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3. High dose IVIG successfully reduces high rhGAA IgG antibody titers in a CRIM-negative infantile Pompe disease patient. Rairikar M; Kazi ZB; Desai A; Walters C; Rosenberg A; Kishnani PS Mol Genet Metab; 2017 Sep; 122(1-2):76-79. PubMed ID: 28648664 [TBL] [Abstract][Full Text] [Related]
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11. A favorable outcome in an infantile-onset Pompe patient with cross reactive immunological material (CRIM) negative disease with high dose enzyme replacement therapy and adjusted immunomodulation. Curelaru S; Desai AK; Fink D; Zehavi Y; Kishnani PS; Spiegel R Mol Genet Metab Rep; 2022 Sep; 32():100893. PubMed ID: 35813979 [TBL] [Abstract][Full Text] [Related]
12. Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease. Messinger YH; Mendelsohn NJ; Rhead W; Dimmock D; Hershkovitz E; Champion M; Jones SA; Olson R; White A; Wells C; Bali D; Case LE; Young SP; Rosenberg AS; Kishnani PS Genet Med; 2012 Jan; 14(1):135-42. PubMed ID: 22237443 [TBL] [Abstract][Full Text] [Related]
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16. Teaching tolerance: New approaches to enzyme replacement therapy for Pompe disease. Cousens LP; Mingozzi F; van der Marel S; Su Y; Garman R; Ferreira V; Martin W; Scott DW; De Groot AS Hum Vaccin Immunother; 2012 Oct; 8(10):1459-64. PubMed ID: 23095864 [TBL] [Abstract][Full Text] [Related]
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