BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

328 related articles for article (PubMed ID: 28752467)

  • 1. Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency.
    Gruntman AM; Flotte TR
    Methods Mol Biol; 2017; 1639():267-275. PubMed ID: 28752467
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Amelioration of Alpha-1 Antitrypsin Deficiency Diseases with Genome Editing in Transgenic Mice.
    Shen S; Sanchez ME; Blomenkamp K; Corcoran EM; Marco E; Yudkoff CJ; Jiang H; Teckman JH; Bumcrot D; Albright CF
    Hum Gene Ther; 2018 Aug; 29(8):861-873. PubMed ID: 29641323
    [TBL] [Abstract][Full Text] [Related]  

  • 3. In Vivo Genome Editing Partially Restores Alpha1-Antitrypsin in a Murine Model of AAT Deficiency.
    Song CQ; Wang D; Jiang T; O'Connor K; Tang Q; Cai L; Li X; Weng Z; Yin H; Gao G; Mueller C; Flotte TR; Xue W
    Hum Gene Ther; 2018 Aug; 29(8):853-860. PubMed ID: 29597895
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Alpha1-antitrypsin deficiency: from genotype to childhood disease.
    Marcus N; Teckman JH; Perlmutter DH
    J Pediatr Gastroenterol Nutr; 1998 Jul; 27(1):65-74. PubMed ID: 9669729
    [No Abstract]   [Full Text] [Related]  

  • 5. Therapeutic Genome Editing With CRISPR/Cas9 in a Humanized Mouse Model Ameliorates α1-antitrypsin Deficiency Phenotype.
    Bjursell M; Porritt MJ; Ericson E; Taheri-Ghahfarokhi A; Clausen M; Magnusson L; Admyre T; Nitsch R; Mayr L; Aasehaug L; Seeliger F; Maresca M; Bohlooly-Y M; Wiseman J
    EBioMedicine; 2018 Mar; 29():104-111. PubMed ID: 29500128
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Alpha-1 Antitrypsin Deficiency as a Candidate for Gene Editing.
    Flotte TR
    Hum Gene Ther; 2018 Aug; 29(8):843-844. PubMed ID: 30096037
    [No Abstract]   [Full Text] [Related]  

  • 7. Emerging Concepts and Human Trials in Alpha-1-Antitrypsin Deficiency Liver Disease.
    Teckman JH
    Semin Liver Dis; 2017 May; 37(2):152-158. PubMed ID: 28564723
    [No Abstract]   [Full Text] [Related]  

  • 8. Advances in Alpha-1 Antitrypsin Gene Therapy.
    Lorincz R; Curiel DT
    Am J Respir Cell Mol Biol; 2020 Nov; 63(5):560-570. PubMed ID: 32668173
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Gene therapy for alpha-1 antitrypsin deficiency: an update.
    Pires Ferreira D; Gruntman AM; Flotte TR
    Expert Opin Biol Ther; 2023 Mar; 23(3):283-291. PubMed ID: 36825473
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Alpha-1 antitrypsin deficiency: a conformational disease associated with lung and liver manifestations.
    Greene CM; Miller SD; Carroll T; McLean C; O'Mahony M; Lawless MW; O'Neill SJ; Taggart CC; McElvaney NG
    J Inherit Metab Dis; 2008 Feb; 31(1):21-34. PubMed ID: 18193338
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Alpha-1-antitrypsin deficiency: current concepts.
    Mulgrew AT; Taggart CC; McElvaney NG
    Lung; 2007; 185(4):191-201. PubMed ID: 17562108
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Recent advancements in understanding the genetic involvement of alpha-1 antitrypsin deficiency associated lung disease: a look at future precision medicine approaches.
    Ghosh AJ; Hobbs BD
    Expert Rev Respir Med; 2022 Feb; 16(2):173-182. PubMed ID: 35025710
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Clinical manifestations of alpha 1-antitrypsin deficiency.
    Perlmutter DH
    Gastroenterol Clin North Am; 1995 Mar; 24(1):27-43. PubMed ID: 7729860
    [TBL] [Abstract][Full Text] [Related]  

  • 14. [Hepatic involvement in hereditary alpha-1-antitrypsin deficiency].
    Lachaux A; Dumortier J
    Rev Mal Respir; 2014 Apr; 31(4):357-64. PubMed ID: 24750955
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Alpha-1 antitrypsin deficiency: current therapy and emerging targets.
    McElvaney OF; Fraughen DD; McElvaney OJ; Carroll TP; McElvaney NG
    Expert Rev Respir Med; 2023 Mar; 17(3):191-202. PubMed ID: 36896570
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Evaluation of cytosine base editing and adenine base editing as a potential treatment for alpha-1 antitrypsin deficiency.
    Packer MS; Chowdhary V; Lung G; Cheng LI; Aratyn-Schaus Y; Leboeuf D; Smith S; Shah A; Chen D; Zieger M; Cafferty BJ; Yan B; Ciaramella G; Gregoire FM; Mueller C
    Mol Ther; 2022 Apr; 30(4):1396-1406. PubMed ID: 35121111
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Survival Advantage of Both Human Hepatocyte Xenografts and Genome-Edited Hepatocytes for Treatment of α-1 Antitrypsin Deficiency.
    Borel F; Tang Q; Gernoux G; Greer C; Wang Z; Barzel A; Kay MA; Shultz LD; Greiner DL; Flotte TR; Brehm MA; Mueller C
    Mol Ther; 2017 Nov; 25(11):2477-2489. PubMed ID: 29032169
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Current status of gene therapy for α-1 antitrypsin deficiency.
    Loring HS; Flotte TR
    Expert Opin Biol Ther; 2015 Mar; 15(3):329-36. PubMed ID: 25363251
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Anti-Proteases and Alpha-1 Antitrypsin Augmentation Therapy.
    Strange C
    Respir Care; 2018 Jun; 63(6):690-698. PubMed ID: 29794204
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Alpha-1-antitrypsin deficiency: diagnosis and treatment.
    Perlmutter DH
    Clin Liver Dis; 2004 Nov; 8(4):839-59, viii-ix. PubMed ID: 15464658
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 17.