concept Gene Editing for the Murine Model of Inducible Arginase-1 Deficiency.
Sin YY; Price PR; Ballantyne LL; Funk CD
Sci Rep; 2017 May; 7(1):2585. PubMed ID: 28566761
[TBL] [Abstract][Full Text] [Related]
2. Arginase-1 deficiency.
Sin YY; Baron G; Schulze A; Funk CD
J Mol Med (Berl); 2015 Dec; 93(12):1287-96. PubMed ID: 26467175
[TBL] [Abstract][Full Text] [Related]
3. Minimal ureagenesis is necessary for survival in the murine model of hyperargininemia treated by AAV-based gene therapy.
Hu C; Tai DS; Park H; Cantero G; Cantero-Nieto G; Chan E; Yudkoff M; Cederbaum SD; Lipshutz GS
Gene Ther; 2015 Feb; 22(2):111-5. PubMed ID: 25474440
[TBL] [Abstract][Full Text] [Related]
4. Transplantation of Gene-Edited Hepatocyte-like Cells Modestly Improves Survival of Arginase-1-Deficient Mice.
Sin YY; Ballantyne LL; Richmond CR; Funk CD
Mol Ther Nucleic Acids; 2018 Mar; 10():122-130. PubMed ID: 29499927
[TBL] [Abstract][Full Text] [Related]
5. Inducible arginase 1 deficiency in mice leads to hyperargininemia and altered amino acid metabolism.
Sin YY; Ballantyne LL; Mukherjee K; St Amand T; Kyriakopoulou L; Schulze A; Funk CD
PLoS One; 2013; 8(11):e80001. PubMed ID: 24224027
[TBL] [Abstract][Full Text] [Related]
6. Interrogation of the Atherosclerosis-Associated
Wang X; Raghavan A; Peters DT; Pashos EE; Rader DJ; Musunuru K
Arterioscler Thromb Vasc Biol; 2018 Jan; 38(1):76-82. PubMed ID: 29097363
[TBL] [Abstract][Full Text] [Related]
7. Rescue of the Functional Alterations of Motor Cortical Circuits in Arginase Deficiency by Neonatal Gene Therapy.
Cantero G; Liu XB; Mervis RF; Lazaro MT; Cederbaum SD; Golshani P; Lipshutz GS
J Neurosci; 2016 Jun; 36(25):6680-90. PubMed ID: 27335400
[TBL] [Abstract][Full Text] [Related]
8. Lipid nanoparticle-targeted mRNA therapy as a treatment for the inherited metabolic liver disorder arginase deficiency.
Truong B; Allegri G; Liu XB; Burke KE; Zhu X; Cederbaum SD; Häberle J; Martini PGV; Lipshutz GS
Proc Natl Acad Sci U S A; 2019 Oct; 116(42):21150-21159. PubMed ID: 31501335
[TBL] [Abstract][Full Text] [Related]
9. Myocyte-mediated arginase expression controls hyperargininemia but not hyperammonemia in arginase-deficient mice.
Hu C; Kasten J; Park H; Bhargava R; Tai DS; Grody WW; Nguyen QG; Hauschka SD; Cederbaum SD; Lipshutz GS
Mol Ther; 2014 Oct; 22(10):1792-802. PubMed ID: 24888478
[TBL] [Abstract][Full Text] [Related]
10. CRISPR-Cas9: a promising tool for gene editing on induced pluripotent stem cells.
Kim EJ; Kang KH; Ju JH
Korean J Intern Med; 2017 Jan; 32(1):42-61. PubMed ID: 28049282
[TBL] [Abstract][Full Text] [Related]
11. Liver-specific knockout of arginase-1 leads to a profound phenotype similar to inducible whole body arginase-1 deficiency.
Ballantyne LL; Sin YY; Al-Dirbashi OY; Li X; Hurlbut DJ; Funk CD
Mol Genet Metab Rep; 2016 Dec; 9():54-60. PubMed ID: 27761413
[TBL] [Abstract][Full Text] [Related]
12. CRISPR/Cas9 Genome Editing: A Promising Tool for Therapeutic Applications of Induced Pluripotent Stem Cells.
Zhang Y; Sastre D; Wang F
Curr Stem Cell Res Ther; 2018; 13(4):243-251. PubMed ID: 29446747
[TBL] [Abstract][Full Text] [Related]
13. Arginase I mRNA therapy - a novel approach to rescue arginase 1 enzyme deficiency.
Asrani KH; Cheng L; Cheng CJ; Subramanian RR
RNA Biol; 2018; 15(7):914-922. PubMed ID: 29923457
[TBL] [Abstract][Full Text] [Related]
14. Lethal phenotype in conditional late-onset arginase 1 deficiency in the mouse.
Kasten J; Hu C; Bhargava R; Park H; Tai D; Byrne JA; Marescau B; De Deyn PP; Schlichting L; Grody WW; Cederbaum SD; Lipshutz GS
Mol Genet Metab; 2013 Nov; 110(3):222-30. PubMed ID: 23920045
[TBL] [Abstract][Full Text] [Related]
15. Hepatic arginase deficiency fosters dysmyelination during postnatal CNS development.
Liu XB; Haney JR; Cantero G; Lambert JR; Otero-Garcia M; Truong B; Gropman A; Cobos I; Cederbaum SD; Lipshutz GS
JCI Insight; 2019 Sep; 4(17):. PubMed ID: 31484827
[TBL] [Abstract][Full Text] [Related]
16. The role and control of arginine levels in arginase 1 deficiency.
Diaz GA; Bechter M; Cederbaum SD
J Inherit Metab Dis; 2023 Jan; 46(1):3-14. PubMed ID: 36175366
[TBL] [Abstract][Full Text] [Related]
17. Restoring Ureagenesis in Hepatocytes by CRISPR/Cas9-mediated Genomic Addition to Arginase-deficient Induced Pluripotent Stem Cells.
Lee PC; Truong B; Vega-Crespo A; Gilmore WB; Hermann K; Angarita SA; Tang JK; Chang KM; Wininger AE; Lam AK; Schoenberg BE; Cederbaum SD; Pyle AD; Byrne JA; Lipshutz GS
Mol Ther Nucleic Acids; 2016 Nov; 5(11):e394. PubMed ID: 27898091
[TBL] [Abstract][Full Text] [Related]
18. Gene Editing With CRISPR/Cas9 RNA-Directed Nuclease.
Doetschman T; Georgieva T
Circ Res; 2017 Mar; 120(5):876-894. PubMed ID: 28254804
[TBL] [Abstract][Full Text] [Related]
19. Characterization and mRNA expression analysis of a novel ARG1 splicing mutation causing hyperargininemia.
Villegas-Ruiz V; Campos-Garcia FJ; Contreras-Capetillo S; Moreno-Graciano CM; Maldonado-Solis FA; Maldonado-Solis MA; Zenteno JC
Clin Biochem; 2015 Dec; 48(18):1273-6. PubMed ID: 26169240
[TBL] [Abstract][Full Text] [Related]
20. AAV-based gene therapy prevents neuropathology and results in normal cognitive development in the hyperargininemic mouse.
Lee EK; Hu C; Bhargava R; Ponnusamy R; Park H; Novicoff S; Rozengurt N; Marescau B; De Deyn P; Stout D; Schlichting L; Grody WW; Cederbaum SD; Lipshutz GS
Gene Ther; 2013 Aug; 20(8):785-96. PubMed ID: 23388701
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]