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6. Growth advantage of corrected hepatocytes in a juvenile model of methylmalonic acidemia following liver directed adeno-associated viral mediated nuclease-free genome editing. Venturoni LE; Chandler RJ; Liao J; Hoffmann V; Ramesh N; Gordo S; Chau N; Venditti CP Mol Genet Metab; 2022; 137(1-2):1-8. PubMed ID: 35868241 [TBL] [Abstract][Full Text] [Related]
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