447 related articles for article (PubMed ID: 31418294)
1. Dual
Dyka FM; Molday LL; Chiodo VA; Molday RS; Hauswirth WW
Hum Gene Ther; 2019 Nov; 30(11):1361-1370. PubMed ID: 31418294
[TBL] [Abstract][Full Text] [Related]
2. An AAV Dual Vector Strategy Ameliorates the Stargardt Phenotype in Adult
McClements ME; Barnard AR; Singh MS; Charbel Issa P; Jiang Z; Radu RA; MacLaren RE
Hum Gene Ther; 2019 May; 30(5):590-600. PubMed ID: 30381971
[TBL] [Abstract][Full Text] [Related]
3. Improved dual AAV vectors with reduced expression of truncated proteins are safe and effective in the retina of a mouse model of Stargardt disease.
Trapani I; Toriello E; de Simone S; Colella P; Iodice C; Polishchuk EV; Sommella A; Colecchi L; Rossi S; Simonelli F; Giunti M; Bacci ML; Polishchuk RS; Auricchio A
Hum Mol Genet; 2015 Dec; 24(23):6811-25. PubMed ID: 26420842
[TBL] [Abstract][Full Text] [Related]
4. Fundus autofluorescence in the Abca4(-/-) mouse model of Stargardt disease--correlation with accumulation of A2E, retinal function, and histology.
Charbel Issa P; Barnard AR; Singh MS; Carter E; Jiang Z; Radu RA; Schraermeyer U; MacLaren RE
Invest Ophthalmol Vis Sci; 2013 Aug; 54(8):5602-12. PubMed ID: 23761084
[TBL] [Abstract][Full Text] [Related]
5. Dual AAV Vectors for Stargardt Disease.
Trapani I
Methods Mol Biol; 2018; 1715():153-175. PubMed ID: 29188512
[TBL] [Abstract][Full Text] [Related]
6. Complement modulation in the retinal pigment epithelium rescues photoreceptor degeneration in a mouse model of Stargardt disease.
Lenis TL; Sarfare S; Jiang Z; Lloyd MB; Bok D; Radu RA
Proc Natl Acad Sci U S A; 2017 Apr; 114(15):3987-3992. PubMed ID: 28348233
[TBL] [Abstract][Full Text] [Related]
7. Expression of ABCA4 in the retinal pigment epithelium and its implications for Stargardt macular degeneration.
Lenis TL; Hu J; Ng SY; Jiang Z; Sarfare S; Lloyd MB; Esposito NJ; Samuel W; Jaworski C; Bok D; Finnemann SC; Radeke MJ; Redmond TM; Travis GH; Radu RA
Proc Natl Acad Sci U S A; 2018 Nov; 115(47):E11120-E11127. PubMed ID: 30397118
[TBL] [Abstract][Full Text] [Related]
8. Correction of the disease phenotype in the mouse model of Stargardt disease by lentiviral gene therapy.
Kong J; Kim SR; Binley K; Pata I; Doi K; Mannik J; Zernant-Rajang J; Kan O; Iqball S; Naylor S; Sparrow JR; Gouras P; Allikmets R
Gene Ther; 2008 Oct; 15(19):1311-20. PubMed ID: 18463687
[TBL] [Abstract][Full Text] [Related]
9. Complement system dysregulation and inflammation in the retinal pigment epithelium of a mouse model for Stargardt macular degeneration.
