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6. Fetal therapies and trials for lysosomal storage diseases: a survey of attitudes of parents and patients. Schwab ME; Brown JEH; Lianoglou B; Jin C; Conroy PC; Gallagher RC; Harmatz P; MacKenzie TC Orphanet J Rare Dis; 2022 Jan; 17(1):25. PubMed ID: 35093147 [TBL] [Abstract][Full Text] [Related]
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