292 related articles for article (PubMed ID: 28899930)
1. Therapeutic gene editing in CD34
Diez B; Genovese P; Roman-Rodriguez FJ; Alvarez L; Schiroli G; Ugalde L; Rodriguez-Perales S; Sevilla J; Diaz de Heredia C; Holmes MC; Lombardo A; Naldini L; Bueren JA; Rio P
EMBO Mol Med; 2017 Nov; 9(11):1574-1588. PubMed ID: 28899930
[TBL] [Abstract][Full Text] [Related]
2. NHEJ-Mediated Repair of CRISPR-Cas9-Induced DNA Breaks Efficiently Corrects Mutations in HSPCs from Patients with Fanconi Anemia.
Román-Rodríguez FJ; Ugalde L; Álvarez L; Díez B; Ramírez MJ; Risueño C; Cortón M; Bogliolo M; Bernal S; March F; Ayuso C; Hanenberg H; Sevilla J; Rodríguez-Perales S; Torres-Ruiz R; Surrallés J; Bueren JA; Río P
Cell Stem Cell; 2019 Nov; 25(5):607-621.e7. PubMed ID: 31543367
[TBL] [Abstract][Full Text] [Related]
3. Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34
Río P; Navarro S; Guenechea G; Sánchez-Domínguez R; Lamana ML; Yañez R; Casado JA; Mehta PA; Pujol MR; Surrallés J; Charrier S; Galy A; Segovia JC; Díaz de Heredia C; Sevilla J; Bueren JA
Blood; 2017 Sep; 130(13):1535-1542. PubMed ID: 28801449
[TBL] [Abstract][Full Text] [Related]
4. Targeted gene therapy and cell reprogramming in Fanconi anemia.
Rio P; Baños R; Lombardo A; Quintana-Bustamante O; Alvarez L; Garate Z; Genovese P; Almarza E; Valeri A; Díez B; Navarro S; Torres Y; Trujillo JP; Murillas R; Segovia JC; Samper E; Surralles J; Gregory PD; Holmes MC; Naldini L; Bueren JA
EMBO Mol Med; 2014 Jun; 6(6):835-48. PubMed ID: 24859981
[TBL] [Abstract][Full Text] [Related]
5. Numbers of long-term hematopoietic stem cells from bone marrow of fanca and fancc knockout mice can be greatly enhanced by their collection and processing in physioxia conditions.
Broxmeyer HE; Capitano ML; Cooper S; Potchanant ES; Clapp DW
Blood Cells Mol Dis; 2021 Feb; 86():102492. PubMed ID: 32896825
[TBL] [Abstract][Full Text] [Related]
6. Transduction of CD34-enriched human peripheral and umbilical cord blood progenitors using a retroviral vector with the Fanconi anemia group C gene.
Walsh CE; Mann MM; Emmons RV; Wang S; Liu JM
J Investig Med; 1995 Aug; 43(4):379-85. PubMed ID: 7552587
[TBL] [Abstract][Full Text] [Related]
7. Therapeutic base editing of human hematopoietic stem cells.
Zeng J; Wu Y; Ren C; Bonanno J; Shen AH; Shea D; Gehrke JM; Clement K; Luk K; Yao Q; Kim R; Wolfe SA; Manis JP; Pinello L; Joung JK; Bauer DE
Nat Med; 2020 Apr; 26(4):535-541. PubMed ID: 32284612
[TBL] [Abstract][Full Text] [Related]
8. In vitro phenotypic correction of hematopoietic progenitors from Fanconi anemia group A knockout mice.
Río P; Segovia JC; Hanenberg H; Casado JA; Martínez J; Göttsche K; Cheng NC; Van de Vrugt HJ; Arwert F; Joenje H; Bueren JA
Blood; 2002 Sep; 100(6):2032-9. PubMed ID: 12200363
[TBL] [Abstract][Full Text] [Related]
9. p53-TP53-Induced Glycolysis Regulator Mediated Glycolytic Suppression Attenuates DNA Damage and Genomic Instability in Fanconi Anemia Hematopoietic Stem Cells.
Li X; Wu L; Zopp M; Kopelov S; Du W
Stem Cells; 2019 Jul; 37(7):937-947. PubMed ID: 30977208
[TBL] [Abstract][Full Text] [Related]
10. Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia.
