253 related articles for article (PubMed ID: 31618280)
1. Gene editing of PKLR gene in human hematopoietic progenitors through 5' and 3' UTR modified TALEN mRNA.
Quintana-Bustamante O; Fañanas-Baquero S; Orman I; Torres R; Duchateau P; Poirot L; Gouble A; Bueren JA; Segovia JC
PLoS One; 2019; 14(10):e0223775. PubMed ID: 31618280
[TBL] [Abstract][Full Text] [Related]
2. Clinically relevant gene editing in hematopoietic stem cells for the treatment of pyruvate kinase deficiency.
Fañanas-Baquero S; Quintana-Bustamante O; Dever DP; Alberquilla O; Sanchez-Dominguez R; Camarena J; Ojeda-Perez I; Dessy-Rodriguez M; Turk R; Schubert MS; Lattanzi A; Xu L; Lopez-Lorenzo JL; Bianchi P; Bueren JA; Behlke MA; Porteus M; Segovia JC
Mol Ther Methods Clin Dev; 2021 Sep; 22():237-248. PubMed ID: 34485608
[TBL] [Abstract][Full Text] [Related]
3. TALEN mediated gene editing in a mouse model of Fanconi anemia.
Pino-Barrio MJ; Giménez Y; Villanueva M; Hildenbeutel M; Sánchez-Dominguez R; Rodríguez-Perales S; Pujol R; Surrallés J; Río P; Cathomen T; Mussolino C; Bueren JA; Navarro S
Sci Rep; 2020 Apr; 10(1):6997. PubMed ID: 32332829
[TBL] [Abstract][Full Text] [Related]
4. Rescue of pyruvate kinase deficiency in mice by gene therapy using the human isoenzyme.
Meza NW; Alonso-Ferrero ME; Navarro S; Quintana-Bustamante O; Valeri A; Garcia-Gomez M; Bueren JA; Bautista JM; Segovia JC
Mol Ther; 2009 Dec; 17(12):2000-9. PubMed ID: 19755962
[TBL] [Abstract][Full Text] [Related]
5. Generation of a High Number of Healthy Erythroid Cells from Gene-Edited Pyruvate Kinase Deficiency Patient-Specific Induced Pluripotent Stem Cells.
Garate Z; Quintana-Bustamante O; Crane AM; Olivier E; Poirot L; Galetto R; Kosinski P; Hill C; Kung C; Agirre X; Orman I; Cerrato L; Alberquilla O; Rodriguez-Fornes F; Fusaki N; Garcia-Sanchez F; Maia TM; Ribeiro ML; Sevilla J; Prosper F; Jin S; Mountford J; Guenechea G; Gouble A; Bueren JA; Davis BR; Segovia JC
Stem Cell Reports; 2015 Dec; 5(6):1053-1066. PubMed ID: 26549847
[TBL] [Abstract][Full Text] [Related]
6. Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency.
Garcia-Gomez M; Calabria A; Garcia-Bravo M; Benedicenti F; Kosinski P; López-Manzaneda S; Hill C; Del Mar Mañu-Pereira M; Martín MA; Orman I; Vives-Corrons JL; Kung C; Schambach A; Jin S; Bueren JA; Montini E; Navarro S; Segovia JC
Mol Ther; 2016 Aug; 24(7):1187-98. PubMed ID: 27138040
[TBL] [Abstract][Full Text] [Related]
7. Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome.
Kuo CY; Long JD; Campo-Fernandez B; de Oliveira S; Cooper AR; Romero Z; Hoban MD; Joglekar AV; Lill GR; Kaufman ML; Fitz-Gibbon S; Wang X; Hollis RP; Kohn DB
Cell Rep; 2018 May; 23(9):2606-2616. PubMed ID: 29847792
[TBL] [Abstract][Full Text] [Related]
8. Improved Genome Editing Efficiency and Flexibility Using Modified Oligonucleotides with TALEN and CRISPR-Cas9 Nucleases.
