These tools will no longer be maintained as of December 31, 2024. Archived website can be found here. PubMed4Hh GitHub repository can be found here. Contact NLM Customer Service if you have questions.


BIOMARKERS

Molecular Biopsy of Human Tumors

- a resource for Precision Medicine *

166 related articles for article (PubMed ID: 32168519)

  • 1. Spinal Muscular Atrophy in the Age of Gene Therapy.
    Williams L
    AACN Adv Crit Care; 2020 Mar; 31(1):86-91. PubMed ID: 32168519
    [No Abstract]   [Full Text] [Related]  

  • 2. Future avenues for therapy development for spinal muscular atrophy.
    Groen EJN
    Expert Opin Drug Discov; 2018 Oct; 13(10):899-902. PubMed ID: 30124076
    [No Abstract]   [Full Text] [Related]  

  • 3. Genetic therapy for spinal muscular atrophy.
    MacKenzie A
    Nat Biotechnol; 2010 Mar; 28(3):235-7. PubMed ID: 20212484
    [No Abstract]   [Full Text] [Related]  

  • 4. Zolgensma - one-time gene therapy for spinal muscular atrophy.
    Med Lett Drugs Ther; 2019 Jul; 61(1577):113-114. PubMed ID: 31381549
    [No Abstract]   [Full Text] [Related]  

  • 5. Advances and challenges in developing a therapy for spinal muscular atrophy.
    Anderton RS; Mastaglia FL
    Expert Rev Neurother; 2015; 15(8):895-908. PubMed ID: 26200127
    [TBL] [Abstract][Full Text] [Related]  

  • 6. Treating neonatal spinal muscular atrophy: A 21st century success story?
    Tizzano EF
    Early Hum Dev; 2019 Nov; 138():104851. PubMed ID: 31604576
    [TBL] [Abstract][Full Text] [Related]  

  • 7. Maximising returns: combining newborn screening with gene therapy for spinal muscular atrophy.
    Gillingwater TH
    J Neurol Neurosurg Psychiatry; 2021 Dec; 92(12):1252. PubMed ID: 34321342
    [No Abstract]   [Full Text] [Related]  

  • 8. Targeting splicing in spinal muscular atrophy.
    Burnett BG; Sumner CJ
    Ann Neurol; 2008 Jan; 63(1):3-6. PubMed ID: 18232015
    [No Abstract]   [Full Text] [Related]  

  • 9. Interventions for spinal muscular atrophy: an impetus for newborn screening.
    EBioMedicine; 2021 Jul; 69():103507. PubMed ID: 34315607
    [No Abstract]   [Full Text] [Related]  

  • 10. Spinal Muscular Atrophy and Common Therapeutic Advances.
    Bozorg Qomi S; Asghari A; Salmaninejad A; Mojarrad M
    Fetal Pediatr Pathol; 2019 Jun; 38(3):226-238. PubMed ID: 31060440
    [TBL] [Abstract][Full Text] [Related]  

  • 11. Gene therapy rescues newborns with spinal muscular atrophy.
    Sheridan C
    Nat Biotechnol; 2018 Aug; 36(8):669-670. PubMed ID: 30080825
    [No Abstract]   [Full Text] [Related]  

  • 12. Developing therapies for spinal muscular atrophy.
    Wertz MH; Sahin M
    Ann N Y Acad Sci; 2016 Feb; 1366(1):5-19. PubMed ID: 26173388
    [TBL] [Abstract][Full Text] [Related]  

  • 13. The End of the Beginning: The Journey to Molecular Therapies for Spinal Muscular Atrophy.
    Pacak CA; Kang PB
    Pediatr Neurol; 2020 Jan; 102():1-2. PubMed ID: 31481328
    [No Abstract]   [Full Text] [Related]  

  • 14. More is needed to complement the available therapies of spinal muscular atrophy.
    Singh RN
    Future Med Chem; 2019 Nov; 11(22):2873-2876. PubMed ID: 31668092
    [No Abstract]   [Full Text] [Related]  

  • 15. Development of gene therapies-lessons from nusinersen.
    Xu L; Irony I; Bryan WW; Dunn B
    Gene Ther; 2017 Sep; 24(9):527-528. PubMed ID: 28737743
    [TBL] [Abstract][Full Text] [Related]  

  • 16. Spinal Muscular Atrophy.
    Nicolau S; Waldrop MA; Connolly AM; Mendell JR
    Semin Pediatr Neurol; 2021 Apr; 37():100878. PubMed ID: 33892848
    [TBL] [Abstract][Full Text] [Related]  

  • 17. Therapeutic strategies for the treatment of spinal muscular atrophy.
    Cherry JJ; Androphy EJ
    Future Med Chem; 2012 Sep; 4(13):1733-50. PubMed ID: 22924510
    [TBL] [Abstract][Full Text] [Related]  

  • 18. Willingness to Pay for a Newborn Screening Test for Spinal Muscular Atrophy.
    Lin PJ; Yeh WS; Neumann PJ
    Pediatr Neurol; 2017 Jan; 66():69-75. PubMed ID: 27769729
    [TBL] [Abstract][Full Text] [Related]  

  • 19. Gene Therapy Briefs.
    Hum Gene Ther Clin Dev; 2019 Jun; 30(2):43-46. PubMed ID: 31215808
    [No Abstract]   [Full Text] [Related]  

  • 20. Moving towards treatments for spinal muscular atrophy: hopes and limits.
    Wirth B; Barkats M; Martinat C; Sendtner M; Gillingwater TH
    Expert Opin Emerg Drugs; 2015 Sep; 20(3):353-6. PubMed ID: 25920617
    [TBL] [Abstract][Full Text] [Related]  

    [Next]    [New Search]
    of 9.