These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

125 related articles for article (PubMed ID: 32033431)

  • 1. Preface of Special Issue "Molecular Therapies for Inherited Retinal Diseases".
    Collin RWJ; Garanto A
    Genes (Basel); 2020 Feb; 11(2):. PubMed ID: 32033431
    [TBL] [Abstract][Full Text] [Related]  

  • 2. Voretigene neparvovec-rzyl for treatment of
    Ciulla TA; Hussain RM; Berrocal AM; Nagiel A
    Expert Opin Biol Ther; 2020 Jun; 20(6):565-578. PubMed ID: 32149547
    [No Abstract]   [Full Text] [Related]  

  • 3. Gene therapy for inherited retinal diseases: progress and possibilities.
    Hu ML; Edwards TL; O'Hare F; Hickey DG; Wang JH; Liu Z; Ayton LN
    Clin Exp Optom; 2021 May; 104(4):444-454. PubMed ID: 33689657
    [TBL] [Abstract][Full Text] [Related]  

  • 4. Inherited Retinal Diseases Due to
    Aoun M; Passerini I; Chiurazzi P; Karali M; De Rienzo I; Sartor G; Murro V; Filimonova N; Seri M; Banfi S
    Int J Mol Sci; 2021 Jul; 22(13):. PubMed ID: 34281261
    [TBL] [Abstract][Full Text] [Related]  

  • 5. Newer therapeutic options for inherited retinal diseases: Gene and cell replacement therapy.
    Battu R; Ratra D; Gopal L
    Indian J Ophthalmol; 2022 Jul; 70(7):2316-2325. PubMed ID: 35791112
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Technological advancements to study cellular signaling pathways in inherited retinal degenerative diseases.
    Roy A; Hilhorst R; Groten J; Paquet-Durand F; Tomar T
    Curr Opin Pharmacol; 2021 Oct; 60():102-110. PubMed ID: 34388439
    [TBL] [Abstract][Full Text] [Related]  

  • 7. RPE65-associated inherited retinal diseases: consensus recommendations for eligibility to gene therapy.
    Sodi A; Banfi S; Testa F; Della Corte M; Passerini I; Pelo E; Rossi S; Simonelli F;
    Orphanet J Rare Dis; 2021 Jun; 16(1):257. PubMed ID: 34088339
    [TBL] [Abstract][Full Text] [Related]  

  • 8. [Progress in research on pathogenic genes and gene therapy for inherited retinal diseases].
    Zhu L; Cao C; Sun J; Gao T; Liang X; Nie Z; Ji Y; Jiang P; Guan M
    Zhonghua Yi Xue Yi Chuan Xue Za Zhi; 2017 Feb; 34(1):118-123. PubMed ID: 28186610
    [TBL] [Abstract][Full Text] [Related]  

  • 9. Molecular Therapies for Inherited Retinal Diseases-Current Standing, Opportunities and Challenges.
    Vázquez-Domínguez I; Garanto A; Collin RWJ
    Genes (Basel); 2019 Aug; 10(9):. PubMed ID: 31466352
    [TBL] [Abstract][Full Text] [Related]  

  • 10. Gene therapy for inherited retinal diseases.
    Nuzbrokh Y; Ragi SD; Tsang SH
    Ann Transl Med; 2021 Aug; 9(15):1278. PubMed ID: 34532415
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Guiding Lights in Genome Editing for Inherited Retinal Disorders: Implications for Gene and Cell Therapy.
    Sanjurjo-Soriano C; Kalatzis V
    Neural Plast; 2018; 2018():5056279. PubMed ID: 29853845
    [TBL] [Abstract][Full Text] [Related]  

  • 12. Future Perspectives of Prime Editing for the Treatment of Inherited Retinal Diseases.
    Hansen S; McClements ME; Corydon TJ; MacLaren RE
    Cells; 2023 Jan; 12(3):. PubMed ID: 36766782
    [TBL] [Abstract][Full Text] [Related]  

  • 13. Cost-effectiveness of Voretigene Neparvovec-rzyl vs Standard Care for RPE65-Mediated Inherited Retinal Disease.
    Johnson S; Buessing M; O'Connell T; Pitluck S; Ciulla TA
    JAMA Ophthalmol; 2019 Oct; 137(10):1115-1123. PubMed ID: 31318398
    [TBL] [Abstract][Full Text] [Related]  

  • 14. RNA-Based Therapeutic Strategies for Inherited Retinal Dystrophies.
    Garanto A
    Adv Exp Med Biol; 2019; 1185():71-77. PubMed ID: 31884591
    [TBL] [Abstract][Full Text] [Related]  

  • 15. Has retinal gene therapy come of age? From bench to bedside and back to bench.
    Trapani I; Auricchio A
    Hum Mol Genet; 2019 Oct; 28(R1):R108-R118. PubMed ID: 31238338
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Cost Utility of Voretigene Neparvovec for Biallelic RPE65-Mediated Inherited Retinal Disease.
    Zimmermann M; Lubinga SJ; Banken R; Rind D; Cramer G; Synnott PG; Chapman RH; Khan S; Carlson J
    Value Health; 2019 Feb; 22(2):161-167. PubMed ID: 30711060
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Pharmaceutical Development of AAV-Based Gene Therapy Products for the Eye.
    Rodrigues GA; Shalaev E; Karami TK; Cunningham J; Slater NKH; Rivers HM
    Pharm Res; 2018 Dec; 36(2):29. PubMed ID: 30591984
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Current Management of Patients with RPE65 Mutation Associated Inherited Retinal Degenerations in Europe: Results of a 2-Year Follow-Up Multinational Survey.
    Lorenz B; Tavares J; van den Born LI; Marques JP; Pilotto E; Stingl K; Charbel Issa P; Leroux D; Dollfus H; Scholl HPN
    Ophthalmic Res; 2023; 66(1):727-748. PubMed ID: 36878196
    [TBL] [Abstract][Full Text] [Related]  

  • 19. The Foundation Fighting Blindness Plays an Essential and Expansive Role in Driving Genetic Research for Inherited Retinal Diseases.
    Shaberman B; Durham T
    Genes (Basel); 2019 Jul; 10(7):. PubMed ID: 31284566
    [TBL] [Abstract][Full Text] [Related]  

  • 20.
    ; ; . PubMed ID:
    [No Abstract]   [Full Text] [Related]  

    [Next]    [New Search]
    of 7.