Río P; Navarro S; Wang W; Sánchez-Domínguez R; Pujol RM; Segovia JC; Bogliolo M; Merino E; Wu N; Salgado R; Lamana ML; Yañez RM; Casado JA; Giménez Y; Román-Rodríguez FJ; Álvarez L; Alberquilla O; Raimbault A; Guenechea G; Lozano ML; Cerrato L; Hernando M; Gálvez E; Hladun R; Giralt I; Barquinero J; Galy A; García de Andoín N; López R; Catalá A; Schwartz JD; Surrallés J; Soulier J; Schmidt M; Díaz de Heredia C; Sevilla J; Bueren JA
Nat Med; 2019 Sep; 25(9):1396-1401. PubMed ID: 31501599
[TBL] [Abstract][Full Text] [Related]
11. Advances in Gene Therapy for Fanconi Anemia.
Río P; Navarro S; Bueren JA
Hum Gene Ther; 2018 Oct; 29(10):1114-1123. PubMed ID: 30117331
[TBL] [Abstract][Full Text] [Related]
12. Lentiviral-mediated genetic correction of hematopoietic and mesenchymal progenitor cells from Fanconi anemia patients.
Jacome A; Navarro S; Río P; Yañez RM; González-Murillo A; Lozano ML; Lamana ML; Sevilla J; Olive T; Diaz-Heredia C; Badell I; Estella J; Madero L; Guenechea G; Casado J; Segovia JC; Bueren JA
Mol Ther; 2009 Jun; 17(6):1083-92. PubMed ID: 19277017
[TBL] [Abstract][Full Text] [Related]
13. TALEN mediated gene editing in a mouse model of Fanconi anemia.
Pino-Barrio MJ; Giménez Y; Villanueva M; Hildenbeutel M; Sánchez-Dominguez R; Rodríguez-Perales S; Pujol R; Surrallés J; Río P; Cathomen T; Mussolino C; Bueren JA; Navarro S
Sci Rep; 2020 Apr; 10(1):6997. PubMed ID: 32332829
[TBL] [Abstract][Full Text] [Related]
14. Phenotypic correction of Fanconi anemia in human hematopoietic cells with a recombinant adeno-associated virus vector.
Walsh CE; Nienhuis AW; Samulski RJ; Brown MG; Miller JL; Young NS; Liu JM
J Clin Invest; 1994 Oct; 94(4):1440-8. PubMed ID: 7929819
[TBL] [Abstract][Full Text] [Related]
15. Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates.
Romero Z; Lomova A; Said S; Miggelbrink A; Kuo CY; Campo-Fernandez B; Hoban MD; Masiuk KE; Clark DN; Long J; Sanchez JM; Velez M; Miyahira E; Zhang R; Brown D; Wang X; Kurmangaliyev YZ; Hollis RP; Kohn DB
Mol Ther; 2019 Aug; 27(8):1389-1406. PubMed ID: 31178391
[TBL] [Abstract][Full Text] [Related]
16. Cell-Cycle-Specific Function of p53 in Fanconi Anemia Hematopoietic Stem and Progenitor Cell Proliferation.
Li X; Wilson AF; Du W; Pang Q
Stem Cell Reports; 2018 Feb; 10(2):339-346. PubMed ID: 29307578
[TBL] [Abstract][Full Text] [Related]
17. Minimal conditioning in Fanconi anemia promotes multi-lineage marrow engraftment at 10-fold lower cell doses.
Haworth KG; Ironside C; Ramirez MA; Weitz S; Beard BC; Schwartz JD; Adair JE; Kiem HP
J Gene Med; 2018 Oct; 20(10-11):e3050. PubMed ID: 30129972
[TBL] [Abstract][Full Text] [Related]
18. Persistent response of Fanconi anemia haematopoietic stem and progenitor cells to oxidative stress.
Li Y; Amarachintha S; Wilson AF; Li X; Du W
Cell Cycle; 2017 Jun; 16(12):1201-1209. PubMed ID: 28475398
[TBL] [Abstract][Full Text] [Related]
19. Retroviral mediated gene transfer of the Fanconi anemia complementation group C gene to hematopoietic progenitors of group C patients.
Liu JM; Young NS; Walsh CE; Cottler-Fox M; Carter C; Dunbar C; Barrett AJ; Emmons R
Hum Gene Ther; 1997 Sep; 8(14):1715-30. PubMed ID: 9322874
[TBL] [Abstract][Full Text] [Related]
20. Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector.
Becker PS; Taylor JA; Trobridge GD; Zhao X; Beard BC; Chien S; Adair J; Kohn DB; Wagner JE; Shimamura A; Kiem HP
Gene Ther; 2010 Oct; 17(10):1244-52. PubMed ID: 20485382
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
