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2. Curative Ex Vivo Hepatocyte-Directed Gene Editing in a Mouse Model of Hereditary Tyrosinemia Type 1. VanLith C; Guthman R; Nicolas CT; Allen K; Du Z; Joo DJ; Nyberg SL; Lillegard JB; Hickey RD Hum Gene Ther; 2018 Nov; 29(11):1315-1326. PubMed ID: 29764210 [TBL] [Abstract][Full Text] [Related]
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