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15. Intraventricular Cerliponase Alfa Treatment in a Patient with Advanced Neuronal Ceroid Lipofuscinosis Type 2. Nakashima S; Hamada M; Kimura T; Tanifuji S; Takahashi A; Yashita D; Kakimoto Y; Matsukawa T; Ishiura H; Toda T Intern Med; 2024 Jun; 63(12):1807-1812. PubMed ID: 37926545 [TBL] [Abstract][Full Text] [Related]
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