Renaud JB; Boix C; Charpentier M; De Cian A; Cochennec J; Duvernois-Berthet E; Perrouault L; Tesson L; Edouard J; Thinard R; Cherifi Y; Menoret S; Fontanière S; de Crozé N; Fraichard A; Sohm F; Anegon I; Concordet JP; Giovannangeli C
Cell Rep; 2016 Mar; 14(9):2263-2272. PubMed ID: 26923600
[TBL] [Abstract][Full Text] [Related]
9. Comparison of gene editing efficiencies of CRISPR/Cas9 and TALEN for generation of MSTN knock-out cashmere goats.
Zhang J; Liu J; Yang W; Cui M; Dai B; Dong Y; Yang J; Zhang X; Liu D; Liang H; Cang M
Theriogenology; 2019 Jul; 132():1-11. PubMed ID: 30981084
[TBL] [Abstract][Full Text] [Related]
10. Genome Editing in Human Pluripotent Stem Cells.
Carlson-Stevermer J; Saha K
Methods Mol Biol; 2017; 1590():165-174. PubMed ID: 28353269
[TBL] [Abstract][Full Text] [Related]
11. Homologous recombination-mediated targeted integration in monkey embryos using TALE nucleases.
Chu C; Yang Z; Yang J; Yan L; Si C; Kang Y; Chen Z; Chen Y; Ji W; Niu Y
BMC Biotechnol; 2019 Jan; 19(1):7. PubMed ID: 30646876
[TBL] [Abstract][Full Text] [Related]
12. Targeted gene therapy into a safe harbor site in human hematopoietic progenitor cells.
Rodriguez-Fornes F; Quintana-Bustamante O; Lozano ML; Segovia JC; Bueren JA; Guenechea G
Gene Ther; 2020 Sep; 27(9):435-450. PubMed ID: 32218505
[TBL] [Abstract][Full Text] [Related]
13. New Bicistronic TALENs Greatly Improve Genome Editing.
Martín-Fernández JM; Fleischer A; Vallejo-Diez S; Palomino E; Sánchez-Gilabert A; Ruiz R; Bejarano Y; Llinàs P; Gayá A; Bachiller D
Curr Protoc Stem Cell Biol; 2020 Mar; 52(1):e104. PubMed ID: 32023363
[TBL] [Abstract][Full Text] [Related]
14. Generation of Stable Knockout Mammalian Cells by TALEN-Mediated Locus-Specific Gene Editing.
Mahata B; Biswas K
Methods Mol Biol; 2017; 1498():107-120. PubMed ID: 27709571
[TBL] [Abstract][Full Text] [Related]
15. TALEN-Mediated Mutagenesis and Genome Editing.
Ma AC; Chen Y; Blackburn PR; Ekker SC
Methods Mol Biol; 2016; 1451():17-30. PubMed ID: 27464798
[TBL] [Abstract][Full Text] [Related]
16. A guide for drug inducible genome editing with HIT systems.
Zhao C; Wei S; Wang Y
Methods Enzymol; 2019; 621():53-68. PubMed ID: 31128789
[TBL] [Abstract][Full Text] [Related]
17. TALEN- and CRISPR-enhanced DNA homologous recombination for gene editing in zebrafish.
Zhang Y; Huang H; Zhang B; Lin S
Methods Cell Biol; 2016; 135():107-20. PubMed ID: 27443922
[TBL] [Abstract][Full Text] [Related]
18. Specific correction of pyruvate kinase deficiency-causing point mutations by CRISPR/Cas9 and single-stranded oligodeoxynucleotides.
Fañanas-Baquero S; Morín M; Fernández S; Ojeda-Perez I; Dessy-Rodriguez M; Giurgiu M; Bueren JA; Moreno-Pelayo MA; Segovia JC; Quintana-Bustamante O
Front Genome Ed; 2023; 5():1104666. PubMed ID: 37188156
[TBL] [Abstract][Full Text] [Related]
19. Analysis of individual differences in radiosensitivity using genome editing.
Matsuura S; Royba E; Akutsu SN; Yanagihara H; Ochiai H; Kudo Y; Tashiro S; Miyamoto T
Ann ICRP; 2016 Jun; 45(1 Suppl):290-6. PubMed ID: 27012844
[TBL] [Abstract][Full Text] [Related]
20. Genome Editing of Silkworms.
Tsubota T; Sezutsu H
Methods Mol Biol; 2017; 1630():205-218. PubMed ID: 28643261
[TBL] [Abstract][Full Text] [Related]
[Next] [New Search]