170 related articles for article (PubMed ID: 30124006)
41. Expression of γ-globin genes in β-thalassemia patients treated with sirolimus: results from a pilot clinical trial (Sirthalaclin).
Zuccato C; Cosenza LC; Zurlo M; Gasparello J; Papi C; D'Aversa E; Breveglieri G; Lampronti I; Finotti A; Borgatti M; Scapoli C; Stievano A; Fortini M; Ramazzotti E; Marchetti N; Prosdocimi M; Gamberini MR; Gambari R
Ther Adv Hematol; 2022; 13():20406207221100648. PubMed ID: 35755297
[TBL] [Abstract][Full Text] [Related]
42. Highly efficient therapeutic gene editing of human hematopoietic stem cells.
Wu Y; Zeng J; Roscoe BP; Liu P; Yao Q; Lazzarotto CR; Clement K; Cole MA; Luk K; Baricordi C; Shen AH; Ren C; Esrick EB; Manis JP; Dorfman DM; Williams DA; Biffi A; Brugnara C; Biasco L; Brendel C; Pinello L; Tsai SQ; Wolfe SA; Bauer DE
Nat Med; 2019 May; 25(5):776-783. PubMed ID: 30911135
[TBL] [Abstract][Full Text] [Related]
43. Lineage-specific BCL11A knockdown circumvents toxicities and reverses sickle phenotype.
Brendel C; Guda S; Renella R; Bauer DE; Canver MC; Kim YJ; Heeney MM; Klatt D; Fogel J; Milsom MD; Orkin SH; Gregory RI; Williams DA
J Clin Invest; 2016 Oct; 126(10):3868-3878. PubMed ID: 27599293
[TBL] [Abstract][Full Text] [Related]
44. Responses of β-thalassemia and compound heterozygote of Sickle/βthalassemia of BCL11A Gene Polymorphism in Pakistani Patients.
Soomro N; Wahid M; Mehmood M; Danish SH
Pak J Med Sci; 2023; 39(6):1788-1792. PubMed ID: 37936787
[TBL] [Abstract][Full Text] [Related]
45. Original Research: A case-control genome-wide association study identifies genetic modifiers of fetal hemoglobin in sickle cell disease.
Liu L; Pertsemlidis A; Ding LH; Story MD; Steinberg MH; Sebastiani P; Hoppe C; Ballas SK; Pace BS
Exp Biol Med (Maywood); 2016 Apr; 241(7):706-18. PubMed ID: 27022141
[TBL] [Abstract][Full Text] [Related]
46. Disruption of the BCL11A Erythroid Enhancer Reactivates Fetal Hemoglobin in Erythroid Cells of Patients with β-Thalassemia Major.
Psatha N; Reik A; Phelps S; Zhou Y; Dalas D; Yannaki E; Levasseur DN; Urnov FD; Holmes MC; Papayannopoulou T
Mol Ther Methods Clin Dev; 2018 Sep; 10():313-326. PubMed ID: 30182035
[TBL] [Abstract][Full Text] [Related]
47. Potent and orally active purine-based fetal hemoglobin inducers for treating β-thalassemia and sickle cell disease.
Lai ZS; Yeh TK; Chou YC; Hsu T; Lu CT; Kung FC; Hsieh MY; Lin CH; Chen CT; James Shen CK; Jiaang WT
Eur J Med Chem; 2021 Jan; 209():112938. PubMed ID: 33109398
[TBL] [Abstract][Full Text] [Related]
48. Mithramycin induces fetal hemoglobin production in normal and thalassemic human erythroid precursor cells.
Fibach E; Bianchi N; Borgatti M; Prus E; Gambari R
Blood; 2003 Aug; 102(4):1276-81. PubMed ID: 12738678
[TBL] [Abstract][Full Text] [Related]
49. Pharmacological Induction of Fetal Hemoglobin in β-Thalassemia and Sickle Cell Disease: An Updated Perspective.
Bou-Fakhredin R; De Franceschi L; Motta I; Cappellini MD; Taher AT
Pharmaceuticals (Basel); 2022 Jun; 15(6):. PubMed ID: 35745672
[TBL] [Abstract][Full Text] [Related]
50. Hydroxyurea responses and fetal hemoglobin induction in beta-thalassemia/HbE patients' peripheral blood erythroid cell culture.
