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8. Mutations in GMPPB cause congenital myasthenic syndrome and bridge myasthenic disorders with dystroglycanopathies. Belaya K; Rodríguez Cruz PM; Liu WW; Maxwell S; McGowan S; Farrugia ME; Petty R; Walls TJ; Sedghi M; Basiri K; Yue WW; Sarkozy A; Bertoli M; Pitt M; Kennett R; Schaefer A; Bushby K; Parton M; Lochmüller H; Palace J; Muntoni F; Beeson D Brain; 2015 Sep; 138(Pt 9):2493-504. PubMed ID: 26133662 [TBL] [Abstract][Full Text] [Related]
9. ISPD mutations account for a small proportion of Italian Limb Girdle Muscular Dystrophy cases. Magri F; Colombo I; Del Bo R; Previtali S; Brusa R; Ciscato P; Scarlato M; Ronchi D; D'Angelo MG; Corti S; Moggio M; Bresolin N; Comi GP BMC Neurol; 2015 Sep; 15():172. PubMed ID: 26404900 [TBL] [Abstract][Full Text] [Related]
10. Refining genotype phenotype correlations in muscular dystrophies with defective glycosylation of dystroglycan. Godfrey C; Clement E; Mein R; Brockington M; Smith J; Talim B; Straub V; Robb S; Quinlivan R; Feng L; Jimenez-Mallebrera C; Mercuri E; Manzur AY; Kinali M; Torelli S; Brown SC; Sewry CA; Bushby K; Topaloglu H; North K; Abbs S; Muntoni F Brain; 2007 Oct; 130(Pt 10):2725-35. PubMed ID: 17878207 [TBL] [Abstract][Full Text] [Related]
11. Two patients with GMPPB mutation: The overlapping phenotypes of limb-girdle myasthenic syndrome and limb-girdle muscular dystrophy dystroglycanopathy. Montagnese F; Klupp E; Karampinos DC; Biskup S; Gläser D; Kirschke JS; Schoser B Muscle Nerve; 2017 Aug; 56(2):334-340. PubMed ID: 27874200 [TBL] [Abstract][Full Text] [Related]
12. Congenital muscular dystrophy and generalized epilepsy caused by GMPPB mutations. Raphael AR; Couthouis J; Sakamuri S; Siskind C; Vogel H; Day JW; Gitler AD Brain Res; 2014 Aug; 1575():66-71. PubMed ID: 24780531 [TBL] [Abstract][Full Text] [Related]
13. Lysosomal degradation of GMPPB is associated with limb-girdle muscular dystrophy type 2T. Tian WT; Zhou HY; Zhan FX; Zhu ZY; Yang J; Chen SD; Luan XH; Cao L Ann Clin Transl Neurol; 2019 Jun; 6(6):1062-1071. PubMed ID: 31211170 [TBL] [Abstract][Full Text] [Related]
14. TRAPPC11 and GOSR2 mutations associate with hypoglycosylation of α-dystroglycan and muscular dystrophy. Larson AA; Baker PR; Milev MP; Press CA; Sokol RJ; Cox MO; Lekostaj JK; Stence AA; Bossler AD; Mueller JM; Prematilake K; Tadjo TF; Williams CA; Sacher M; Moore SA Skelet Muscle; 2018 May; 8(1):17. PubMed ID: 29855340 [TBL] [Abstract][Full Text] [Related]
15. Expanding the phenotype of GMPPB mutations. Cabrera-Serrano M; Ghaoui R; Ravenscroft G; Johnsen RD; Davis MR; Corbett A; Reddel S; Sue CM; Liang C; Waddell LB; Kaur S; Lek M; North KN; MacArthur DG; Lamont PJ; Clarke NF; Laing NG Brain; 2015 Apr; 138(Pt 4):836-44. PubMed ID: 25681410 [TBL] [Abstract][Full Text] [Related]
16. Steroid therapy in an alpha-dystroglycanopathy due to GMPPB gene mutations: A case report. Fecarotta S; Gragnaniello V; Della Casa R; Romano A; Raiano E; Torella A; Savarese M; Nigro V; Strisciuglio P; Andria G; Parenti G Neuromuscul Disord; 2018 Nov; 28(11):956-960. PubMed ID: 30126629 [TBL] [Abstract][Full Text] [Related]
17. Mutations in GMPPA cause a glycosylation disorder characterized by intellectual disability and autonomic dysfunction. Koehler K; Malik M; Mahmood S; Gießelmann S; Beetz C; Hennings JC; Huebner AK; Grahn A; Reunert J; Nürnberg G; Thiele H; Altmüller J; Nürnberg P; Mumtaz R; Babovic-Vuksanovic D; Basel-Vanagaite L; Borck G; Brämswig J; Mühlenberg R; Sarda P; Sikiric A; Anyane-Yeboa K; Zeharia A; Ahmad A; Coubes C; Wada Y; Marquardt T; Vanderschaeghe D; Van Schaftingen E; Kurth I; Huebner A; Hübner CA Am J Hum Genet; 2013 Oct; 93(4):727-34. PubMed ID: 24035193 [TBL] [Abstract][Full Text] [Related]
18. Congenital muscular dystrophies with defective glycosylation of dystroglycan: a population study. Mercuri E; Messina S; Bruno C; Mora M; Pegoraro E; Comi GP; D'Amico A; Aiello C; Biancheri R; Berardinelli A; Boffi P; Cassandrini D; Laverda A; Moggio M; Morandi L; Moroni I; Pane M; Pezzani R; Pichiecchio A; Pini A; Minetti C; Mongini T; Mottarelli E; Ricci E; Ruggieri A; Saredi S; Scuderi C; Tessa A; Toscano A; Tortorella G; Trevisan CP; Uggetti C; Vasco G; Santorelli FM; Bertini E Neurology; 2009 May; 72(21):1802-9. PubMed ID: 19299310 [TBL] [Abstract][Full Text] [Related]
19. GMPPA defects cause a neuromuscular disorder with α-dystroglycan hyperglycosylation. Franzka P; Henze H; Jung MJ; Schüler SC; Mittag S; Biskup K; Liebmann L; Kentache T; Morales J; Martínez B; Katona I; Herrmann T; Huebner AK; Hennings JC; Groth S; Gresing L; Horstkorte R; Marquardt T; Weis J; Kaether C; Mutchinick OM; Ori A; Huber O; Blanchard V; von Maltzahn J; Hübner CA J Clin Invest; 2021 May; 131(9):. PubMed ID: 33755596 [TBL] [Abstract][Full Text] [Related]
20. Toward understanding tissue-specific symptoms in dolichol-phosphate-mannose synthesis disorders; insight from DPM3-CDG. van Tol W; Michelakakis H; Georgiadou E; van den Bergh P; Moraitou M; Papadimas GK; Papadopoulos C; Huijben K; Alsady M; Willemsen MA; Lefeber DJ J Inherit Metab Dis; 2019 Sep; 42(5):984-992. PubMed ID: 30931530 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]