111 related articles for article (PubMed ID: 30912054)
1. CRISPR Gene Therapy of the Eye: Targeted Knockout of Vegfa in Mouse Retina by Lentiviral Delivery.
Holmgaard A; Alsing S; Askou AL; Corydon TJ
Methods Mol Biol; 2019; 1961():307-328. PubMed ID: 30912054
[TBL] [Abstract][Full Text] [Related]
2. In Vivo Knockout of the Vegfa Gene by Lentiviral Delivery of CRISPR/Cas9 in Mouse Retinal Pigment Epithelium Cells.
Holmgaard A; Askou AL; Benckendorff JNE; Thomsen EA; Cai Y; Bek T; Mikkelsen JG; Corydon TJ
Mol Ther Nucleic Acids; 2017 Dec; 9():89-99. PubMed ID: 29246327
[TBL] [Abstract][Full Text] [Related]
3. Targeted Knockout of the Vegfa Gene in the Retina by Subretinal Injection of RNP Complexes Containing Cas9 Protein and Modified sgRNAs.
Holmgaard AB; Askou AL; Jensen EG; Alsing S; Bak RO; Mikkelsen JG; Corydon TJ
Mol Ther; 2021 Jan; 29(1):191-207. PubMed ID: 33022212
[TBL] [Abstract][Full Text] [Related]
4. CRISPR-LbCpf1 prevents choroidal neovascularization in a mouse model of age-related macular degeneration.
Koo T; Park SW; Jo DH; Kim D; Kim JH; Cho HY; Kim J; Kim JH; Kim JS
Nat Commun; 2018 May; 9(1):1855. PubMed ID: 29748595
[TBL] [Abstract][Full Text] [Related]
5. Tumor cell-targeted delivery of CRISPR/Cas9 by aptamer-functionalized lipopolymer for therapeutic genome editing of VEGFA in osteosarcoma.
Liang C; Li F; Wang L; Zhang ZK; Wang C; He B; Li J; Chen Z; Shaikh AB; Liu J; Wu X; Peng S; Dang L; Guo B; He X; Au DWT; Lu C; Zhu H; Zhang BT; Lu A; Zhang G
Biomaterials; 2017 Dec; 147():68-85. PubMed ID: 28938163
[TBL] [Abstract][Full Text] [Related]
6. Curative Ex Vivo Hepatocyte-Directed Gene Editing in a Mouse Model of Hereditary Tyrosinemia Type 1.
VanLith C; Guthman R; Nicolas CT; Allen K; Du Z; Joo DJ; Nyberg SL; Lillegard JB; Hickey RD
Hum Gene Ther; 2018 Nov; 29(11):1315-1326. PubMed ID: 29764210
[TBL] [Abstract][Full Text] [Related]
7. Lentiviral delivery of co-packaged Cas9 mRNA and a Vegfa-targeting guide RNA prevents wet age-related macular degeneration in mice.
Ling S; Yang S; Hu X; Yin D; Dai Y; Qian X; Wang D; Pan X; Hong J; Sun X; Yang H; Paludan SR; Cai Y
Nat Biomed Eng; 2021 Feb; 5(2):144-156. PubMed ID: 33398131
[TBL] [Abstract][Full Text] [Related]
8. Generation of novel Il2rg-knockout mice with clustered regularly interspaced short palindromic repeats (CRISPR) and Cas9.
Byambaa S; Uosaki H; Hara H; Nagao Y; Abe T; Shibata H; Nureki O; Ohmori T; Hanazono Y
Exp Anim; 2020 Apr; 69(2):189-198. PubMed ID: 31801915
[TBL] [Abstract][Full Text] [Related]
9. CRISPR therapy towards an HIV cure.
Herrera-Carrillo E; Gao Z; Berkhout B
Brief Funct Genomics; 2020 May; 19(3):201-208. PubMed ID: 31711197
[TBL] [Abstract][Full Text] [Related]
10. Development of gene therapy for treatment of age-related macular degeneration.
Askou AL
Acta Ophthalmol; 2014 Jul; 92 Thesis3():1-38. PubMed ID: 24953666
[TBL] [Abstract][Full Text] [Related]
11. In Vivo CRISPR/Cas9-Mediated Genome Editing Mitigates Photoreceptor Degeneration in a Mouse Model of X-Linked Retinitis Pigmentosa.
Hu S; Du J; Chen N; Jia R; Zhang J; Liu X; Yang L
Invest Ophthalmol Vis Sci; 2020 Apr; 61(4):31. PubMed ID: 32330228
[TBL] [Abstract][Full Text] [Related]
12. Genome surgery using Cas9 ribonucleoproteins for the treatment of age-related macular degeneration.
Kim K; Park SW; Kim JH; Lee SH; Kim D; Koo T; Kim KE; Kim JH; Kim JS
Genome Res; 2017 Mar; 27(3):419-426. PubMed ID: 28209587
[TBL] [Abstract][Full Text] [Related]
13. Suppression of Choroidal Neovascularization in Mice by Subretinal Delivery of Multigenic Lentiviral Vectors Encoding Anti-Angiogenic MicroRNAs.
Askou AL; Benckendorff JNE; Holmgaard A; Storm T; Aagaard L; Bek T; Mikkelsen JG; Corydon TJ
Hum Gene Ther Methods; 2017 Aug; 28(4):222-233. PubMed ID: 28817343
[TBL] [Abstract][Full Text] [Related]
14. AAV-Mediated CRISPR/Cas Gene Editing of Retinal Cells In Vivo.
Hung SS; Chrysostomou V; Li F; Lim JK; Wang JH; Powell JE; Tu L; Daniszewski M; Lo C; Wong RC; Crowston JG; Pébay A; King AE; Bui BV; Liu GS; Hewitt AW
Invest Ophthalmol Vis Sci; 2016 Jun; 57(7):3470-6. PubMed ID: 27367513
[TBL] [Abstract][Full Text] [Related]
15. Methods for In Vivo CRISPR/Cas Editing of the Adult Murine Retina.
Hung SS; Li F; Wang JH; King AE; Bui BV; Liu GS; Hewitt AW
Methods Mol Biol; 2018; 1715():113-133. PubMed ID: 29188510
[TBL] [Abstract][Full Text] [Related]
16. CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice.
Ohmori T; Nagao Y; Mizukami H; Sakata A; Muramatsu SI; Ozawa K; Tominaga SI; Hanazono Y; Nishimura S; Nureki O; Sakata Y
Sci Rep; 2017 Jun; 7(1):4159. PubMed ID: 28646206
[TBL] [Abstract][Full Text] [Related]
17. Development and application of CRISPR/Cas9 technologies in genomic editing.
Zhang C; Quan R; Wang J
Hum Mol Genet; 2018 Aug; 27(R2):R79-R88. PubMed ID: 29659822
[TBL] [Abstract][Full Text] [Related]
18. Cas9 immunity creates challenges for CRISPR gene editing therapies.
Crudele JM; Chamberlain JS
Nat Commun; 2018 Aug; 9(1):3497. PubMed ID: 30158648
[TBL] [Abstract][Full Text] [Related]
19. Engineered CRISPR Systems for Next Generation Gene Therapies.
Pineda M; Moghadam F; Ebrahimkhani MR; Kiani S
ACS Synth Biol; 2017 Sep; 6(9):1614-1626. PubMed ID: 28558198
[TBL] [Abstract][Full Text] [Related]
20. CRISPR-Cpf1: A New Tool for Plant Genome Editing.
Zaidi SS; Mahfouz MM; Mansoor S
Trends Plant Sci; 2017 Jul; 22(7):550-553. PubMed ID: 28532598
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
