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22. What´s new in Gene Therapy of Hemophilia. Rodriguez-Merchan EC Curr Gene Ther; 2018; 18(2):107-114. PubMed ID: 29446741 [TBL] [Abstract][Full Text] [Related]
23. AAV-mediated gene transfer for hemophilia. High K Genet Med; 2002; 4(6 Suppl):56S-61S. PubMed ID: 12544490 [TBL] [Abstract][Full Text] [Related]
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33. Successful Phenotype Improvement following Gene Therapy for Severe Hemophilia A in Privately Owned Dogs. Callan MB; Haskins ME; Wang P; Zhou S; High KA; Arruda VR PLoS One; 2016; 11(3):e0151800. PubMed ID: 27011017 [TBL] [Abstract][Full Text] [Related]
34. Gene therapy for the hemophilias. Walsh CE Curr Opin Pediatr; 2002 Feb; 14(1):12-6. PubMed ID: 11880728 [TBL] [Abstract][Full Text] [Related]
35. AAV5-Factor VIII Gene Transfer in Severe Hemophilia A. Rangarajan S; Walsh L; Lester W; Perry D; Madan B; Laffan M; Yu H; Vettermann C; Pierce GF; Wong WY; Pasi KJ N Engl J Med; 2017 Dec; 377(26):2519-2530. PubMed ID: 29224506 [TBL] [Abstract][Full Text] [Related]