These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

251 related articles for article (PubMed ID: 29101575)

  • 1. Current and Future Treatments for Lysosomal Storage Disorders.
    Rastall DPW; Amalfitano A
    Curr Treat Options Neurol; 2017 Nov; 19(12):45. PubMed ID: 29101575
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Stem Cell Applications in Lysosomal Storage Disorders: Progress and Ongoing Challenges.
    Köse S; Aerts-Kaya F; Uçkan Çetinkaya D; Korkusuz P
    Adv Exp Med Biol; 2021; 1347():135-162. PubMed ID: 33977438
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Recent advances in gene therapy for lysosomal storage disorders.
    Rastall DP; Amalfitano A
    Appl Clin Genet; 2015; 8():157-69. PubMed ID: 26170711
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Lysosomal storage diseases: Stem cell-based cell- and gene-therapy.
    Kim SU
    Cell Transplant; 2014 May; ():. PubMed ID: 24853878
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Hematopoietic stem cell transplant for lysosomal storage diseases.
    Lund TC
    Pediatr Endocrinol Rev; 2013 Nov; 11 Suppl 1():91-8. PubMed ID: 24380127
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Fetal therapies and trials for lysosomal storage diseases: a survey of attitudes of parents and patients.
    Schwab ME; Brown JEH; Lianoglou B; Jin C; Conroy PC; Gallagher RC; Harmatz P; MacKenzie TC
    Orphanet J Rare Dis; 2022 Jan; 17(1):25. PubMed ID: 35093147
    [TBL] [Abstract][Full Text] [Related]  

  • 7. An update on gene therapy for lysosomal storage disorders.
    Nagree MS; Scalia S; McKillop WM; Medin JA
    Expert Opin Biol Ther; 2019 Jul; 19(7):655-670. PubMed ID: 31056978
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Clinical Trials for Gene Therapy in Lysosomal Diseases With CNS Involvement.
    Sevin C; Deiva K
    Front Mol Biosci; 2021; 8():624988. PubMed ID: 34604300
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Current and potential therapeutic strategies for mucopolysaccharidoses.
    Noh H; Lee JI
    J Clin Pharm Ther; 2014 Jun; 39(3):215-24. PubMed ID: 24612142
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Enzyme Replacement Therapy: A Review and Its Role in Treating Lysosomal Storage Diseases.
    Li M
    Pediatr Ann; 2018 May; 47(5):e191-e197. PubMed ID: 29750286
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I.
    Penati R; Fumagalli F; Calbi V; Bernardo ME; Aiuti A
    J Inherit Metab Dis; 2017 Jul; 40(4):543-554. PubMed ID: 28560469
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Gene therapy for Mucopolysaccharidoses.
    Sawamoto K; Chen HH; Alméciga-Díaz CJ; Mason RW; Tomatsu S
    Mol Genet Metab; 2018 Feb; 123(2):59-68. PubMed ID: 29295764
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Treatments for lysosomal storage disorders.
    Lachmann R
    Biochem Soc Trans; 2010 Dec; 38(6):1465-8. PubMed ID: 21118108
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Combination Therapies for Lysosomal Storage Diseases: A Complex Answer to a Simple Problem.
    Macauley SL
    Pediatr Endocrinol Rev; 2016 Jun; 13 Suppl 1(Suppl 1):639-48. PubMed ID: 27491211
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Substrate reduction therapy.
    Platt FM; Jeyakumar M
    Acta Paediatr; 2008 Apr; 97(457):88-93. PubMed ID: 18339196
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Gene therapy for lysosomal storage diseases: the lessons and promise of animal models.
    Ellinwood NM; Vite CH; Haskins ME
    J Gene Med; 2004 May; 6(5):481-506. PubMed ID: 15133760
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Pharmaceutical Chaperones and Proteostasis Regulators in the Therapy of Lysosomal Storage Disorders: Current Perspective and Future Promises.
    Mohamed FE; Al-Gazali L; Al-Jasmi F; Ali BR
    Front Pharmacol; 2017; 8():448. PubMed ID: 28736525
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Gene therapy for lysosomal storage disorders.
    Barranger JM; Novelli EA
    Expert Opin Biol Ther; 2001 Sep; 1(5):857-67. PubMed ID: 11728220
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Hematopoietic Stem Cell Transplantation for Storage Disorders: Present Status.
    Chakraborty S; Gupta AK; Gupta N; Meena JP; Seth R; Kabra M
    Indian J Pediatr; 2024 Aug; 91(8):830-838. PubMed ID: 38639861
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Therapeutic approaches for lysosomal storage diseases: a patent update.
    Urbanelli L; Sagini K; Polidoro M; Brozzi A; Magini A; Emiliani C
    Recent Pat CNS Drug Discov; 2013 Aug; 8(2):91-109. PubMed ID: 23713988
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 13.