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5. Laying the Foundation for Neuromuscular Disease Gene Therapy. Duan D Hum Gene Ther; 2020 Aug; 31(15-16):785-786. PubMed ID: 32640898 [No Abstract] [Full Text] [Related]
6. Friedreich's ataxia. Cooper JM; Bradley JL Int Rev Neurobiol; 2002; 53():147-73. PubMed ID: 12512339 [No Abstract] [Full Text] [Related]
7. [Association of Friedreich's disease and a parkinsonian syndrome in several patients in one family]. CASTAIGNE P; CAMBIER J; CATHALA HP; AUGUSTIN P Rev Neurol (Paris); 1961 Nov; 105():452-4. PubMed ID: 13877145 [No Abstract] [Full Text] [Related]
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18. Partial correction of sensitivity to oxidant stress in Friedreich ataxia patient fibroblasts by frataxin-encoding adeno-associated virus and lentivirus vectors. Fleming J; Spinoulas A; Zheng M; Cunningham SC; Ginn SL; McQuilty RC; Rowe PB; Alexander IE Hum Gene Ther; 2005 Aug; 16(8):947-56. PubMed ID: 16076253 [TBL] [Abstract][Full Text] [Related]
19. Molecular basis of the neurodegenerative disorders. Martin JB N Engl J Med; 1999 Jun; 340(25):1970-80. PubMed ID: 10379022 [No Abstract] [Full Text] [Related]
20. Friedreich ataxia: an update on animal models, frataxin function and therapies. González-Cabo P; Llorens JV; Palau F; Moltó MD Adv Exp Med Biol; 2009; 652():247-61. PubMed ID: 20225031 [TBL] [Abstract][Full Text] [Related] [Next] [New Search]