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5. In Vivo Base Editing of PCSK9 (Proprotein Convertase Subtilisin/Kexin Type 9) as a Therapeutic Alternative to Genome Editing. Chadwick AC; Wang X; Musunuru K Arterioscler Thromb Vasc Biol; 2017 Sep; 37(9):1741-1747. PubMed ID: 28751571 [TBL] [Abstract][Full Text] [Related]
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20. Genome Editing as a Treatment for the Most Prevalent Causative Genes of Autosomal Dominant Retinitis Pigmentosa. Diakatou M; Manes G; Bocquet B; Meunier I; Kalatzis V Int J Mol Sci; 2019 May; 20(10):. PubMed ID: 31126147 [No Abstract] [Full Text] [Related] [Next] [New Search]