These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

276 related articles for article (PubMed ID: 29803277)

  • 1. Genetic Therapies for Sickle Cell Disease.
    Jayavaradhan R; Malik P
    Pediatr Clin North Am; 2018 Jun; 65(3):465-480. PubMed ID: 29803277
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia.
    Dong AC; Rivella S
    Adv Exp Med Biol; 2017; 1013():155-176. PubMed ID: 29127680
    [TBL] [Abstract][Full Text] [Related]  

  • 3. Genetic treatment of a molecular disorder: gene therapy approaches to sickle cell disease.
    Hoban MD; Orkin SH; Bauer DE
    Blood; 2016 Feb; 127(7):839-48. PubMed ID: 26758916
    [TBL] [Abstract][Full Text] [Related]  

  • 4. A New Era for Hemoglobinopathies: More Than One Curative Option.
    Psatha N; Papayanni PG; Yannaki E
    Curr Gene Ther; 2017; 17(5):364-378. PubMed ID: 29357790
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Investigational curative gene therapy approaches to sickle cell disease.
    Williams DA; Esrick E
    Blood Adv; 2021 Dec; 5(23):5452. PubMed ID: 34905048
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Lentiviral and genome-editing strategies for the treatment of β-hemoglobinopathies.
    Magrin E; Miccio A; Cavazzana M
    Blood; 2019 Oct; 134(15):1203-1213. PubMed ID: 31467062
    [TBL] [Abstract][Full Text] [Related]  

  • 7. A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction.
    Perumbeti A; Higashimoto T; Urbinati F; Franco R; Meiselman HJ; Witte D; Malik P
    Blood; 2009 Aug; 114(6):1174-85. PubMed ID: 19474450
    [TBL] [Abstract][Full Text] [Related]  

  • 8. Sickle cell anemia therapy: progress since Pauling.
    Schechter AN; Rodgers GP
    Science; 2000 Jan; 287(5453):592-3. PubMed ID: 10691539
    [No Abstract]   [Full Text] [Related]  

  • 9. Gene Therapy in a Patient with Sickle Cell Disease.
    Ribeil JA; Hacein-Bey-Abina S; Payen E; Magnani A; Semeraro M; Magrin E; Caccavelli L; Neven B; Bourget P; El Nemer W; Bartolucci P; Weber L; Puy H; Meritet JF; Grevent D; Beuzard Y; Chrétien S; Lefebvre T; Ross RW; Negre O; Veres G; Sandler L; Soni S; de Montalembert M; Blanche S; Leboulch P; Cavazzana M
    N Engl J Med; 2017 Mar; 376(9):848-855. PubMed ID: 28249145
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Genetic strategies for the treatment of sickle cell anaemia.
    Mansilla-Soto J; Rivière I; Sadelain M
    Br J Haematol; 2011 Sep; 154(6):715-27. PubMed ID: 21707580
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Stem cell therapy for sickle cell disease: transplantation and gene therapy.
    Walters MC
    Hematology Am Soc Hematol Educ Program; 2005; ():66-73. PubMed ID: 16304361
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Gene Therapy as the New Frontier for Sickle Cell Disease.
    Garg H; Tatiossian KJ; Peppel K; Kato GJ; Herzog E
    Curr Med Chem; 2022; 29(3):453-466. PubMed ID: 34047257
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Hematopoietic stem cell gene transfer for the treatment of hemoglobin disorders.
    Persons DA
    Hematology Am Soc Hematol Educ Program; 2009; ():690-7. PubMed ID: 20008255
    [TBL] [Abstract][Full Text] [Related]  

  • 14. Genetic therapies for sickle cell disease.
    Esrick EB; Bauer DE
    Semin Hematol; 2018 Apr; 55(2):76-86. PubMed ID: 29958563
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Gene therapy for sickle cell disease: An update.
    Demirci S; Uchida N; Tisdale JF
    Cytotherapy; 2018 Jul; 20(7):899-910. PubMed ID: 29859773
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Diverse Approaches to Gene Therapy of Sickle Cell Disease.
    White SL; Hart K; Kohn DB
    Annu Rev Med; 2023 Jan; 74():473-487. PubMed ID: 36067800
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Cellular therapy for sickle cell disease.
    Abraham A; Jacobsohn DA; Bollard CM
    Cytotherapy; 2016 Nov; 18(11):1360-1369. PubMed ID: 27421743
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Gene replacement therapy for sickle cell disease and other blood disorders.
    Townes TM
    Hematology Am Soc Hematol Educ Program; 2008; ():193-6. PubMed ID: 19074080
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Progress toward safe and effective gene therapy for beta-thalassemia and sickle cell disease.
    Lebensburger J; Persons DA
    Curr Opin Drug Discov Devel; 2008 Mar; 11(2):225-32. PubMed ID: 18283610
    [TBL] [Abstract][Full Text] [Related]  

  • 20. Gene therapy for sickle cell disease.
    The Lancet Haematology
    Lancet Haematol; 2016 Oct; 3(10):e446. PubMed ID: 27692301
    [No Abstract]   [Full Text] [Related]  

    [Next]    [New Search]
    of 14.