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3. Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls. Mendell JR; Khan N; Sha N; Eliopoulos H; McDonald CM; Goemans N; Mercuri E; Lowes LP; Alfano LN; J Neuromuscul Dis; 2021; 8(4):469-479. PubMed ID: 33523015 [TBL] [Abstract][Full Text] [Related]
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