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3. Cln1-mutations suppress Rab7-RILP interaction and impair autophagy contributing to neuropathology in a mouse model of infantile neuronal ceroid lipofuscinosis. Sarkar C; Sadhukhan T; Bagh MB; Appu AP; Chandra G; Mondal A; Saha A; Mukherjee AB J Inherit Metab Dis; 2020 Sep; 43(5):1082-1101. PubMed ID: 32279353 [TBL] [Abstract][Full Text] [Related]
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9. A function retained by the common mutant CLN3 protein is responsible for the late onset of juvenile neuronal ceroid lipofuscinosis. Kitzmüller C; Haines RL; Codlin S; Cutler DF; Mole SE Hum Mol Genet; 2008 Jan; 17(2):303-12. PubMed ID: 17947292 [TBL] [Abstract][Full Text] [Related]
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12. Intrathecal enzyme replacement therapy improves motor function and survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis. Lu JY; Nelvagal HR; Wang L; Birnbaum SG; Cooper JD; Hofmann SL Mol Genet Metab; 2015; 116(1-2):98-105. PubMed ID: 25982063 [TBL] [Abstract][Full Text] [Related]
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