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3. Lentiviral-Mediated Gene Therapy in Fanconi Anemia-A Mice Reveals Long-Term Engraftment and Continuous Turnover of Corrected HSCs. Molina-Estevez FJ; Nowrouzi A; Lozano ML; Galy A; Charrier S; von Kalle C; Guenechea G; Bueren JA; Schmidt M Curr Gene Ther; 2015; 15(6):550-62. PubMed ID: 26415575 [TBL] [Abstract][Full Text] [Related]
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