Watanapokasin R; Sanmund D; Winichagoon P; Muta K; Fucharoen S
Ann Hematol; 2006 Mar; 85(3):164-9. PubMed ID: 16389564
[TBL] [Abstract][Full Text] [Related]
51. Induction of Fetal Hemoglobin In Vivo Mediated by a Synthetic γ-Globin Zinc Finger Activator.
Costa FC; Fedosyuk H; Neades R; de Los Rios JB; Barbas CF; Peterson KR
Anemia; 2012; 2012():507894. PubMed ID: 22778925
[TBL] [Abstract][Full Text] [Related]
52. Human fetal hemoglobin expression is regulated by the developmental stage-specific repressor BCL11A.
Sankaran VG; Menne TF; Xu J; Akie TE; Lettre G; Van Handel B; Mikkola HK; Hirschhorn JN; Cantor AB; Orkin SH
Science; 2008 Dec; 322(5909):1839-42. PubMed ID: 19056937
[TBL] [Abstract][Full Text] [Related]
53. The Optimized γ-Globin Lentiviral Vector GGHI-mB-3D Leads to Nearly Therapeutic HbF Levels In Vitro in CD34
Drakopoulou E; Georgomanoli M; Lederer CW; Panetsos F; Kleanthous M; Voskaridou E; Valakos D; Papanikolaou E; Anagnou NP
Viruses; 2022 Dec; 14(12):. PubMed ID: 36560719
[TBL] [Abstract][Full Text] [Related]
54. Hemoglobin genetics: recent contributions of GWAS and gene editing.
Smith EC; Orkin SH
Hum Mol Genet; 2016 Oct; 25(R2):R99-R105. PubMed ID: 27340226
[TBL] [Abstract][Full Text] [Related]
55. A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition.
Traxler EA; Yao Y; Wang YD; Woodard KJ; Kurita R; Nakamura Y; Hughes JR; Hardison RC; Blobel GA; Li C; Weiss MJ
Nat Med; 2016 Sep; 22(9):987-90. PubMed ID: 27525524
[TBL] [Abstract][Full Text] [Related]
56. Detection of CRISPR/Cas9-Mediated Fetal Hemoglobin Reactivation in Erythroblasts Derived from Cord Blood-Hematopoietic Stem Cells.
Maroofi N; Maleki MSM; Tahmasebi M; Khorshid HRK; Modaberi Y; Najafipour R; Banan M
Mol Biotechnol; 2024 Apr; ():. PubMed ID: 38649638
[TBL] [Abstract][Full Text] [Related]
57. Trienone analogs of curcuminoids induce fetal hemoglobin synthesis via demethylation at
Nuamsee K; Chuprajob T; Pabuprapap W; Jintaridth P; Munkongdee T; Phannasil P; Vadolas J; Chaichompoo P; Suksamrarn A; Svasti S
Sci Rep; 2021 Apr; 11(1):8552. PubMed ID: 33879818
[TBL] [Abstract][Full Text] [Related]
58. KLF1 directly activates expression of the novel fetal globin repressor
Norton LJ; Funnell APW; Burdach J; Wienert B; Kurita R; Nakamura Y; Philipsen S; Pearson RCM; Quinlan KGR; Crossley M
Blood Adv; 2017 Apr; 1(11):685-692. PubMed ID: 29296711
[TBL] [Abstract][Full Text] [Related]
59. SIRT1 activates the expression of fetal hemoglobin genes.
Dai Y; Chen T; Ijaz H; Cho EH; Steinberg MH
Am J Hematol; 2017 Nov; 92(11):1177-1186. PubMed ID: 28776729
[TBL] [Abstract][Full Text] [Related]
60. DNA methylation patterns of β-globin cluster in β-thalassemia patients.
Bao X; Zuo Y; Chen D; Zhao C
Clin Epigenetics; 2020 Dec; 12(1):187. PubMed ID: 33272312
[TBL] [Abstract][Full Text] [Related]
[Previous] [Next] [New Search]