Radu RA; Hu J; Yuan Q; Welch DL; Makshanoff J; Lloyd M; McMullen S; Travis GH; Bok D
J Biol Chem; 2011 May; 286(21):18593-601. PubMed ID: 21464132
[TBL] [Abstract][Full Text] [Related]
10. Increased cone sensitivity to ABCA4 deficiency provides insight into macular vision loss in Stargardt's dystrophy.
Conley SM; Cai X; Makkia R; Wu Y; Sparrow JR; Naash MI
Biochim Biophys Acta; 2012 Jul; 1822(7):1169-79. PubMed ID: 22033104
[TBL] [Abstract][Full Text] [Related]
11. Effective delivery of large genes to the retina by dual AAV vectors.
Trapani I; Colella P; Sommella A; Iodice C; Cesi G; de Simone S; Marrocco E; Rossi S; Giunti M; Palfi A; Farrar GJ; Polishchuk R; Auricchio A
EMBO Mol Med; 2014 Feb; 6(2):194-211. PubMed ID: 24150896
[TBL] [Abstract][Full Text] [Related]
12. Lipofuscin and N-retinylidene-N-retinylethanolamine (A2E) accumulate in retinal pigment epithelium in absence of light exposure: their origin is 11-cis-retinal.
Boyer NP; Higbee D; Currin MB; Blakeley LR; Chen C; Ablonczy Z; Crouch RK; Koutalos Y
J Biol Chem; 2012 Jun; 287(26):22276-86. PubMed ID: 22570475
[TBL] [Abstract][Full Text] [Related]
13. Non-viral Gene Therapy for Stargardt Disease with ECO/pRHO-ABCA4 Self-Assembled Nanoparticles.
Sun D; Schur RM; Sears AE; Gao SQ; Vaidya A; Sun W; Maeda A; Kern T; Palczewski K; Lu ZR
Mol Ther; 2020 Jan; 28(1):293-303. PubMed ID: 31611143
[TBL] [Abstract][Full Text] [Related]
14. Split AAV8 Mediated ABCA4 Expression for Gene Therapy of Mouse Stargardt Disease (STGD1).
Li R; Jing Q; She K; Wang Q; Jin X; Zhao Q; Su J; Song L; Fu J; Wu X; Xu Q; Lu F; Wei Y; Yang Y
Hum Gene Ther; 2023 Jul; 34(13-14):616-628. PubMed ID: 37227014
[TBL] [Abstract][Full Text] [Related]
15. Assessment of AAV Dual Vector Safety in the
McClements ME; Barnard AR; Charbel Issa P; MacLaren RE
Transl Vis Sci Technol; 2020 Jun; 9(7):20. PubMed ID: 32724727
[TBL] [Abstract][Full Text] [Related]
16. Characterization of native retinal fluorophores involved in biosynthesis of A2E and lipofuscin-associated retinopathies.
Bui TV; Han Y; Radu RA; Travis GH; Mata NL
J Biol Chem; 2006 Jun; 281(26):18112-9. PubMed ID: 16638746
[TBL] [Abstract][Full Text] [Related]
17. ATP-binding cassette transporter ABCA4: molecular properties and role in vision and macular degeneration.
Molday RS
J Bioenerg Biomembr; 2007 Dec; 39(5-6):507-17. PubMed ID: 17994272
[TBL] [Abstract][Full Text] [Related]
18. Functional Characterization of ABCA4 Missense Variants Linked to Stargardt Macular Degeneration.
Garces FA; Scortecci JF; Molday RS
Int J Mol Sci; 2020 Dec; 22(1):. PubMed ID: 33375396
[TBL] [Abstract][Full Text] [Related]
19. Omega-3 Fatty Acids Supplementation: Therapeutic Potential in a Mouse Model of Stargardt Disease.
Prokopiou E; Kolovos P; Kalogerou M; Neokleous A; Nicolaou O; Sokratous K; Kyriacou K; Georgiou T
Invest Ophthalmol Vis Sci; 2018 Jun; 59(7):2757-2767. PubMed ID: 29860462
[TBL] [Abstract][Full Text] [Related]
20. Localization and functional characterization of the p.Asn965Ser (N965S) ABCA4 variant in mice reveal pathogenic mechanisms underlying Stargardt macular degeneration.
Molday LL; Wahl D; Sarunic MV; Molday RS
Hum Mol Genet; 2018 Jan; 27(2):295-306. PubMed ID: 29145636
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]
